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Clinical Trials on Congenital Myasthenic Syndromes in United Kingdom
Total 16699 results
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Oregon Health and Science UniversityJacobus PharmaceuticalNo longer availableLambert-Eaton Myasthenic Syndrome (LEMS) | Congenital Myasthenia (CM)United States
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Ricardo MaselliCatalyst Pharmaceuticals, Inc.No longer availableCongenital Myasthenic SyndromeUnited States
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Mayo ClinicCompletedCongenital Myasthenic SyndromeUnited States
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argenxRecruitingCongenital Myasthenic SyndromeUnited States, Canada, France
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Catalyst Pharmaceuticals, Inc.CompletedMyasthenic Syndromes, CongenitalUnited States
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Lahey ClinicApproved for marketingLambert-Eaton Myasthenic Syndrome | Congenital Myasthenic SyndromeUnited States
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Catalyst Pharmaceuticals, Inc.No longer availableLambert-Eaton Myasthenic Syndrome | Congenital Myasthenic Syndrome | Nystagmus, AcquiredUnited States
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Vern C. Juel, M.D.No longer available
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University of Colorado, DenverApproved for marketingLambert Eaton Myasthenic SyndromeUnited States
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David P. Richman, MDJacobus PharmaceuticalNo longer available
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Jacobus PharmaceuticalCompletedLambert-Eaton Myasthenic Syndrome | Eaton-Lambert Myasthenic SyndromeUnited States
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Catalyst Pharmaceuticals, Inc.CompletedA Phase 3 Study of Amifampridine Phosphate in Patients With Lambert Eaton Myasthenic Syndrome (LEMS)Lambert Eaton Myasthenic SyndromeUnited States, Spain, Serbia, Russian Federation, Hungary, France, Germany, Poland
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Louis H. Weimer, MDNo longer availableLambert Eaton Myasthenic Syndrome (LEMS)United States
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The Cleveland ClinicNo longer availableLambert-Eaton Myasthenic SyndromeUnited States
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Catalyst Pharmaceuticals, Inc.CompletedLambert-Eaton Myasthenic SyndromeUnited States
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Vitaccess LtdargenxRecruiting
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argenxRecruitingGeneralized Myasthenia GravisUnited States, Netherlands, Belgium, Poland, United Kingdom
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Fred Hutchinson Cancer CenterActive, not recruitingMyasthenia Gravis | Neuromyelitis Optica | Autoimmune Disease | Chronic Inflammatory Demyelinating Polyneuropathy | Lambert Eaton Myasthenic Syndrome | Cerebellar Degeneration | Stiff Person Syndrome | Opsoclonus Myoclonus Syndrome | Neurologic Autoimmune Disease | Autologous Transplant Autoimmune | Multiple... and other conditionsUnited States
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Hoffmann-La RocheAspreva PharmaceuticalsCompletedMyasthenia Gravis GeneralisedFrance, Ukraine, Germany, United States, Italy, United Kingdom, Former Serbia and Montenegro
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GlaxoSmithKlineCompletedMyasthaenia GravisUnited States, Canada, Germany, Italy
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argenxRecruitingGeneralized Myasthenia GravisUnited Kingdom, Spain, United States, Austria, Germany, Belgium, Italy, Netherlands, France, Georgia, Poland, Canada
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UCB Biopharma SRLActive, not recruitingGeneralized Myasthenia GravisUnited States, Canada, Georgia, Germany, Italy, Japan, Poland, Serbia, Spain, United Kingdom
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Premaitha HealthCompletedClinical Evaluation of the IONA Test for Non-invasive Pre Natal Screening in Twin Pregnancies (TWIN)Down Syndrome | Patau Syndrome | Edward's SyndromeUnited Kingdom
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Barts & The London NHS TrustLiverpool Heart and Chest Hospital NHS Foundation Trust; Aortic Dissection...RecruitingMarfan Syndrome | Marfan Syndrome Cardiovascular ManifestationsUnited Kingdom
