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Clinical Trials on Congenital Bone Marrow Failure Syndromes
Total 12505 results
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Peking Union Medical College HospitalNot yet recruiting
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Bing HanNot yet recruiting
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King's College Hospital NHS TrustRecruiting
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Novartis PharmaceuticalsCompleted
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The Cleveland ClinicCompletedAplastic AnemiaUnited States
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PfizerCompleted
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Kyowa Kirin Co., Ltd.CompletedAplastic AnemiaJapan, Korea, Republic of
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Safaa AA KhaledAssiut UniversityCompletedAplastic AnemiaEgypt
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Shengyun LinUnknown
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Shengyun LinCompleted
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Xiaofan ZhuUnknown
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The Korean Society of Pediatric Hematology OncologyUnknown
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M.D. Anderson Cancer CenterCompletedAplastic AnemiaUnited States
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Guangzhou General Hospital of Guangzhou Military...Guangzhou Municipal Twelfth People's Hospital; Guangdong Prevention and Treatment...Unknown
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI)Terminated
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Fred Hutchinson Cancer CenterUniversity of California, Los Angeles; Oregon Health and Science University; Ohio... and other collaboratorsCompletedAnemia, AplasticUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAplastic AnemiaUnited States
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University of FloridaLive Like Bella Pediatric Cancer ResearchCompletedCommon Variable Immunodeficiency | Severe Combined Immunodeficiency | Sickle Cell Disease | Hurler Syndrome | Chronic Granulomatous Disease | Thalassemia | Wiskott-Aldrich Syndrome | Adrenoleukodystrophy | X-linked Lymphoproliferative Disease | Diamond Blackfan Anemia | Bone Marrow Failure Syndrome | Hemophagocytic... and other conditionsUnited States
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Peking Union Medical College HospitalNot yet recruitingAplastic AnemiaChina
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B. HöchsmannRecruitingAnemia, AplasticGermany
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Kyowa Kirin Korea Co., Ltd.CompletedAplastic AnemiaKorea, Republic of
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Kyowa Kirin Co., Ltd.Enrolling by invitation
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Kyowa Kirin Co., Ltd.Completed
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Kyowa Kirin Co., Ltd.Completed
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Medical College of WisconsinNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute... and other collaboratorsCompletedAnemia, AplasticUnited States
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Asociacion Instituto BiodonostiaActive, not recruiting
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The Cleveland ClinicAstellas Pharma US, Inc.Terminated
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Hebei Medical UniversityUnknown
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Mayo ClinicCompletedAnemia, AplasticUnited States
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Jinan Military General HospitalGuangzhou First People's Hospital; Shengjing Hospital; Qingdao University; Institute... and other collaboratorsUnknown
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Tianjin Medical University General HospitalUnknown
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Yizhou ZhengUnknown
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...TerminatedAplastic AnemiaUnited States
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National Institute of Blood Disease Center, PakistanUnknown
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National Heart, Lung, and Blood Institute (NHLBI)CompletedAnemia, Aplastic | Blood Disease
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Shandong UniversityNational Natural Science Foundation of ChinaUnknown
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St. Jude Children's Research HospitalCompleted
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Office of Rare Diseases (ORD)Rare Diseases Clinical Research NetworkUnknown
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Novartis PharmaceuticalsCompleted
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Columbia UniversityCompletedMyelodysplastic Syndromes | Sickle Cell Disease | Aplastic Anemia | Transfusional Iron Overload | Thalassemia MajorUnited States
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Roswell Park Cancer InstituteCompletedLymphoma | Myelodysplastic Syndromes | Leukemia | Chronic Myeloproliferative Disorders | Fanconi Anemia | Multiple Myeloma and Plasma Cell Neoplasm | Myelodysplastic/Myeloproliferative Diseases | Aplastic AnemiaUnited States
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Sidney Kimmel Comprehensive Cancer Center at Johns...RecruitingPrimary Immune Deficiency Disorder | Bone Marrow Failure | Immune Deficiency DiseaseUnited States
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University Hospital, LilleWithdrawn
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Assiut UniversityCompleted
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHematologic Diseases | Anemia, Aplastic | Pancytopenia | Blood Disease
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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Peking Union Medical College HospitalNot yet recruitingDrug Effect | Aplastic AnemiaChina
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European Society for Blood and Marrow TransplantationCHUGAI sanofi-aventisTerminatedAplastic AnaemiaFrance, Netherlands, Germany, United Kingdom, Switzerland, Italy, Sweden, Greece, Czechia
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Peking Union Medical College HospitalCompletedDrug Effect | Aplastic AnemiaChina