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Clinical Trials on Congenital Myotonic Dystrophy in Italy
Total 573 results
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Virginia Commonwealth UniversityRecruitingCongenital Myotonic Dystrophy | Childhood Myotonic Dystrophy | CDM | CHDMUnited States, Italy
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Virginia Commonwealth UniversityUniversity of Western Ontario, Canada, Children's Health Research Institute; Fondazione Serena Onlus - Centro Clinico NeMO MilanoRecruitingCongenital Myotonic DystrophyUnited States, Italy, Canada
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IRCCS Eugenio MedeaRecruiting
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Istituto Auxologico ItalianoFondazione Serena Onlus - Centro Clinico NeMO MilanoCompletedMyotonic Dystrophy 1Italy
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Dyne TherapeuticsRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, France, Netherlands, Italy, Germany, New Zealand
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University of Campania "Luigi Vanvitelli"RecruitingSudden Cardiac Death | Myotonic Dystrophy 1Italy
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Virginia Commonwealth UniversityRadboud University Medical Center; University of California, Los Angeles; University... and other collaboratorsRecruitingMyotonic Dystrophy 1United States, Netherlands, United Kingdom, New Zealand, Germany, Italy, Canada, France
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Fondazione Serena Onlus - Centro Clinico NeMO MilanoAzienda Ospedaliera Città della Salute e della Scienza di Torino; Fondazione... and other collaboratorsActive, not recruiting
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Richard Barohn, MDCompletedNon-Dystrophic Myotonia | MyotoniaUnited States, Canada, Italy, United Kingdom
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Istituto Ortopedico RizzoliCompletedBethlem Myopathy | Ullrich Congenital Muscular DystrophyItaly
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Catholic University of the Sacred HeartFondazione TelethonUnknownMyotonic Dystrophy | Sudden Cardiac DeathItaly
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IRCCS Eugenio MedeaRecruitingMuscular Dystrophies | Becker Muscular Dystrophy | Limb Girdle Muscular Dystrophy | Facio-Scapulo-Humeral DystrophyItaly
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Catholic University, ItalyUnknownDuchenne Muscular Dystrophy | Becker Muscular DystrophyItaly
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Parent Project, ItalyCompletedDuchenne Muscular Dystrophy (DMD)Italy
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Istituto Superiore di SanitàFondazione G.B. Bietti, IRCCS; Ospedale Pediatrico Bambin GesùRecruitingRetinitis Pigmentosa | Macular Dystrophy | Inherited Retinal DystrophyItaly
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Fondazione Policlinico Universitario Agostino Gemelli...Recruiting
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Politecnico di MilanoIRCCS Eugenio Medea; Villa Beretta Rehabilitation CenterCompletedMuscular Dystrophies | Muscular Dystrophy, Duchenne | Muscular Dystrophy, Becker | Muscular Dystrophy, Limb-Girdle Type 2Italy
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ItalfarmacoCompletedDuchenne Muscular Dystrophy (DMD)Italy
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IRCCS San RaffaeleRecruiting
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingStudy of Genotype and Phenotype Characterization in Duchenne Muscular Dystrophy With Small MutationsMuscular Dystrophy, DuchenneItaly
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Catholic University of the Sacred HeartUniversity of Padova; Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta; Azienda Ospedaliera San Giovanni Battista and other collaboratorsUnknown
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Fondazione G.B. Bietti, IRCCSRecruitingMacular Edema | Inherited Retinal Dystrophy | Laser RetinopathyItaly
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IRCCS San Camillo, Venezia, ItalyUniversita di Verona; Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico and other collaboratorsEnrolling by invitationCalpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2AItaly
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University of MessinaCompleted
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingDuchenne Muscular Dystrophy | Natural History | Motor Function; RetardationItaly
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ItalfarmacoCompletedBecker Muscular DystrophyNetherlands, Italy
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Netherlands, France, Italy
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ReveraGen BioPharma, Inc.Santhera PharmaceuticalsRecruitingBecker Muscular DystrophyUnited States, Italy
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ProQR TherapeuticsRecruitingEye Diseases | Neurologic Manifestations | Retinal Degeneration | Retinal Dystrophies | Sensation Disorders | Vision Disorders | Blindness | Leber Congenital Amaurosis | Leber Congenital Amaurosis 10 | Retinal Disease | Eye Disorders CongenitalBelgium, Brazil, Canada, Germany, Italy, Netherlands, United Kingdom
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular DystrophyUnited States, Italy, Netherlands
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular Dystrophy | Limb Girdle Muscular DystrophyUnited States, Denmark, Italy
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University of TriesteUnknownChoroidal Neovascularization Secondary to Pattern DystrophyItaly
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BioMarin PharmaceuticalCompletedDuchenne Muscular DystrophyBelgium, Netherlands, Italy, Sweden
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Great Ormond Street Hospital for Children NHS Foundation...Catholic University of the Sacred Heart; Università degli Studi di Ferrara; Universidad... and other collaboratorsRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyDenmark, France, Italy, Netherlands, Spain, United Kingdom
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyBelgium, France, Italy, United Kingdom
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyBelgium, Netherlands, Italy, Sweden
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Centre Hospitalier Universitaire de NiceRecruitingFacioscapulohumeral Muscular Dystrophy Type 2France, Italy, Spain
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyNetherlands, Belgium, Italy, Sweden
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aTyr Pharma, Inc.CompletedFacioscapulohumeral Muscular Dystrophy (FSHD)United States, France, Italy
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Great Ormond Street Hospital for Children NHS Foundation...Catholic University of the Sacred Heart; Università degli Studi di Ferrara; Universidad... and other collaboratorsRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyDenmark, France, Italy, Spain, United Kingdom, Netherlands
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Sarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyBelgium, France, Italy, United Kingdom
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EspeRare FoundationCompletedMuscular Dystrophy, DuchenneItaly, France, Spain, United Kingdom
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyUnited Kingdom, Italy, Belgium, Netherlands, France
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King's College LondonKing's College Hospital NHS Trust; Charles University, Czech Republic; Hopital... and other collaboratorsRecruitingJuvenile Myoclonic EpilepsyUnited States, Canada, Czechia, Denmark, Estonia, France, Italy, Norway, United Kingdom
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Hoffmann-La RocheActive, not recruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, United Kingdom, Italy, Denmark
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Sarepta Therapeutics, Inc.University College, London; Catholic University of the Sacred Heart; University... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited Kingdom, United States, France, Italy
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BioMarin PharmaceuticalTerminatedDuchenne Muscular DystrophyBelgium, Netherlands, France, United Kingdom, Italy
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ITAB - Institute for Advanced Biomedical TechnologiesItalian Society of CardiologyCompletedCongenital Coronary Artery AbnormalityItaly
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Cooperative International Neuromuscular Research...Washington University School of Medicine; Children's National Research Institute and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Australia, Italy
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.CompletedDuchenne Muscular DystrophySpain, United States, Russian Federation, Italy, China, Turkey