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- US Clinical Trials Registry
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Clinical Trials on Congenital Myasthenic Syndrome
Total 40721 results
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Catalyst Pharmaceuticals, Inc.CompletedMyasthenia Gravis, GeneralizedUnited States
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Instituto Nacional de Ciencias Medicas y Nutricion...CompletedMyasthenia Gravis, Thymectomy
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University Hospital FreiburgCompletedMyelodysplastic Syndromes | Fanconi Anemia | Dyskeratosis Congenita | Pearson Marrow-pancreas Syndrome | Shwachman-diamond SyndromeSpain, Germany, Switzerland, Austria, Netherlands, Italy, Czech Republic, Belgium, Denmark, Ireland
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Fondation Ophtalmologique Adolphe de RothschildCompleted
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Shanghai Jiaolian Drug Research and Development...Shanghai Pharmaceuticals Holding Co., LtdNot yet recruitingGeneralized Myasthenia GravisChina
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XiaoYong LiuRecruitingCytomegalovirus Infections | Ocular Myasthenia GravisChina
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Mansoura UniversityCompletedMyasthenia Gravis | Guillain-Barre SyndromeEgypt
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Beijing Tongren HospitalCompletedMyasthenia Gravis, Ocular | Gene PolymorphismChina
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University of California, San FranciscoNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Leukemia | Congenital Amegakaryocytic Thrombocytopenia | Severe Congenital NeutropeniaUnited States
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Ting Chang, MDNot yet recruiting
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Huashan HospitalChina Alliance for Rare Diseases; National Center for Neurological Disorders... and other collaboratorsRecruiting
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Jagiellonian UniversityRecruiting
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University of ManchesterKing's College Hospital NHS Trust; Cardiff University; University College London... and other collaboratorsNot yet recruitingMyasthenia Gravis
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Huashan HospitalRecruiting
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Da, Yuwei, M.D.Recruiting
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Yale UniversityRecruiting
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SanofiTerminatedMyasthenia GravisItaly, Hungary, United States, Canada, China, Japan, Poland, Spain, United Kingdom
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Yale UniversityNational Institute of Neurological Disorders and Stroke (NINDS); National Center...CompletedMyasthenia GravisUnited States
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Yonsei UniversityCompleted
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First Affiliated Hospital, Sun Yat-Sen UniversityCompleted
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UCB Biopharma S.P.R.L.CompletedMyasthenia GravisUnited States, Belgium, Canada, Czechia, Denmark, Germany, Spain
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Rigshospitalet, DenmarkWithdrawn
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University of AarhusUnknownMyasthenia GravisDenmark
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Alexion PharmaceuticalsTerminatedMyasthenia GravisUnited States, Canada, United Kingdom
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CuraVacUniversity Hospital, Antwerp; Leiden University Medical Center; AepodiaCompletedMyasthenia GravisBelgium
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First Affiliated Hospital, Sun Yat-Sen UniversityUnknownMyasthenia GravisChina
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Qualitix Clinical Research Co., Ltd.Unknown
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Emory UniversityChildren's Healthcare of AtlantaTerminatedSickle Cell Disease | Fanconi Anemia | Thalassemia | Severe Congenital Neutropenia | Wiskott-Aldrich Syndrome | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Glanzmann Thrombasthenia | Leukocyte Adhesion Deficiency | Dyskeratosis-congenita | Chediak-Higashi Syndrome | Chronic-granulomatous Disease | Schwachman-Diamond...United States
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Universiti Putra MalaysiaEnrolling by invitationExperimental MyastheniaChina
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Universiti Putra MalaysiaCompletedExperimental MyastheniaChina
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Assistance Publique - Hôpitaux de ParisRecruitingOndine Syndrome | Congenital Central Hypoventilation Syndrome (CCHS)France
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ZS AssociatesUniversity of California, San FranciscoRecruitingNeuromuscular Diseases | Neuromuscular Manifestations | Myasthenia GravisUnited States
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Hacettepe UniversityRecruiting
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Yale UniversityNational Institute of Neurological Disorders and Stroke (NINDS); National Center...RecruitingMyasthenia GravisUnited States
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Uppsala UniversityRecruitingMyasthenia GravisSweden
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Ad scientiamRecruitingMyasthenia GravisUnited States, France
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Harbour BioMed (Guangzhou) Co. Ltd.Not yet recruiting
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Assiut UniversityNot yet recruitingMyasthenia Gravis
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Janssen Research & Development, LLCRecruitingMyasthenia GravisUnited States, Japan, Netherlands, Poland
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Janssen Research & Development, LLCRecruitingMyasthenia GravisUnited States, Korea, Republic of, Japan, Taiwan, Denmark, Germany, Czechia, China, Spain, Belgium, Canada, Mexico, Poland, Italy, France, Australia, Sweden
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Da, Yuwei, M.D.RecruitingMyasthenia GravisChina
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DAS-MG, IncRecruitingMyasthenia GravisUnited States
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Immunovant Sciences GmbHCompleted
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First Affiliated Hospital of Jinan UniversityEnrolling by invitationMyasthenia GravisChina
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TakedaCompletedMyasthenia GravisUnited States, Spain, Canada, Serbia, Italy, Poland
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doc.ai incUCB Biopharma SRLCompletedMyasthenia GravisUnited States
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Rigshospitalet, DenmarkCompleted
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Grifols Therapeutics LLCCompletedMyasthenia GravisUnited States, Belgium, Czechia, Estonia, Canada, France, Germany, Hungary, Poland, Lithuania
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Hacettepe UniversityCompletedMyasthenia GravisTurkey
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Yale UniversityNational Institute of Neurological Disorders and Stroke (NINDS)Completed