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Clinical Trials on Coproporphyria, Hereditary in Japan
Total 56 results
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Alnylam PharmaceuticalsCompletedAcute Hepatic Porphyria | Acute Intermittent Porphyria | Porphyria, Acute Intermittent | Acute Porphyria | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP) | ALA Dehydratase Deficient Porphyria (ADP)United States, Spain, United Kingdom, Korea, Republic of, Australia, Bulgaria, Canada, Denmark, Finland, France, Germany, Italy, Japan, Mexico, Netherlands, Poland, Sweden, Taiwan
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TakedaRecruitingHereditary Angioedema (HAE)Japan
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TakedaRecruitingHereditary Angioedema (HAE)Japan
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ShireCompletedHereditary Angioedema (HAE)Japan
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TakedaCompletedHereditary AngioedemaJapan
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BioCryst PharmaceuticalsCompletedHereditary Angioedema, HAEJapan
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Astellas Pharma IncCompleted
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Janssen Pharmaceutical K.K.CompletedX-Linked Retinitis PigmentosaJapan
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Janssen Pharmaceutical K.K.RecruitingX-Linked Retinitis PigmentosaJapan
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ShireCompleted
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Astellas Pharma IncCompleted
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TakedaCompletedHereditary AngioedemaJapan
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Tohoku UniversityCompletedHereditary Inclusion Body Myopathy | Nonaka MyopathyJapan
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NobelpharmaCompletedGNE Myopathy | Nonaka Disease | Distal Myopathy With Rimmed Vacuoles (DMRV) | Hereditary Inclusion Body Myopathy (hIBM)Japan
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ShireTakedaCompleted
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ShireCompletedHereditary Angioedema (HAE)Japan
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NobelpharmaCompletedPlaque | Tuberous Sclerosis | Angiofibroma | Hypomelanotic MaculeJapan
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NobelpharmaCompletedPlaque | Tuberous Sclerosis | Angiofibroma | Hypomelanotic MaculeJapan
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Mitsubishi Tanabe Pharma CorporationCompletedBehcet Syndrome | Behcet's Disease | Neuro-Behcet's DiseaseJapan
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CSL BehringCompletedHereditary AngioedemaUnited States, Germany, Japan, Hungary, Canada, Netherlands, Israel
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CENTOGENE GmbH RostockCompletedAbdominal Pain | Functional Abdominal PainUnited Kingdom, Germany, Turkey, Poland, Italy, Japan
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NobelpharmaTerminated
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NobelpharmaActive, not recruitingTuberous Sclerosis ComplexJapan
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Novartis PharmaceuticalsCompletedPeriodic Fevers SyndromeJapan
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KalVista Pharmaceuticals, Ltd.RecruitingHereditary AngioedemaUnited States, Bulgaria, France, Greece, Israel, Netherlands, Spain, United Kingdom, Australia, Germany, South Africa, Slovakia, Austria, New Zealand, Romania, Canada, Japan
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KalVista Pharmaceuticals, Ltd.CompletedHereditary AngioedemaUnited States, Australia, Bulgaria, Canada, France, Germany, Greece, Hungary, Israel, Italy, Japan, Netherlands, New Zealand, North Macedonia, Poland, Portugal, Puerto Rico, Romania, Slovakia, Spain, United Kingdom
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CSL BehringActive, not recruitingHereditary AngioedemaAustralia, Canada, United States, New Zealand, Germany, Hong Kong, Netherlands, Taiwan, Czechia, Israel, Hungary, Japan, Russian Federation, Spain
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KalVista Pharmaceuticals, Ltd.RecruitingHereditary AngioedemaUnited States, Bulgaria, France, Greece, Hungary, Israel, Italy, Netherlands, New Zealand, North Macedonia, Poland, Spain, United Kingdom, Australia, Germany, South Africa, Austria, Portugal, Slovakia, Romania, Canada, Saudi Arabia, Japa...
