- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Congenital Malformation in New Zealand
Total 850 results
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Institute of Liver and Biliary Sciences, IndiaUnknownPortal Hypertension, Biliary AtresiaIndia
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NYU Langone HealthUniversity of California, Los Angeles; University of Southern California; University... and other collaboratorsWithdrawnPierre Robin SequenceUnited States
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Grifols Therapeutics LLCInstituto Grifols, S.A.CompletedCongenital AfibrinogenemiaIndia, United States, Italy, Lebanon
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W.L.Gore & AssociatesActive, not recruitingMigraine | Patent Foramen Ovale | PFO - Patent Foramen OvaleUnited States
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Memorial Sloan Kettering Cancer CenterRecruitingSickle Cell Disease | Thalassemia | Thalassemia, BetaUnited States
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PfizerNo longer availableSickle Cell DiseaseUnited States
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Boston UniversityCompletedBeta-ThalassemiaUnited States, United Kingdom
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Mirum Pharmaceuticals, Inc.Clinigen, Inc.Approved for marketingAlagille SyndromeUnited States
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ArQule, Inc. (a wholly owned subsidiary of Merck...Worldwide Clinical TrialsTerminatedPIK3CA-Related Overgrowth Spectrum (PROS)/Proteus SyndromeUnited States, Australia, Italy, Spain
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Stryker CraniomaxillofacialQmed Consulting A/SEnrolling by invitationCraniofacial Abnormalities | Cranioplasty | Craniofacial InjuriesGermany, Spain, United States, Austria, France, United Kingdom
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Hospital for Special Surgery, New YorkThe Hospital for Sick Children; Boston Children's Hospital; Nicklaus Children... and other collaboratorsWithdrawnCerebral Palsy | Hip DysplasiaUnited States, Canada
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Memorial Sloan Kettering Cancer CenterBoston Children's Hospital; Fred Hutchinson Cancer Center; Children's Hospital... and other collaboratorsCompletedLeukemia | Myelodysplastic Syndrome | Aplastic AnemiaUnited States
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Novartis PharmaceuticalsCompleted
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Invenux, LLCState University of New York - Downstate Medical CenterActive, not recruitingSickle Cell Disease | Sickle-Beta Zero ThalassemiaUnited States
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ActelionCanadian Heart Research CentreCompletedPulmonary Arterial HypertensionUnited States
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Children's Health System, Inc.Walter Lorenz Surgical CorporationUnknownRepair of Pectus ExcavatumUnited States, Canada
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University of RochesterCompletedNeurodevelopmental Abnormality | Extreme PrematurityUnited States
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DisperSol Technologies, LLCCompletedThalassemia MajorThailand, United States
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Tenaya TherapeuticsMedical University of South Carolina; Johns Hopkins University; University of... and other collaboratorsRecruitingArrhythmogenic Right Ventricular CardiomyopathyUnited States, Italy, United Kingdom, France, Sweden, Germany
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GE HealthcareLaboratory Corporation of AmericaCompletedTransthoracic Echocardiography | Suspected or Known Structural or Functional Cardiac AbnormalityUnited States
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International Spine Study Group FoundationOrthofix Inc.; DePuy SynthesRecruitingCervical DeformityUnited States
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National Institute of Diabetes and Digestive and...Completed
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Gilead SciencesTerminatedLong QT Syndrome Type 3United States, Germany, Canada, Netherlands, Italy, France, Israel, United Kingdom
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Novartis PharmaceuticalsCompletedHealthy Volunteers | Atopic Dermatitis | Netherton SyndromeNetherlands, United States
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Boehringer IngelheimRecruitingNetherton SyndromeBelgium, United Kingdom, Australia, Germany, China, Malaysia, United States, Japan, France, Israel, Bulgaria, Italy, Switzerland, Austria, Netherlands, Portugal
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Natera, Inc.CompletedTrisomy 21 | Trisomy 18 | Trisomy 13 | Sex Chromosome Abnormalities | Microdeletion SyndromesUnited States, Spain, Taiwan
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AO Foundation, AO SpineCompletedSpinal DeformityUnited States, Turkey, Hong Kong, United Kingdom, China, Australia, Netherlands, Canada, Japan, Brazil, India, Israel, Pakistan, Spain
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Novartis PharmaceuticalsCompletedMyelodysplastic Syndromes | Fanconi Syndrome | Anemia, Aplastic | Beta-thalassemia | Anemia, Diamond-BlackfanUnited States
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National Center for Research Resources (NCRR)Completed
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NovartisCompletedSickle Cell DiseaseUnited States
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PfizerWithdrawn
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Novartis PharmaceuticalsActive, not recruitingSickle Cell DiseaseUnited States
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Columbia UniversityNational Institute of Nursing Research (NINR)CompletedSickle Cell DiseaseUnited States
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Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta... and other collaboratorsRecruitingIntellectual Disability | Autism Spectrum Disorder | Fragile X Syndrome | Developmental Disability | Congenital Anomaly | Facioscapulohumeral Muscular Dystrophy 1United States
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Community Medical Center, Toms River, NJMonmouth Medical Center; Newark Beth Israel Medical Center; Rutgers Robert Wood...Not yet recruitingPain, Acute | Sickle Cell Disease | Sickle Cell CrisisUnited States
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Medicem International CR s.r.o.CompletedLabor; Forced or Induced, Affecting Fetus or Newborn | Labour Onset and Length AbnormalitiesUnited States, Germany, Czechia, India, Russian Federation, Slovakia, United Kingdom
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Office of Rare Diseases (ORD)UnknownAdrenal Hyperplasia, CongenitalUnited States, Brazil, France
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Far Eastern Memorial HospitalCompletedStress Urinary Incontinence | Vaginal AgenesisTaiwan
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Columbia UniversityNew York Blood CenterCompleted
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QOL Medical, LLCJohns Hopkins University; Massachusetts General Hospital; Baylor College of Medicine and other collaboratorsCompletedCongenital Sucrase-isomaltase Deficiency (CSID)United States
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Columbia UniversityCompleted
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Billy SinTerminatedPain | Sickle Cell DisorderUnited States
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Hoffmann-La RocheCompletedDown SyndromeUnited States, Italy, Argentina, France, Spain, Mexico, Canada, New Zealand, Singapore, United Kingdom
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI); FDA Office of Orphan Products... and other collaboratorsCompletedMarfan SyndromeUnited States, Canada, Belgium
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bluebird bioEnrolling by invitationSickle Cell DiseaseUnited States, France
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NYU Langone HealthCompletedCongenital Heart Block | Neonatal Lupus | Autoantibody-Associated Heart BlockUnited States
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Genzyme, a Sanofi CompanyCompletedBeta-ThalassemiaUnited States
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AfimmuneRecruitingSickle Cell DiseaseUnited States
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Duke UniversityNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health... and other collaboratorsCompletedSickle Cell DiseaseUnited States
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Lenetix Medical Screening LaboratoryUnknownDown Syndrome (Trisomy 21) | Edward's Syndrome (Trisomy 18) | Patau Syndrome (Trisomy 13) | Klinefelter Syndrome (47, XXY) | and Other Chromosome | Abnormalities.United States