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Clinical Trials on Congenital Myotonic Dystrophy
Total 10232 results
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CENTOGENE GmbH RostockTerminatedNephritis, Hereditary | Hematuria-Nephropathy-Deafness SyndromeIndia, Sri Lanka, Albania, Georgia, Lithuania, Pakistan, Romania
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Kerecis Ltd.Active, not recruiting
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Dana-Farber Cancer InstituteNational Cancer Institute (NCI); Wyeth is now a wholly owned subsidiary of... and other collaboratorsCompletedTuberous Sclerosis | Nonmalignant Neoplasm | Lymphangioleimyomatosis | Kidney AngiomyolipomaUnited States
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Stanford UniversityCompletedEpidermolysis Bullosa Simplex | Epidermolysis Bullosa Simplex Kobner | Weber-Cockayne SyndromeUnited States
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PellePharm, Inc.CompletedBasal Cell Nevus SyndromeUnited States, Spain, Germany, United Kingdom, Italy, France, Belgium, Canada, Denmark, Netherlands
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University of OklahomaOU Medical CenterCompletedInfant, Premature, Diseases | Cholestasis | Gastroschisis | Intestinal Atresia | Short Bowel Syndrome | Cholestasis of Parenteral Nutrition | Total Parenteral Nutrition-induced CholestasisUnited States
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Fondazione TelethonUnknownUsher Syndrome, Type 1BItaly, Netherlands, Spain
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University of South FloridaNational Institute of Neurological Disorders and Stroke (NINDS); University... and other collaboratorsCompletedCarpal Tunnel Syndrome | Charcot-Marie-Tooth Disease | Inherited Peripheral NeuropathyUnited States
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Novo Nordisk A/SCompletedHealthy | Prader-Willi Syndrome | Genetic Disorder | Growth Disorder | Idiopathic Short StatureUnited States
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Chang Gung Memorial HospitalUnknownSurgery | Mandibular Prognathism | Injury of Trigeminal NerveTaiwan
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Cantonal Hospital GraubuendenUniversity of ZurichNot yet recruitingAutosomal Dominant Polycystic Kidney DiseaseSwitzerland
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Rege Nephro Co., Ltd.RecruitingAutosomal Dominant Polycystic Kidney Disease (ADPKD)Japan
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Children's Health IrelandBelfast Health and Social Care Trust; University of Edinburgh; University Hospital... and other collaboratorsRecruitingQuality of Life | Obstructive Sleep Apnea | Down Syndrome | Behavior | Adherence, TreatmentUnited Kingdom, Ireland
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Institut National de la Santé Et de la Recherche...Recruiting
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Maxima Medical CenterRecruitingChronic Pain Syndrome | Nerve Entrapment Syndrome | Anterior Cutaneous Nerve Entrapment SyndromeNetherlands
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New York Institute of TechnologyRecruitingPain, Chronic | Ehlers-Danlos SyndromeUnited States
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Palvella Therapeutics, Inc.RecruitingBCCs in Gorlin Syndrome PatientsUnited States, United Kingdom
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingAutosomal Dominant Polycystic Kidney DiseaseUnited States
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University Hospital, BrestRecruiting
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Montefiore Medical CenterTerminatedAnemia, Sickle Cell | Nocturnal EnuresisUnited States
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Semnan University of Medical SciencesTerminatedPolycystic Ovary Syndrome | Hyperandrogenism
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National Human Genome Research Institute (NHGRI)CompletedPain | Anxiety | Sickle Cell Disease | Health Care Utilization | IsolationUnited States
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University of NebraskaCompletedKidney Failure, ChronicUnited States
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Weill Medical College of Cornell UniversityThe Rogosin InstituteEnrolling by invitationAutosomal Dominant Polycystic Kidney DiseaseUnited States
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NYU Langone HealthCompletedSystemic Lupus Erythematosus | Congenital Heart Block | Sjogren's Syndrome | Neonatal LupusUnited States
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Novartis PharmaceuticalsCompletedSickle Cell Disease (SCD)United Kingdom, Spain, Greece, Brazil, Turkey, France, United States, Netherlands, Lebanon, Ireland, Panama
