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Clinical Trials on Corneal Dystrophies, Hereditary in New Zealand
Total 603 results
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AllerganCompletedDry Eye Disease (DED)United States
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PfizerCompletedEye Diseases | Macular Degeneration | Retinal Degeneration | Age-Related Maculopathies | Age-Related MaculopathyUnited States
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedFacioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
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Avidity Biosciences, Inc.Active, not recruitingNervous System Diseases | Genetic Diseases, Inborn | Musculoskeletal Diseases | Muscular Diseases | Neuromuscular Diseases | Neurodegenerative Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Heredodegenerative Disorders, Nervous System | Myotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy... and other conditionsUnited States
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Clementia Pharmaceuticals Inc.TerminatedExostoses, Multiple HereditaryUnited States, Spain, Canada, Japan, Italy, Portugal, United Kingdom, Turkey, Australia, Belgium, France, Netherlands
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Fulcrum TherapeuticsActive, not recruitingFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Canada, France, Spain
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Fulcrum TherapeuticsCompletedFacioscapulohumeral Muscular Dystrophy (FSHD)United States, Canada, France, Spain
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State University of New York at BuffaloEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsRecruiting
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Yale UniversityThe Hospital for Sick Children; United States Department of Defense; Connecticut...CompletedChronic Pain | Neurofibromatosis 1United States
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The Cooper Health SystemCompletedMetachromatic LeukodystrophyUnited States
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Memorial Sloan Kettering Cancer CenterActive, not recruitingHearing Loss | Intraocular RetinoblastomaUnited States
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NFlection Therapeutics, Inc.CompletedNeurofibromatosis 1 | Cutaneous NeurofibromaUnited States
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La Jolla Pharmaceutical CompanyPRA Health SciencesCompletedHereditary HemochromatosisUnited States, Australia, France, United Kingdom
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Hoffmann-La RocheCompletedDuchenne Muscular DystrophyUnited States, Belgium, Canada, Australia, Japan, France, Netherlands, Spain, Argentina, Germany, Italy, United Kingdom, Sweden
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National Human Genome Research Institute (NHGRI)CompletedMelanoma | Breast Neoplasm | Ovarian Neoplasm | Hereditary Neoplastic SyndromeUnited States, Finland, Iceland, Sweden
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Aspa TherapeuticsRecruiting
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TakedaTakeda Development Center Americas, Inc.CompletedAngioedemaUnited States, Spain, Netherlands, Hungary, Italy, Canada, Germany, France, Japan, Poland
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National Cancer Institute (NCI)CompletedRecurrent Fallopian Tube Carcinoma | Recurrent Ovarian Carcinoma | Recurrent Primary Peritoneal Carcinoma | Breast Carcinoma | Ovarian Carcinoma | Pancreatic Carcinoma | Prostate Carcinoma | Recurrent Breast Carcinoma | Estrogen Receptor Negative | HER2/Neu Negative | Progesterone Receptor Negative | Triple-Negative... and other conditionsUnited States
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NightstaRx Ltd, a Biogen CompanyCompletedChoroideremiaFinland, United States, Canada, Denmark, Netherlands, Germany, United Kingdom, Brazil, France
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Gemini Therapeutics, Inc.TerminatedMacular Degeneration | Retinal Degeneration | Geographic Atrophy | Dry Age-related Macular Degeneration | Retinal DiseaseUnited States
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Sarepta Therapeutics, Inc.Completed
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Dana-Farber Cancer InstituteNovartis PharmaceuticalsCompletedTuberous Sclerosis Complex | TSC1 | TSC2 | MTORUnited States
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National Cancer Institute (NCI)Completed
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Wave Life Sciences Ltd.TerminatedDuchenne Muscular DystrophyUnited States, Belgium, United Kingdom, Czechia, Canada, France, Italy, Sweden
