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- US Clinical Trials Registry
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Clinical Trials on Congenital Myotonic Dystrophy
Total 10148 results
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GlaxoSmithKlineCompletedMuscular DystrophiesGermany, Belgium, Turkey, Netherlands, Spain, Israel, Australia, France, United Kingdom
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University of MessinaCompleted
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Cedars-Sinai Medical CenterCompleted
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Cooperative International Neuromuscular Research...United States Department of DefenseTerminated
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Cedars-Sinai Medical CenterMuscular Dystrophy AssociationCompleted
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Rigshospitalet, DenmarkGlostrup University Hospital, CopenhagenCompletedBecker Muscular DystrophyDenmark
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Cooperative International Neuromuscular Research...Washington University School of Medicine; Children's National Research Institute and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Australia, Italy
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Santhera PharmaceuticalsCompletedDuchenne Muscular DystrophyBelgium
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Assistance Publique - Hôpitaux de ParisCompletedMuscular Dystrophy, DuchenneFrance
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National Center for Research Resources (NCRR)Children's National Research InstituteCompletedMuscular Dystrophy, DuchenneUnited States
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University of TurkuUnknownUnverricht-Lundborg SyndromeFinland
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Medical University of ViennaCompletedFuchs' Endothelial DystrophyAustria
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Centre Hospitalier Régional Metz-ThionvilleCompletedEndothelial Corneal Dystrophy
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University Hospital, GrenobleRecruitingArthrogryposis Multiplex Congenita (AMC)France
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BioMarin PharmaceuticalRecruitingDuchenne Muscular DystrophySpain, United Kingdom
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Solid Biosciences Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Hoffmann-La RocheSarepta Therapeutics, Inc.Recruiting
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West China HospitalRecruiting
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Hacettepe UniversityNot yet recruitingDuchenne Muscular DystrophyTurkey
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Edgewise Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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PepGen IncRecruitingDuchenne Muscular DystrophyCanada
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NS Pharma, Inc.Nippon Shinyaku Co., Ltd.RecruitingDuchenne Muscular DystrophyUnited States
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Beni-Suef UniversityNot yet recruitingDuchenne Muscular Dystrophy
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingStudy of Genotype and Phenotype Characterization in Duchenne Muscular Dystrophy With Small MutationsMuscular Dystrophy, DuchenneItaly
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Muş Alparlan UniversityHacettepe UniversityRecruitingDuchenne Muscular DystrophyTurkey
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Edgewise Therapeutics, Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Edgewise Therapeutics, Inc.Medpace, Inc.; SYSNAV; ImagingNMDRecruitingBecker Muscular DystrophyUnited States, Netherlands, United Kingdom
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ReveraGen BioPharma, Inc.Santhera PharmaceuticalsRecruitingBecker Muscular DystrophyUnited States, Italy
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Taiho Pharmaceutical Co., Ltd.RecruitingDuchenne Muscular DystrophyJapan
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GenethonRecruiting
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Halic UniversityIstanbul University; Biruni UniversityCompletedDuchenne Muscular DystrophyTurkey
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Edgewise Therapeutics, Inc.Medpace, Inc.CompletedBecker Muscular DystrophyUnited States
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PfizerActive, not recruitingMuscular Dystrophy, DuchenneUnited States, Australia
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Sarepta Therapeutics, Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States, Korea, Republic of, Italy, United Kingdom, Canada, Poland, Spain, France, Germany, Belgium, Australia, Czechia, Serbia, Greece, Argentina, Bulgaria, Denmark, Hungary, India, Ireland, Israel, Mexico, Russian Federation, ...
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Sarepta Therapeutics, Inc.Hansa Biopharma ABActive, not recruitingDuchenne Muscular DystrophySpain
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Wave Life Sciences Ltd.Active, not recruitingDuchenne Muscular DystrophyJordan, United Kingdom
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Hacettepe UniversityCompleted
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Çağtay MadenCompleted
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Hacettepe UniversityCompleted
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FibroGenActive, not recruitingDuchenne Muscular DystrophyUnited States, Spain, Canada, Australia, China, Italy, Belgium, France, Netherlands, Austria, United Kingdom
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Sarepta Therapeutics, Inc.Hoffmann-La RocheActive, not recruitingDuchenne Muscular DystrophyUnited States, Japan, Taiwan, Belgium, Spain, Germany, Hong Kong, Italy, United Kingdom
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ItalfarmacoCromsourceEnrolling by invitationDuchenne Muscular DystrophySpain, United States, Canada, Belgium, France, Israel, Italy, Netherlands, Serbia, Germany, United Kingdom
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Kevin FlaniganSarepta Therapeutics, Inc.Completed
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Solid Biosciences Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States
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Kevin FlaniganActive, not recruitingDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyBelgium, France, Italy, United Kingdom
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Solid Biosciences Inc.CompletedDuchenne Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.Hoffmann-La RocheEnrolling by invitation
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Megan WaldropAudentes TherapeuticsActive, not recruitingDuchenne Muscular DystrophyUnited States