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Clinical Trials on Congenital Muscular Dystrophy Type 1A in Italy
Total 543 results
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A | Haemophilia BSpain, Italy, Greece, Germany, United Kingdom
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Stichting European Myeloma NetworkCelgene Corporation; Healt Data Specialists - HeaDS (CRO); EMN Research Italy...Active, not recruitingMultiple MyelomaFrance, Greece, Italy, Netherlands
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Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka TypeUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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Translational Research Center for Medical Innovation...RecruitingNeutral Lipid Storage DiseaseChina, United States, France, Austria, Germany, Italy, Japan, Netherlands, United Kingdom
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SECRETO Study ConsortiumSahlgrenska University Hospital, Sweden; Academy of Finland; Hospital District... and other collaboratorsRecruitingIschemic Stroke | Thrombosis | Brain Infarction | Foramen Ovale, PatentItaly, Estonia, Finland, Germany, Lithuania, Netherlands, Norway, Sweden, Turkey, United Kingdom, Greece, Portugal, Spain
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Sigma Tau Research Switzerland SACompleted
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University of Modena and Reggio EmiliaAzienda USL - IRCCS di Reggio EmiliaRecruitingNeoplasms | Lymphoma | Cancer | Breast Cancer | Multiple Myeloma | Colorectal Cancer | Prostate Cancer | Thyroid CancerItaly
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Silvio AimeCompleted
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Scholar Rock, Inc.Active, not recruitingNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Anti-myostatin | Spinal Muscular Atrophy Type IIUnited States, Spain, Belgium, Germany, Netherlands, Poland, Italy, France, United Kingdom
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SanofiCompletedMultiple MyelomaFrance, Italy
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University of Turin, ItalyCompletedDiabetes Mellitus, Type 2 | Metabolic Syndrome | Hypertension,Essential | Catecholamine; Overproduction | Hypertensive Heart Disease | Catecholamine; Secretion | Hypertensive Kidney DiseaseItaly
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyFrance, United States, Israel, Spain, Switzerland, Germany, Canada, Japan, United Kingdom, Italy, Finland, Austria
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AGC Biologics S.p.A.Horizon 2020 - European CommissionTerminatedAcute Myeloid Leukemia | Multiple MyelomaItaly, Czechia
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IRCCS San RaffaeleAlleanza Contro il CancroRecruitingHigh Grade Glioma | High Grade MeningiomaItaly
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Ultragenyx Pharmaceutical IncTerminatedHereditary Inclusion Body Myopathy | GNE Myopathy | Distal Myopathy With Rimmed Vacuoles | Distal Myopathy, Nonaka Type | Quadriceps Sparing MyopathyUnited States, Canada, United Kingdom, Israel, Italy, Bulgaria, France
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University of Milano BicoccaComitato Maria Letizia Verga,ItalyRecruitingLymphoma, Non-Hodgkin | Leukemia, Myeloid, Acute | Leukemia, B-cell | Adrenoleukodystrophy | Lymphoma, Hodgkin | Thalassemia Major | Leukemia, T Cell | DrepanocytosisItaly
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Scholar Rock, Inc.Active, not recruitingNeuromuscular Diseases | Neuromuscular Manifestations | Atrophy | Muscular Atrophy | Spinal Muscular Atrophy | Muscular Atrophy, Spinal | Spinal Muscular Atrophy Type 3 | SMA | Spinal Muscular Atrophy Type 2 | Anti-myostatinUnited States, Germany, Belgium, Spain, United Kingdom, Netherlands, France, Italy, Poland
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Fondazione EMN Italy OnlusRecruiting
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rEVO BiologicsCompletedAntithrombin Deficiency, CongenitalFrance, United Kingdom, Germany, United States, Sweden, Italy
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Azienda Socio Sanitaria Territoriale degli Spedali...CompletedAtaxia | Multiple System Atrophy | Spinocerebellar Ataxias | Spinocerebellar Ataxia 3 | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Ataxia With Oculomotor Apraxia | CANVASItaly
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Helsinki University Central HospitalAssistance Publique - Hôpitaux de Paris; Universitaire Ziekenhuizen KU Leuven; Azienda Ospedaliera Universitaria Integrata Verona and other collaboratorsActive, not recruitingType A Aortic DissectionSpain, Belgium, Finland, United Kingdom, Germany, Italy, Czechia, France
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Pharvaris Netherlands B.V.Active, not recruitingHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsUnited States, Poland, Germany, Austria, Bulgaria, Canada, Ireland, Italy, United Kingdom
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Janssen Research & Development, LLCApproved for marketingRelapsed or Refractory Multiple MyelomaBrazil, Germany, Italy, Netherlands, Romania, Switzerland, United Kingdom
