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Clinical Trials on Congenital Muscular Dystrophy Type 1A in United Kingdom
Total 4065 results
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The Cleveland ClinicNational Eye Institute (NEI)CompletedRetinal Detachment | Epiretinal Membrane | Fuchs Endothelial Dystrophy | Macular HoleUnited States
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Eunice Kennedy Shriver National Institute of Child...National Institutes of Health Clinical Center (CC); National Institute of Neurological... and other collaboratorsActive, not recruitingGenetic DisorderUnited States
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Emma AitkenNHS Greater Glasgow and ClydeUnknownEnd Stage Renal DiseaseUnited Kingdom
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NHS Greater Glasgow and ClydeUnknownNeuropathic Pain | Arteriovenous FistulaeUnited Kingdom
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Bangor UniversityBetsi Cadwaladr University Health BoardCompleted
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NHS Greater Glasgow and ClydeUnknown
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Editas Medicine, Inc.Active, not recruitingRetinal Degeneration | Eye Diseases, Hereditary | Vision Disorders | Leber Congenital Amaurosis 10 | Inherited Retinal Dystrophies | Retinal Disease | Eye Disorders CongenitalUnited States
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University College, LondonRecruitingHereditary Sensory Neuropathy Type IUnited Kingdom
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The Lowy Medical Research Institute LimitedActive, not recruitingMacular Telangiectasia Type 2United States, United Kingdom
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Krystal Biotech, Inc.CompletedDystrophic Epidermolysis Bullosa | Recessive Dystrophic Epidermolysis Bullosa | Dominant Dystrophic Epidermolysis BullosaUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyUnited States, Israel, United Kingdom
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Foundation Fighting BlindnessRecruitingRetinitis Pigmentosa | Choroideremia | Usher Syndrome | Batten Disease | Leber Congenital Amaurosis | Goldmann-Favre Syndrome | Kearns-Sayre Syndrome | Retinal Disease | Bardet-Biedl Syndrome | Stargardt Disease | Cone Dystrophy | Retinoschisis | Achromatopsia | Gyrate Atrophy | Eye Diseases Hereditary | Bassen-Kornzweig... and other conditionsUnited States
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Krystal Biotech, Inc.RecruitingDystrophic Epidermolysis Bullosa | Recessive Dystrophic Epidermolysis Bullosa | Dominant Dystrophic Epidermolysis BullosaUnited States
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Imperial College LondonCompletedHereditary Haemorrhagic Telangiectasia (HHT)United Kingdom
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Newcastle-upon-Tyne Hospitals NHS TrustRecruitingX-linked Myotubular Myopathy | Centronuclear Myopathy | Myotubular Myopathy | Myotubular Myopathy 1 | Myotubular (Centronuclear) Myopathy | Centronuclear Myopathy, X-LinkedUnited Kingdom
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Cambridge University Hospitals NHS Foundation TrustCompletedSteal Syndrome | Arteriovenous Fistulas | Renal Failure, End-StageUnited Kingdom
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National Institute of Neurological Disorders and...RecruitingMuscular Dystrophy | Peripheral Neuropathy | Normal Physiology | Motor Neuron DisorderUnited States
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Barnsley HospitalCompletedType 2 Diabetes | Peripheral Vascular Disease | HypogonadismUnited Kingdom
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National Eye Institute (NEI)TerminatedInherited Retinal Degeneration | Inherited Ophthalmic DiseasesUnited States
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Astellas Gene TherapiesCompletedX-linked Myotubular MyopathyUnited States, France, United Kingdom, Canada, Germany
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The Leeds Teaching Hospitals NHS TrustNot yet recruitingPartial Anomalous Pulmonary Venous ConnectionUnited Kingdom
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The Cleveland ClinicNational Eye Institute (NEI)RecruitingRetinal Diseases | Retinal Detachment | Epiretinal Membrane | Fuchs Endothelial Dystrophy | Macular HoleUnited States
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Cambridge University Hospitals NHS Foundation TrustUnknownStroke | Osteoarthritis | Back Pain | Sciatica | Fibromyalgia | Complex Regional Pain Syndromes | Traumatic Brain InjuryUnited Kingdom
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Optos, PLCJohns Hopkins University; University of Southern CaliforniaCompletedAge-Related Macular Degeneration | Diabetic Retinopathy | Macular Edema | Retinal Vein Occlusion | Geographic Atrophy | Epiretinal Membrane | Macular Hole | Pattern Dystrophy of Macula | Central Serous RetinopathyUnited States
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Johns Hopkins UniversityCompletedBladder ExstrophyUnited States
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Astellas Gene TherapiesCompletedMales With X-linked Myotubular Myopathy (XLMTM)United States, United Kingdom
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Laminate Medical TechnologiesCompletedEnd Stage Renal Disease | Vascular AccessUnited Kingdom, Israel
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Connecticut Children's Medical CenterCompletedBladder ExstrophyUnited States
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Massachusetts General HospitalBeth Israel Deaconess Medical Center; Brigham and Women's Hospital; University...Recruiting
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University of ChicagoRecruitingMuscular Dystrophy | Arrhythmia | CardiomyopathyUnited States
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Thomas Jefferson UniversityOnconova Therapeutics, Inc.RecruitingRecessive Dystrophic Epidermolysis BullosaUnited States
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Stanford UniversityCompletedEpidermolysis Bullosa DystrophicaUnited States
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Stanford UniversityRecruitingEpidermolysis Bullosa DystrophicaUnited States
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University of Texas Southwestern Medical CenterActive, not recruitingArteriovenous MalformationsUnited States
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Stanford UniversityTerminatedEpidermolysis Bullosa DystrophicaUnited States
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King's College LondonCompletedMyelodysplastic Syndromes | Leukemia, Myeloid, AcuteUnited Kingdom
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University of Southern CaliforniaRecruitingRecessive Dystrophic Epidermolysis BullosaUnited States
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Abeona Therapeutics, IncNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedEpidermolysis Bullosa | Epidermolysis Bullosa DystrophicaUnited States
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University of Southern CaliforniaCompleted
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Phoenix Tissue Repair, Inc.Phoenix Tissue Repair, a BridgeBio companyCompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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Phoenix Tissue Repair, Inc.CompletedRecessive Dystrophic Epidermolysis BullosaUnited States
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Royal Brompton & Harefield NHS Foundation TrustGlaxoSmithKline; CORDA, The Heart CharityUnknownVascular Diseases | Hypertension | Diabetes Mellitus, Type 2United Kingdom
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Imperial College LondonTerminatedHereditary Haemorrhagic TelangiectasiaUnited Kingdom
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Phoenicis TherapeuticsNot yet recruitingDystrophic Epidermolysis BullosaUnited States
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Stanford UniversityCompletedEpidermolysis Bullosa | Epidermolysis Bullosa DystrophicaUnited States
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Krystal Biotech, Inc.Stanford UniversityWithdrawnDystrophic Epidermolysis Bullosa | DEB - Dystrophic Epidermolysis BullosaUnited States
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Columbia UniversityTerminatedEpidermolysis BullosaUnited States
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University College London HospitalsCompletedDistal Hereditary Motor Neuropathy, Type II | Distal Hereditary Motor Neuropathy, Type V | Distal Hereditary Motor Neuronopathy Type I | Distal Hereditary Motor Neuronopathy Type VIUnited Kingdom
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St. Joseph's Hospital and Medical Center, PhoenixTranslational Genomics Research Institute; The Joe Niekro FoundationActive, not recruiting
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Phoenix Tissue Repair, Inc.CompletedRecessive Dystrophic Epidermolysis BullosaUnited States