Clinical Trials on Congenital Malformation in New Zealand
Total 857 results
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Scioderm, Inc.Amicus TherapeuticsTerminatedEpidermolysis BullosaPoland, Spain, Serbia, Netherlands, United States, Austria, Australia, Israel, Germany, France, United Kingdom, Lithuania
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Lenus Therapeutics, LLCTerminatedDystrophic Epidermolysis Bullosa | Junctional Epidermolysis BullosaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Terminated
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Wake Forest University Health SciencesPatient-Centered Outcomes Research Institute; Atrium Health Levine Cancer InstituteCompletedSickle Cell DiseaseUnited States
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Rhythm Pharmaceuticals, Inc.CompletedPrader-Willi SyndromeUnited States
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Cyclerion TherapeuticsCompletedSickle Cell DiseaseUnited States, United Kingdom, Lebanon
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Aegerion Pharmaceuticals, Inc.Active, not recruitingGeneralized LipodystrophyUnited States
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Boston Children's HospitalEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruitingIntellectual Disability | Autism Spectrum Disorder | Phelan-McDermid SyndromeUnited States
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Grifols Therapeutics LLCGrifols Biologicals, LLCTerminatedHemophilia A, CongenitalUnited States, Spain, Italy, India, Canada, Russian Federation
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Sideris PharmaceuticalsTerminatedIron Overload | Beta-ThalassemiaUnited States, Canada, Lebanon, Thailand, Turkey
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New York Institute of TechnologyRecruitingPain, Chronic | Ehlers-Danlos SyndromeUnited States
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UCSF Benioff Children's Hospital OaklandGenentech, Inc.CompletedBasal Cell Nevus Syndrome | Gorlin SyndromeUnited States
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CSL BehringCompletedSickle Cell DiseaseUnited States, United Kingdom, Netherlands
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UCSF Benioff Children's Hospital OaklandGenentech, Inc.CompletedBasal Cell Nevus Syndrome | Gorlin's SyndromeUnited States
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Zimmer BiometRecruitingRheumatoid Arthritis | Osteoarthritis, Knee | Avascular Necrosis | Traumatic Arthritis | Varus Deformity | Valgus Deformity | Knee Pain Chronic | Polyarthritis | Flexion Deformity of KneeUnited States
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Novartis PharmaceuticalsCompletedSickle Cell Disease (SCD)United States
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Forma Therapeutics, Inc.Novo Nordisk A/SRecruiting
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University of California, San FranciscoNational Cancer Institute (NCI)CompletedNon-melanomatous Skin CancerUnited States
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Genzyme, a Sanofi CompanyCompletedAlport Syndrome Patients With eGFR Between 45-90 ml/Min/1.73 m2France, Germany, Australia, United States, United Kingdom, Canada
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BioMarin PharmaceuticalCompletedSickle Cell DiseaseUnited States
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Novartis PharmaceuticalsCompletedTumors Characterized by Genetic Abnormalities of ALKAustralia, Belgium, Germany, Netherlands, Spain, Italy, Singapore, Korea, Republic of, United Kingdom, United States, Canada
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University of RochesterRecruitingLymphoma | Myelodysplastic Syndromes | Multiple Myeloma | Solid Tumor | Acute Leukemia | Aplastic Anemia | Chronic Leukemia | Immune Deficiency Disorder | Congenital Hematological Disorder | Metabolism DisorderUnited States
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Forma Therapeutics, Inc.Novo Nordisk A/SRecruitingSickle Cell DiseaseUnited States, Italy, Spain, United Kingdom, France, Lebanon, Germany, Oman, Canada, Greece
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Sickle Cell Disease | Hemoglobinopathies | Sickle Cell Anemia | Thalassemia | Beta-ThalassemiaUnited States, Italy, Germany, Saudi Arabia
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UCSF Benioff Children's Hospital OaklandNational Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Sickle CellUnited States
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GlycoMimetics IncorporatedCompletedAnemia, Sickle CellUnited States, Canada
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National Heart, Lung, and Blood Institute (NHLBI)National Institutes of Health (NIH)CompletedSickle Cell AnemiaUnited States
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La Jolla Pharmaceutical CompanyTerminatedBeta-ThalassemiaAustralia, Thailand, United States, Greece, Italy, Lebanon, Turkey, United Kingdom
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DNage B.V.TerminatedCockayne SyndromeUnited States, France, United Kingdom
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Forma Therapeutics, Inc.RecruitingSickle Cell Disease | ThalassemiaUnited States, Lebanon, Canada
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Memorial Sloan Kettering Cancer CenterRecruitingCutaneous Melanocytic Neoplasm | Large Cutaneous Melanocytic Nevi | Neurocutaneous MelanocytosisUnited States
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Boston Children's HospitalPhelan-McDermid Syndrome FoundationCompletedIntellectual Disability | Autism Spectrum Disorder | Phelan-McDermid SyndromeUnited States
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WestatEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedSickle Cell Disease | Thalassemia | Pediatric CancerUnited States, Brazil
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Roche Sequencing SolutionsPerinatal Quality Foundation: Nuchal Translucency Quality ReviewCompletedTrisomy 21United States, Belgium, Netherlands, Sweden, Italy, Canada
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Elizabeth Berry-KravisNational Institute of Neurological Disorders and Stroke (NINDS); Novartis PharmaceuticalsCompleted
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University Hospital MuensterUniversity of Pisa; Medical University of Vienna; Hacettepe University; Charite... and other collaboratorsRecruitingPrimary Ciliary Dyskinesia | Ciliary Motility DisordersGermany
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Arbor Research Collaborative for HealthNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)SuspendedLiver Diseases | Alpha 1-Antitrypsin Deficiency | Alagille SyndromeUnited States, Canada
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Sequenom, Inc.PRA Health SciencesCompletedPregnancy | Down Syndrome | Aneuploidy | Edwards SyndromeUnited States, France
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University Hospital MuensterUniversity of Pisa; Medical University of Vienna; Hacettepe University; Charite... and other collaboratorsRecruitingPrimary Ciliary Dyskinesia | Ciliary Motility DisordersGermany
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Eunice Kennedy Shriver National Institute of Child...UnknownDown Syndrome | Chromosome AbnormalitiesUnited States
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Translational Research Center for Medical Innovation...RecruitingNeutral Lipid Storage DiseaseChina, United States, France, Austria, Germany, Italy, Japan, Netherlands, United Kingdom
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ShireTakeda Development Center Americas, Inc.Completed
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Neurocrine BiosciencesActive, not recruitingCongenital Adrenal HyperplasiaUnited States, Spain, Belgium, Austria, Bulgaria, Canada, Czechia, France, Germany, Greece, Israel, Italy, Netherlands, Poland, Portugal, Serbia, Sweden, United Kingdom
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Beam Therapeutics Inc.RecruitingSickle Cell DiseaseUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Sickle CellUnited States
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Monica BhatiaCompletedSickle Cell Disease | Graft Versus Host DiseaseUnited States
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PfizerCompletedPhase 1 Sickle CellUnited States, United Kingdom, Belgium, Netherlands, Italy
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Hematological DiseasesUnited States, Belgium, Canada, France, Germany, Italy, United Kingdom
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Regeneron PharmaceuticalsRecruitingCongenital Hearing Loss Secondary to Biallelic Mutations of the Otoferlin Gene (OTOF)Spain, United Kingdom, United States