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Barts & The London NHS TrustLiverpool Heart and Chest Hospital NHS Foundation Trust; Aortic Dissection...CompletedMarfan Syndrome | Marfan Syndrome Cardiovascular ManifestationsUnited Kingdom
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Hoffmann-La RocheAspreva PharmaceuticalsCompletedMyasthenia Gravis, GeneralizedSpain, India, Ukraine, Canada, Germany, Russian Federation, United States, France, Mexico, Italy, United Kingdom, Israel, Netherlands, Former Serbia and Montenegro
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Momenta Pharmaceuticals, Inc.TerminatedGeneralized Myasthenia GravisUnited States, Belgium, Canada, Germany, Italy, Poland, Spain, United Kingdom
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COUR Pharmaceutical Development Company, Inc.RecruitingMyasthenia Gravis | Generalized Myasthenia | AChR Myasthenia Gravis | MuSK MGUnited States
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Cardiff UniversityCompleted
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Alexion Pharmaceuticals, Inc.CompletedMyasthenia Gravis | Myasthenia Gravis, Generalized | Myasthenia Gravis, Juvenile FormUnited States, Japan, Netherlands
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Alexion PharmaceuticalsCompletedRefractory Generalized Myasthenia GravisItaly, United Kingdom, Spain, Belgium, Turkey, Japan, United States, Netherlands, Korea, Republic of, Argentina, Hungary, Sweden, Denmark, Brazil, Czechia, Finland, Canada
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Ad scientiamRecruitingMyasthenia GravisUnited Kingdom, United States, Canada
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Momenta Pharmaceuticals, Inc.CompletedGeneralized Myasthenia GravisUnited States, Belgium, Canada, Germany, Italy, Poland, Spain, United Kingdom
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ProgenaBiomeRecruitingMyasthenia Gravis | Myasthenia Gravis, GeneralizedUnited States
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Alexion PharmaceuticalsWithdrawnGeneralized Myasthenia GravisUnited States
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argenxRecruiting
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University of OxfordOxford University Hospitals NHS TrustUnknown
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Myasthenia Gravis Rare Disease NetworkRecruitingMyasthenia Gravis | MuSK Myasthenia Gravis | MuSK MGUnited States
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University of Missouri-ColumbiaUniversity of Kansas Medical CenterRecruitingGeneralized Myasthenia GravisUnited States
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Catalyst Pharmaceuticals, Inc.Active, not recruitingMyasthenia Gravis, MuSKUnited States
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Great Ormond Street Hospital for Children NHS Foundation...Unknown
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Silence Therapeutics plcWithdrawnNon-transfusion-dependent Thalassemia | Low Risk Myelodysplastic SyndromeUnited Kingdom, Bulgaria
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University of VermontGenentech, Inc.Completed
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Dianthus TherapeuticsRecruitingMyasthenia Gravis, GeneralizedUnited States
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Ra Pharmaceuticals, Inc.Active, not recruitingGeneralized Myasthenia GravisUnited States, Canada, France, Germany, Italy, Japan, Norway, Poland, Spain, United Kingdom
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King's College LondonCompletedMyelodysplastic Syndromes | Leukemia, Myeloid, AcuteUnited Kingdom
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Ra Pharmaceuticals, Inc.CompletedMyasthenia Gravis, GeneralizedUnited States, Canada, France, Germany, Italy, Japan, Norway, Poland, Spain, United Kingdom
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UCB Biopharma SRLRecruitingGeneralized Myasthenia GravisItaly, United States, Korea, Republic of
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UCB Biopharma SRLCompletedGeneralized Myasthenia GravisUnited States, Belgium, Canada, Czechia, Denmark, France, Georgia, Germany, Hungary, Italy, Japan, Poland, Russian Federation, Serbia, Spain, Taiwan, United Kingdom