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Clinical Trials on Congenital Muscular Dystrophy Type 1A in Italy
Total 543 results
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Mallinckrodt ARD LLCTerminatedMuscular Dystrophy, DuchenneSpain, Bulgaria, Italy, United States, Mexico, Israel, Serbia, Turkey
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University of GenovaUnknownCharcot-Marie-Tooth Disease | Charcot-Marie-Tooth Disease Type 1AItaly
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Santhera PharmaceuticalsTerminatedDuchenne Muscular Dystrophy (DMD)United States, Spain, Netherlands, Sweden, Germany, France, Belgium, United Kingdom, Italy, Ireland, Switzerland, Austria, Bulgaria, Hungary, Israel
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyUnited States, Netherlands, Belgium, Germany, Argentina, Brazil, France, Italy, Sweden, Turkey
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Wave Life Sciences Ltd.TerminatedDuchenne Muscular DystrophyUnited States, Belgium, United Kingdom, Czechia, Canada, France, Italy, Sweden
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Cooperative International Neuromuscular Research...UnknownBecker Muscular DystrophyUnited States, Canada, Italy, United Kingdom
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Belgium, Spain, United Kingdom, Netherlands, Germany, Canada, Italy
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PTC TherapeuticsCompletedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Germany, Spain, Sweden, Canada, Italy, Australia, Belgium, France, Israel, United Kingdom
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingRetinal Detachment | Epiretinal Membrane | Macular Holes | Macular DystrophiesItaly
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States, Belgium, Australia, Canada, France, Germany, Israel, Italy, Spain, Sweden, United Kingdom
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Japan, Italy
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.Active, not recruitingDuchenne Muscular DystrophyKorea, Republic of, Chile, Japan, China, United Kingdom, Netherlands, Spain, Norway, Russian Federation, Australia, Greece, Italy, New Zealand, Turkey, Mexico, Czechia, Canada
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Santhera PharmaceuticalsCompletedMuscular Dystrophy, Duchenne | Ambulatory CareUnited States, Spain, Austria, Belgium, France, Germany, Italy, Netherlands, Sweden, Switzerland
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Cooperative International Neuromuscular Research...United States Department of Defense; National Institutes of Health (NIH); U.S... and other collaboratorsUnknownDuchenne Muscular DystrophyUnited States, Canada, Australia, India, Israel, Argentina, Italy, Sweden
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Sarepta Therapeutics, Inc.Hoffmann-La RocheRecruitingDuchenne Muscular DystrophyBelgium, United States, Japan, Spain, Italy, United Kingdom
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Newcastle... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Germany, Italy
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Santhera PharmaceuticalsTerminatedDuchenne Muscular DystrophyUnited States, Belgium, United Kingdom, Austria, France, Germany, Italy, Spain, Switzerland
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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ItalfarmacoCromsourceEnrolling by invitationDuchenne Muscular DystrophySpain, United States, Canada, Belgium, France, Israel, Italy, Netherlands, Serbia, Germany, United Kingdom
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IRCCS Eugenio MedeaCompletedMuscular DystrophiesItaly
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophyKorea, Republic of, Chile, Taiwan, China, United States, United Kingdom, Netherlands, Spain, Australia, Norway, Russian Federation, Greece, Italy, Turkey, Mexico, Canada, Hong Kong, New Zealand, Ukraine
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ItalfarmacoSyneos HealthCompletedDuchenne Muscular DystrophyUnited States, Italy, Spain, Canada, Belgium, France, Germany, Israel, Netherlands, Serbia, United Kingdom
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PfizerTerminatedDuchenne Muscular DystrophyUnited States, Australia, Canada, United Kingdom, Japan, Bulgaria, Italy, Poland
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BioMarin PharmaceuticalNo longer availableDuchenne Muscular DystrophyUnited States, Germany, United Kingdom, Japan, Netherlands, France, Spain, Korea, Republic of, Italy, Belgium, Taiwan, Argentina, Australia, Bulgaria, Czechia, Israel, Norway, Poland, Russian Federation, Turkey
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Belgium, Israel, Spain, Canada, Australia, Switzerland, United Kingdom, France, China, Netherlands, Italy, Austria, Czechia
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Sarepta Therapeutics, Inc.Hoffmann-La RocheActive, not recruitingDuchenne Muscular DystrophyUnited States, Japan, Taiwan, Belgium, Spain, Germany, Hong Kong, Italy, United Kingdom
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Sarepta Therapeutics, Inc.TerminatedAn Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular DystrophyDuchenne Muscular DystrophyUnited States, Belgium, Canada, Spain, United Kingdom, Czechia, Germany, Israel, Bulgaria, France, Italy, Poland, Sweden