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NYU Langone HealthCompletedNeurofibromatosis 1 and 2 (NF1 and NF2)United States
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NYU Langone HealthCompletedAnxiety Disorders | Familial Dysautonomia | Dysthymia | Paroxysmal Hypertension | Autosomal Recessive DiseaseUnited States
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AlexionRecruiting
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Alkeus Pharmaceuticals, Inc.RecruitingStargardt Disease | Stargardt Macular Degeneration | Stargardt Macular Dystrophy | Autosomal Recessive Stargardt Disease 1 (ABCA4-related)United States
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Mimetogen Pharmaceuticals USA, Inc.Active, not recruitingDry Eye Syndromes | Dry Eye Disease | Kerato Conjunctivitis SiccaUnited States
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Lihir Medical CentreLondon School of Hygiene and Tropical MedicineCompletedYaws | Scabies | Lymphatic Filariases | Trachoma | StrongyloidiasisPapua New Guinea
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Aspa TherapeuticsRecruitingCanavan DiseaseUnited States
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University of RochesterCompletedCharcot Marie Tooth DiseaseUnited States
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Bausch & Lomb IncorporatedCompletedDry Eye Disease (DED)United States
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John Jay High SchoolUnknownNeurofibromatosis Type 1United States
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UCSF Benioff Children's Hospital OaklandNational Cancer Institute (NCI)Completed
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Genzyme, a Sanofi CompanyCompletedAlport Syndrome Patients With eGFR Between 45-90 ml/Min/1.73 m2France, Germany, Australia, United States, United Kingdom, Canada
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National Cancer Institute (NCI)Active, not recruitingLynch Syndrome | Stage III Colon Cancer AJCC v8 | Colon Adenocarcinoma | DNA Repair DisorderUnited States, Puerto Rico, Germany
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Capricor Inc.RecruitingNervous System Diseases | Genetic Diseases, Inborn | Genetic Diseases, X-Linked | Muscular Diseases | Neuromuscular Diseases | Muscular Dystrophies | Muscular Disorders, Atrophic | Muscular Dystrophy, DuchenneUnited States
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid PolyneuropathiesUnited States, Canada, Argentina, Australia, Bulgaria, Cyprus, Italy, Japan, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Germany, France, Brazil, Turkey, Korea, Republic of, Taiwan, United Kingdom
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedKidney CancerUnited States, Canada, Puerto Rico, Australia, Netherlands, New Zealand, Switzerland
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AstraZenecaApproved for marketingNF type1 With Inoperable Plexiform NeurofibromasUnited States
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Sarepta Therapeutics, Inc.Hoffmann-La RocheRecruitingDuchenne Muscular DystrophyBelgium, United States, Japan, Spain, Italy, United Kingdom
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UCSF Benioff Children's Hospital OaklandNational Cancer Institute (NCI)CompletedNeoplastic SyndromeUnited States
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Novartis PharmaceuticalsCompletedIron Overload | Hereditary HemochromatosisUnited States, Germany, Italy, Australia, Canada, France
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Massachusetts General HospitalNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes... and other collaboratorsCompletedNervous System Diseases | Amyotrophic Lateral Sclerosis | Primary Lateral Sclerosis | Lou Gehrig's Disease | Hereditary Spastic ParaparesisUnited States, Canada
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Horizon Pharma USA, Inc.Approved for marketingThyroid Eye Disease | Graves' OrbitopathyUnited States
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Dompé Farmaceutici S.p.ARecruitingDry Eye | Sjögren SyndromeUnited States
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The Cleveland ClinicCompletedFamilial Mediterranean FeverUnited States
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Children's Oncology GroupNational Cancer Institute (NCI)CompletedKidney CancerUnited States, Canada, Puerto Rico, Australia, Netherlands, Switzerland, New Zealand
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Avidity Biosciences, Inc.CompletedMyotonic Dystrophy | Myotonic Disorders | Myotonic Dystrophy Type 1 (DM1) | Myotonic Dystrophy 1 | Myotonic Muscular Dystrophy | DM1 | Dystrophy Myotonic | Steinert DiseaseUnited States