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Clinical Trials on Congenital Malformation in New Zealand
Total 850 results
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Alexander KolevzonCompletedEpilepsy | Phelan-McDermid SyndromeUnited States
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NuVasiveCompletedSpinal Deformity | Spinal Trauma | Vertebra; DegenerationUnited States, Brazil
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Abbott Medical DevicesRecruitingStroke | Patent Foramen OvaleUnited States, Germany, Canada, Switzerland, Italy, Portugal, United Kingdom
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Diane GeorgeActive, not recruitingSickle Cell Disease | Hemoglobinopathies | Severe Congenital Neutropenia | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Macrophage Activation Syndrome | Bone Marrow Failure Syndrome | Amegakaryocytic Thrombocytopenia | Schwachman Diamond Syndrome | Primary Immunodeficiency Syndromes | Acquired Immunodeficiency... and other conditionsUnited States
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International Spine Study Group FoundationDePuy SpineCompletedScoliosis | Kyphosis | Cervical DeformityUnited States
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Spruce BiosciencesRecruitingCongenital Adrenal Hyperplasia | 21-OHDUnited States
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Emory UniversityNational Heart, Lung, and Blood Institute (NHLBI)Recruiting
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Mezzion Pharma Co. LtdNational Heart, Lung, and Blood Institute (NHLBI)UnknownFunctional Single Ventricle Heart DiseaseUnited States, Korea, Republic of, Canada
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Intact Medical CorporationCompleted
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Kanecia Obie ZimmermanNational Institutes of Health (NIH); The Emmes Company, LLCCompletedInfantile HemangiomaUnited States
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bluebird bioRecruitingSickle Cell DiseaseUnited States
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Taiho Oncology, Inc.TerminatedAdvanced Solid Tumors With HER2 Abnormalities | Advanced Solid Tumors With HER3 AbnormalitiesUnited States, Spain, France, United Kingdom
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Yale UniversityLilly PharmaceuticalCompanyNot yet recruitingIdiopathic Subglottic StenosisUnited States
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Abyrx, Inc.TerminatedAnkylosing Spondylitis | Fused Vertebrae | Sagittal Deformities | Thoracolumbar KyphosisUnited States
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Natera, Inc.Montefiore Medical Center; Tufts Medical Center; MOUNT SINAI HOSPITAL; Long Island...CompletedTrisomy 21 | Trisomy 18 | Trisomy 13 | Sex Chromosome AbnormalitiesUnited States
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PfizerCompletedHealthy | Sickle Cell AnemiaUnited States
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Mezzion Pharma Co. LtdNational Heart, Lung, and Blood Institute (NHLBI)CompletedSingle Ventricle Heart DiseaseUnited States, Korea, Republic of, Canada
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National Heart, Lung, and Blood Institute (NHLBI)National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedMarfan Syndrome | Turner Syndrome | Ehlers-Danlos Syndrome | Loeys-Dietz Syndrome | Shprintzen-Goldberg Syndrome | FBN1, TGFBR1, TGFBR2, ACTA2 or MYH11 Genetic Mutation | Bicuspid Aortic Valve Without Known Family History | Bicuspid Aortic Valve With Family History | Bicuspid Aortic Valve With Coarctation and other conditionsUnited States
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Albert Einstein College of MedicineTerminated
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Kirby InstituteNational Heart, Lung, and Blood Institute (NHLBI); St Vincent's Hospital, Sydney and other collaboratorsCompletedGlucose Metabolism Disorders | Metabolic Diseases | HIV Infections | Cardiovascular Disease | Dyslipidemias | LipodystrophyAustralia
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Mast Therapeutics, Inc.CompletedSickle Cell DiseaseUnited States
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Abbott Medical DevicesTerminated
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NYU Langone HealthCompletedKidney, Polycystic, Autosomal DominantUnited States
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The Rogosin InstituteWeill Medical College of Cornell University; New York Presbyterian HospitalRecruiting
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Mark LebwohlCompletedPseudoxanthoma ElasticumUnited States