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Novartis PharmaceuticalsCompletedFamilial Cold Autoinflammatory Syndrome | Muckle-Wells Syndrome | Neonatal Onset Multisystem Inflammatory Disease | Cryopyrin-associated Periodic SyndromesJapan
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R-Tech Ueno, Ltd.TerminatedRetinitis PigmentosaJapan
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ShireTakeda Development Center Americas, Inc.CompletedAngioedemaUnited States, France, Netherlands, Spain, Hungary, Italy, Canada, Poland, Japan, Germany
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Baxalta now part of ShireCompletedHereditary Thrombotic Thrombocytopenic Purpura (TTP)United States, Germany, United Kingdom, Switzerland, Austria, Japan, Poland
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Clementia Pharmaceuticals Inc.TerminatedExostoses, Multiple HereditaryUnited States, Spain, Canada, Japan, Italy, Portugal, United Kingdom, Turkey, Australia, Belgium, France, Netherlands
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AbbVie (prior sponsor, Abbott)Eisai Co., Ltd.CompletedIntestinal Behçet's DiseaseJapan
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ShireCompletedMetachromatic Leukodystrophy (MLD)Australia, Denmark, Japan, France, Germany
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TakedaTakeda Development Center Americas, Inc.CompletedAngioedemaUnited States, Spain, Netherlands, Hungary, Italy, Canada, Germany, France, Japan, Poland
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Novartis PharmaceuticalsCompletedHereditary Periodic FeversBelgium, Italy, Japan, Russian Federation, Turkey, Spain, Germany, United Kingdom, France, United States, Ireland, Israel, Canada, Hungary, Netherlands, Switzerland
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid PolyneuropathiesUnited States, Canada, Argentina, Australia, Bulgaria, Cyprus, Italy, Japan, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Germany, France, Brazil, Turkey, Korea, Republic of, Taiwan, United Kingdom
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Ionis Pharmaceuticals, Inc.RecruitingAlexander DiseaseUnited States, United Kingdom, Australia, Canada, Israel, Italy, Japan, Netherlands
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AstraZenecaMerck Sharp & Dohme LLCActive, not recruitingNeurofibromatosis Type 1United States, Spain, Germany, Netherlands, Russian Federation, Italy, Japan
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ShireTakeda Development Center Americas, Inc.Active, not recruitingMetachromatic Leukodystrophy (MLD)Denmark, Germany, Japan, Australia, France, Brazil, Czechia
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Chugai PharmaceuticalNot yet recruitingAntiphospholipid Syndrome (APS) | Immune Thrombocytopenia (ITP) | Dermatomyositis (DM) | Bullous Pemphigoid (BP) | Behçet's Syndrome (BS) | Immune-mediated Necrotizing Myopathy (IMNM)United States, Japan
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Hoffmann-La RocheRecruitingThyroid Eye Disease | TEDJapan, Australia, Singapore, United States, Argentina, Germany, Italy, Hong Kong
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ShireTerminatedMetabolic Diseases | Brain Diseases | Central Nervous System Diseases | Nervous System Diseases | Demyelinating Diseases | Genetic Diseases, Inborn | Metabolism, Inborn Errors | Lysosomal Storage Diseases | Lipid Metabolism Disorders | Sphingolipidoses | Hereditary Central Nervous System Demyelinating Diseases and other conditionsUnited States, Denmark, France, Argentina, Belgium, Brazil, Canada, Germany, Japan, Turkey
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Immunovant Sciences GmbHRecruitingThyroid Eye DiseaseUnited States, Italy, Poland, United Kingdom, Canada, Israel, Germany, Japan
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis | Amyloidosis, HereditaryUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Cyprus, France, Germany, Greece, Italy, Japan, Korea, Republic of, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Taiwan, United Kingdom
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AstraZenecaMerck Sharp & Dohme LLCActive, not recruitingNeurofibromatosis 1 | Plexiform Neurofibroma (PN)United States, Canada, France, Italy, Germany, China, United Kingdom, Spain, Japan, Russian Federation, Australia, Poland, Brazil
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ShireTakeda Development Center Americas, Inc.Active, not recruitingMetachromatic Leukodystrophy (MLD)United States, Canada, Belgium, Israel, Netherlands, United Kingdom, Germany, Spain, Japan, Brazil, Argentina, France, Greece, Italy
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AmgenCompletedBehçet's SyndromeUnited States, Korea, Republic of, Israel, Italy, Turkey, France, Germany, Greece, Lebanon, Japan