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Istituto Oncologico Veneto IRCCSBayerNot yet recruitingMeningioma, MalignantItaly
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Azienda Ospedaliera di PerugiaRecruitingCoronary Artery Disease | Diabetes Mellitus, Type 2 | Alzheimer DiseaseItaly
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IRCCS Policlinico S. MatteoRecruitingAL Amyloidosis | Monoclonal Gammopathy of Undetermined Significance | Smoldering Multiple MyelomaItaly
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Azienda Socio Sanitaria Territoriale degli Spedali...CompletedCerebellar Ataxia | Multiple System Atrophy | Spinocerebellar Ataxias | Spinocerebellar Degenerations | Spinocerebellar Ataxia 3 | Friedreich Ataxia | Spinocerebellar Ataxia Type 1 | Spinocerebellar Ataxia Type 2 | Ataxia, Spinocerebellar | Ataxia, Cerebellar | Ataxia With Oculomotor ApraxiaItaly
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University of WuerzburgUnknownMultiple MyelomaAustria, Germany, Italy
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University of Turin, ItalyCompletedMultiple MyelomaItaly
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Galapagos NVTerminatedAutosomal Dominant Polycystic Kidney DiseaseBelgium, Netherlands, Italy, Spain, Czechia, Germany, Poland
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European Myeloma NetworkJanssen, LPActive, not recruitingMultiple Myeloma | Extramedullary PlasmacytomaTurkey, Italy, Greece
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Association for Innovation and Biomedical Research...European Vision Institute Clinical Research NetworkActive, not recruitingDiabetes Mellitus, Type 2 | Retinal Disease | NPDR - Non Proliferative Diabetic RetinopathyFrance, Italy, Portugal
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Gruppo Italiano per lo Studio del Mieloma MultiploCompleted
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TME Pharma AGCompletedMultiple MyelomaAustria, France, Germany, Italy
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Tiziana MarangonWithdrawn
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AmgenCompletedMultiple MyelomaGreece, Italy, Netherlands
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European Myeloma NetworkSanofi; Amgen; EMN Research ItalyActive, not recruitingMultiple MyelomaCzechia, Germany, Greece, Italy, Netherlands, Norway, Spain
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Swiss Group for Clinical Cancer ResearchTerminatedMultiple MyelomaSwitzerland, Italy
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European Myeloma NetworkCompletedMultiple Myeloma | Hematologic MalignanciesSpain, Sweden, Germany, Italy
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)CompletedStage I Multiple Myeloma | Stage II Multiple Myeloma | Stage III Multiple Myeloma | Refractory Multiple MyelomaUnited States, Italy
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European Myeloma NetworkFondazione EMN Italy OnlusCompletedMultiple MyelomaNetherlands, Italy
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LMU KlinikumUniversity of Pisa; German Federal Ministry of Education and Research; European...RecruitingMitochondrial Diseases | MDS | Mitochondrial Myopathies | MELAS Syndrome | MIDD | Kearns-Sayre Syndrome | MERRF Syndrome | Barth Syndrome | Leigh Syndrome | MNGIE | LHON | Pearson Syndrome | NARP Syndrome | Coenzyme Q10 Deficiency | SANDO | SCAE | MIRAS | CPEOAustria, Germany, Italy
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EMN Research ItalyActive, not recruitingRelapsed Multiple MyelomaItaly
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University of IowaJohns Hopkins University; University of Colorado, Denver; King's College Hospital... and other collaboratorsRecruitingCharcot-Marie-Tooth Disease, Type Ia (Disorder) | HMSNUnited States, Italy, United Kingdom, Australia
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Bristol-Myers SquibbTerminatedMultiple MyelomaUnited States, Italy, France, Spain
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Pharvaris Netherlands B.V.CompletedHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsBulgaria, United States, Spain, Israel, Germany, Canada, Czechia, France, Hungary, Italy, Netherlands, Poland, United Kingdom
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Advice Pharma Group srlCompletedAcute Myeloid Leukemia | Multiple Myeloma | Hodgkin Lymphoma | Amyloidosis | Chronic Lymphocytic Leukemia | Chronic Myeloid Leukemia | Treatment Adherence | Myelodysplasia | Lymphocytic Lymphoma | Treatment Adherence and Compliance | T Cell Non-Hodgkin Lymphoma | B-cell Non Hodgkin Lymphoma | Solitary Plasmacytoma and other conditionsItaly
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Otsuka Pharmaceutical Development & Commercialization...CompletedAutosomal Dominant Polycystic Kidney Disease (ADPKD)Germany, Italy, Belgium, United Kingdom
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National Cancer Institute (NCI)CompletedMultiple Myeloma and Plasma Cell NeoplasmUnited States, Italy
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Glanzmann's DiseaseSpain, Bulgaria, Pakistan, Belgium, Germany, France, United Kingdom, Italy, Hungary, Netherlands, United States, Algeria, Austria, Sweden, Switzerland