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Mayne Pharma International Pty LtdTerminatedLamellar IchthyosisUnited States, Spain, Canada, Germany, France, Australia, Israel, Ukraine, United Kingdom
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Taipei Tzu Chi Hospital, Buddhist Tzu Chi Medical...Unknown
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NICHD Neonatal Research NetworkNational Center for Research Resources (NCRR); Medical Research Council of...CompletedDuctus Arteriosus, Patent | Infant, Very Low Birth Weight | Infant, PrematureUnited States
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Instituto Grifols, S.A.WithdrawnHypofibrinogenemia | Congenital AfibrinogenemiaIndia, Turkey, Lebanon, United States, Bulgaria
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Garvan Institute of Medical ResearchCompletedPrader-Willi SyndromeAustralia
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Icahn School of Medicine at Mount SinaiMayo Clinic; Baylor College of Medicine; Children's Hospital of Philadelphia; University... and other collaboratorsRecruitingCongenital Disorders of GlycosylationUnited States
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Boston Children's HospitalBoston Medical Center; National Human Genome Research Institute (NHGRI); The... and other collaboratorsRecruitingGenetic Predisposition to Disease | Genetics Disease | Genetics/Birth DefectsUnited States
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Timber Pharmaceuticals Inc.Active, not recruitingIchthyosisUnited States, Canada, Germany, France, Italy
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Abbott Medical DevicesCompletedPost-Infarction Ventricular Septal DefectUnited States
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Neuren Pharmaceuticals LimitedRecruiting
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Sydney Local Health DistrictEnrolling by invitationClass III Malocclusion | UnderbiteAustralia
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Daiichi Sankyo, Inc.PXE InternationalActive, not recruitingPseudoxanthoma ElasticumUnited States, Netherlands
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Foresee Pharmaceuticals Co., Ltd.Recruiting
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Medical College of WisconsinNational Heart, Lung, and Blood Institute (NHLBI); Dana-Farber Cancer Institute and other collaboratorsCompletedSickle Cell DiseaseUnited States
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PfizerPfizerAvailableSickle Cell DiseaseUnited States, Brazil
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Abigail NixonRecruitingAnalgesia | Sickle Cell Disease | Ketamine | Vaso-occlusive Crisis | Vaso-Occlusive Pain Episode in Sickle Cell Disease | Intranasal KetamineUnited States
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Memorial Sloan Kettering Cancer CenterPediatric Brain Tumor ConsortiumTerminatedFanconi Anemia | Myelodysplastic Syndrome (MDS) | Acute Myelogenous Leukemia (AML)United States
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Icahn School of Medicine at Mount SinaiNational Institute of Neurological Disorders and Stroke (NINDS)Enrolling by invitationAutism Spectrum Disorder (ASD) | Phelan-McDermid SyndromeUnited States
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bluebird bioCompletedSickle Cell DiseaseUnited States
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Montefiore Medical CenterJazz Pharmaceuticals; Foundation for Prader-Willi ResearchActive, not recruitingPrader-Willi SyndromeUnited States
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NICHD Neonatal Research NetworkEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingInfant, Newborn, Diseases | Patent Ductus Arteriosus | Infant, Premature | Patent Ductus Arteriosus After Premature BirthUnited States
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Novartis PharmaceuticalsCompleted
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Gamida Cell ltdCompletedSickle Cell Disease & ThalassemiaUnited States
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Growing Spine Study GroupGrowing Spine FoundationCompletedEarly Onset Scoliosis | Thoracic Insufficiency Syndrome | Congenital Spinal Deformities | Infantile Idiopathic Scoliosis | Neuromuscular Spinal Deformity | Syndromic Spinal DeformityUnited States, Canada, United Kingdom, Egypt, Ghana, Spain, Turkey
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Boston Children's HospitalAgios Pharmaceuticals, Inc.CompletedPyruvate Kinase Deficiency | Congenital Non-Spherocytic Hemolytic AnemiaUnited States, Germany, Canada, Czechia, Italy, Netherlands