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University of California, San FranciscoCalifornia Institute for Regenerative Medicine (CIRM)Enrolling by invitationHemoglobinopathies | Alpha Thalassemia Major | Thalassemia Major | Fetal Hydrops | Hemoglobinopathy; With Thalassemia | Fetal Anemia | Alpha; Thalassemia | Thalassemia Alpha | A-ThalassemiaUnited States
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Bispebjerg HospitalCompletedBrain Neoplasms | Cerebral Hemorrhage | Intracranial Arteriovenous Malformations | Intracranial Hemorrhage, HypertensiveDenmark
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UCSF Benioff Children's Hospital OaklandGenentech, Inc.CompletedBasal Cell Nevus Syndrome | Gorlin SyndromeUnited States
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Hospices Civils de LyonCompletedAutism Spectrum Disorder | Williams Beuren Syndrome
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Universitair Ziekenhuis BrusselUnknownSleep DisorderBelgium
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Pharnext SACompletedCharcot-Marie-Tooth Disease | Hereditary Neuropathy With Liability to Pressure Palsies | Genetic DisordersFrance
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Children's Hospital of PhiladelphiaCompletedObstructive Sleep Apnea Syndrome | Down SyndromeUnited States
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University of OklahomaCompletedCerebral Palsy | Spinal Muscular Atrophy | Arthrogryposis | Other Central Nervous System or Musculoskeletal DisordersUnited States
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University of RochesterCompletedAndrogen Excess | Polycystic Ovarian Syndrome (PCOS) | Irregular Menstrual CyclesUnited States
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Imperial College LondonUnknownAsthma | COPD | Hereditary Hemorrhagic Telangiectasia | Pulmonary Arteriovenous Malformations
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Hadassah Medical OrganizationUnknownBrittle Cornea Syndrome | Ehlers-Danlos Syndrome Type 6Israel
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Mario Negri Institute for Pharmacological ResearchNot yet recruiting
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UMC UtrechtKarolinska University Hospital; Erasmus Medical Center; Great Ormond Street Hospital... and other collaboratorsNot yet recruitingOesophageal Atresia | Tracheomalacia | Oesophageal Atresia With Tracheo-Oesophageal Fistula
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University Health Network, TorontoNot yet recruitingIrritable Bowel Syndrome | Gastrointestinal Dysfunction | Ehlers-Danlos Syndrome | Hypermobility SyndromeCanada
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PYC TherapeuticsRecruitingOptic Atrophies, Hereditary | Autosomal Dominant Optic Atrophy | Optic Atrophy, Autosomal Dominant | Kjer Optic AtrophyAustralia
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Brugmann University HospitalRecruitingChronic Kidney DiseasesBelgium
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Regulus Therapeutics Inc.RecruitingPolycystic Kidney, Autosomal Dominant | Autosomal Dominant Polycystic Kidney Disease | ADPKDUnited States
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University Hospital Southampton NHS Foundation...University of Southampton; NeoKare Nutrition LtdRecruitingAnorectal Malformations | Gastroschisis | Hirschsprung Disease | Volvulus | Meconium Ileus | Intestinal Perforation | Preterm | NEC | Cows Milk Allergy | Atresia, Intestinal | ExomphalosUnited Kingdom
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Boston Children's HospitalCureAP4 FoundationRecruitingHereditary Spastic Paraplegia | SPG50 | SPG47 | SPG51 | SPG52 | AP4-related Hereditary Spastic Paraplegia | Early Onset Hereditary Spastic Paraplegia | SPG4 | SPG3A | SPG15 | SPG11United States
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University of VirginiaRecruitingRelative Contributions of Predictors of Hyperandrogenism in Older vs. Young Women With PCOS (SHK001)Polycystic Ovary SyndromeUnited States
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University Medical Centre LjubljanaSlovenian Research AgencyRecruitingPeripheral Nervous System Diseases | Nerve Compression Syndromes | Cubital Tunnel SyndromeSlovenia
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Virginia Polytechnic Institute and State UniversityRecruitingCerebral Palsy | Microcephaly | Acquired Brain Injury | Autism | Trauma, Brain | Neuromotor Impairments | Pediatric StrokeUnited States
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University of California, San FranciscoUniversity of Chicago; National Institute of Neurological Disorders and Stroke... and other collaboratorsRecruitingCerebral Cavernous Malformations | Cavernous Angioma, Familial | Cerebral Cavernous HemangiomaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHypertension | Cardiovascular Disease | Williams Syndrome | Multisystem Developmental Disorder | Elastin Gene DeletionUnited States