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Hoffmann-La RocheCompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, Australia, Japan, France, Netherlands, Spain, Argentina, Germany, Italy, United Kingdom, Sweden
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Sarepta Therapeutics, Inc.Active, not recruitingMuscular Dystrophy, DuchenneUnited States, Korea, Republic of, India, Slovenia, Turkey, United Kingdom, Germany, Switzerland, Spain, Czechia, France, Serbia, Taiwan, Netherlands, Mexico, Colombia, Denmark, New Zealand, Norway, Greece, Hungary, Ireland, Italy, Jo... and more
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GlaxoSmithKlineCompletedMuscular DystrophiesFrance, Denmark, Germany, Belgium, Spain, Turkey, Korea, Republic of, Brazil, Netherlands, Italy, Chile, Japan, Canada, Hungary, Russian Federation, Czechia, Poland, Norway, Argentina, Taiwan
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Fondazione IRCCS Ca' Granda, Ospedale Maggiore...CompletedMuscular Dystrophies | Muscle InflammationItaly
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Alessandra PedrocchiCompletedMuscular DystrophiesItaly
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PfizerActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Belgium, Korea, Republic of, Taiwan, Canada, Australia, Germany, Japan, France, Italy, United Kingdom, Russian Federation, Israel, Switzerland
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FibroGenTerminatedDuchenne Muscular DystrophyUnited States, Spain, Canada, Australia, China, Italy, Belgium, France, Netherlands, Austria, United Kingdom
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Eli Lilly and CompanyTerminatedMuscular Dystrophy, DuchenneGermany, United States, Spain, Belgium, France, Italy, Taiwan, Netherlands, Turkey, Korea, Republic of, Argentina, Canada, Japan, Puerto Rico, Russian Federation, United Kingdom
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States, Canada, Argentina, Australia, Israel, Italy
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Korea, Republic of, Italy, United Kingdom, Canada, Poland, Spain, France, Germany, Belgium, Australia, Czechia, Serbia, Greece, Argentina, Bulgaria, Denmark, Hungary, India, Ireland, Israel, Mexico, Russian Federation, ...
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GlaxoSmithKlineTerminatedMuscular DystrophiesFrance, Bulgaria, Denmark, Germany, Belgium, Canada, Spain, Turkey, United Kingdom, Korea, Republic of, Brazil, Netherlands, Italy, Japan, Czech Republic, Chile, Israel, Hungary, Russian Federation, Australia, Poland, Norway, Argentina and more
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IRCCS Eugenio MedeaCompleted
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Fondazione Serena Onlus - Centro Clinico NeMO MilanoAzienda Ospedaliera Città della Salute e della Scienza di Torino; Fondazione... and other collaboratorsActive, not recruiting
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Sarepta Therapeutics, Inc.RecruitingLimb-girdle Muscular DystrophyUnited States, Brazil, Belgium, Canada, Germany, Italy, Spain, Sweden, Turkey, United Kingdom
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Catholic University of the Sacred HeartUnknownRetinal Degeneration | Genetic Disease | Single-Gene Defects | Macular DystrophyItaly
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PTC TherapeuticsCooperative International Neuromuscular Research Group; The John Walton Muscular...Active, not recruitingMuscular Dystrophy, DuchenneGermany, France, United Kingdom, Brazil, Italy, Austria, Sweden, Czechia, Greece, Hungary, Israel, Latvia, Norway, Portugal, Romania, Slovenia
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ProQR TherapeuticsRecruitingEye Diseases | Neurologic Manifestations | Retinal Degeneration | Retinal Dystrophies | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalBelgium, Brazil, Canada, Germany, Italy, Netherlands, United Kingdom
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Astellas Pharma Global Development, Inc.Active, not recruitingStargardt's Macular DystrophyItaly, United States, Israel, United Kingdom, Germany, Spain, Hungary, France
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PTC TherapeuticsTerminatedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Germany, Brazil, Bulgaria, Chile, Czechia, Poland, Sweden, Switzerland, Turkey
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Catholic University of the Sacred HeartFondazione TelethonUnknownMyotonic Dystrophy | Sudden Cardiac DeathItaly
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PTC TherapeuticsCompletedNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States, Spain, Korea, Republic of, Belgium, France, Canada, Australia, United Kingdom, Israel, Italy, Brazil, Chile, Czechia, Sweden, Switzerland, Turkey, Germany, Poland
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Michele De BonisCompletedBicuspid Aortic Valve | Ascending Aorta AneurysmItaly
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Istituto Ortopedico RizzoliRecruitingVascular MalformationsItaly