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- US Clinical Trials Registry
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Clinical Trials on Craniofacial Abnormalities in South Africa
Total 1398 results
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Murdoch Childrens Research InstituteCompleted
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New York State Institute for Basic ResearchEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsUnknownAlzheimer Disease | Down SyndromeUnited States, Canada, Australia, United Kingdom
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Grifols Therapeutics LLCCompleted
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Tetra Discovery PartnersRecruitingFragile X SyndromeUnited States
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Tetra Discovery PartnersEnrolling by invitationFragile X SyndromeUnited States
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Baxalta now part of ShireBaxter Healthcare, Ltd. (New Zealand), Baxter Healthcare Pty. Ltd. (Australia)CompletedAlpha 1-Antitrypsin DeficiencyAustralia, New Zealand
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Medical University of South CarolinaNational Center for Research Resources (NCRR); Alpha-1 FoundationCompletedAlpha-1 Antitrypsin DeficiencyUnited States
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Novartis PharmaceuticalsCompletedLong-term Safety of TIPItaly, Spain, Germany, United States, Australia, Canada, Hungary, Mexico, Argentina
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University of PittsburghNational Heart, Lung, and Blood Institute (NHLBI)Completed
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Western Sydney Local Health DistrictMonash University; University of Sydney; University of Melbourne; The University... and other collaboratorsNot yet recruiting
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Boston Children's HospitalChildren's Hospital Colorado; Cedars-Sinai Medical Center; Hospital for Special... and other collaboratorsRecruitingAdolescent Idiopathic Scoliosis | Idiopathic Scoliosis | Spondylolisthesis | Spine Deformity | Neuromuscular Scoliosis | Congenital ScoliosisUnited States
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Novartis PharmaceuticalsCompletedAcute Myeloid Leukemia (AML)Germany, Spain, United States
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Natera, Inc.Eunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsTerminatedAneuploidy | Trisomy 21 | Trisomy 18 | Trisomy 13United States, Ireland, Canada, Italy, Korea, Republic of, Spain
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Novartis PharmaceuticalsCompletedFragile X SyndromeUnited States, Switzerland, Germany, Australia, Canada, Denmark, France, Italy, Spain, United Kingdom
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BioMarin PharmaceuticalActive, not recruitingHemophilia AUnited States, Taiwan, United Kingdom, Australia, Israel, Belgium, Brazil, France, Germany, Italy, Korea, Republic of, South Africa, Spain
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Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta... and other collaboratorsRecruitingIntellectual Disability | Autism Spectrum Disorder | Fragile X Syndrome | Developmental Disability | Congenital Anomaly | Facioscapulohumeral Muscular Dystrophy 1United States
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Bioverativ Therapeutics Inc.CompletedHemophilia AUnited States, Canada, Italy, Australia, Austria, Belgium, Brazil, France, Germany, Hong Kong, India, Ireland, Israel, Japan, Netherlands, New Zealand, Poland, South Africa, Spain, Sweden, Switzerland, United Kingdom
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Johns Hopkins UniversityMedtronicCompletedTetralogy of Fallot | Pulmonary Regurgitation | Pulmonary StenosisUnited States
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncActive, not recruitingMucopolysaccharidosis III | Sanfilippo Syndrome | MPS IIIA | Sanfilippo AUnited States, Australia, Spain
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Calcilytix Therapeutics, Inc., a BridgeBio companyRecruitingAutosomal Dominant Hypocalcemia (ADH)United States, Australia, United Kingdom, Denmark, Italy, France, Japan, Taiwan, Canada, Czechia, Netherlands
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Akesobio Australia Pty LtdCompletedAtopic DermatitisNew Zealand, Australia
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Percheron TherapeuticsActive, not recruitingDuchenne Muscular DystrophyUnited Kingdom, Australia, Serbia, Turkey, Bulgaria
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MedImmune LLCCompletedCongenital Heart DiseaseUnited States, Spain, United Kingdom, Canada, Belgium, Germany, Israel, Austria, Poland, Russian Federation, Sweden, Lebanon, France, Czech Republic, Hungary, Denmark, Bulgaria
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Imara, Inc.CompletedSickle Cell DiseaseUnited States, United Kingdom
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Trefoil Therapeutics, Inc.CompletedFuchs' Endothelial Dystrophy | Fuchs Dystrophy | FuchsUnited States
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BioCryst PharmaceuticalsCompleted
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Catalyst BiosciencesTerminatedHemophilia A With Inhibitor | Hemophilia B With InhibitorUnited States, United Kingdom, Taiwan, Italy, Spain, India, Turkey, Malaysia, Russian Federation, Armenia, Georgia, Hungary, Mexico, Poland, South Africa, Ukraine
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Chris GossUniversity of Washington; University of Arkansas; Harvard University; Cystic Fibrosis...Completed
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Arena PharmaceuticalsCompletedAtopic DermatitisUnited States, Australia, Canada
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Children's Oncology GroupNational Cancer Institute (NCI)RecruitingDown Syndrome | Myeloid Leukemia Associated With Down Syndrome | B Acute Lymphoblastic Leukemia Associated With Down SyndromeUnited States
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Duke UniversityNational Heart, Lung, and Blood Institute (NHLBI); RTI InternationalCompletedHematologic Diseases | Sickle Cell Disease | Anemia, Sickle Cell | Genetic DiseaseUnited States
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Eunice Kennedy Shriver National Institute of Child...CompletedFetal Growth Restriction | Growth DiscordancyUnited States
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Novoteris, LLCMallinckrodt; Cystic Fibrosis FoundationTerminatedCystic FibrosisUnited States, Canada
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisAustralia, United Kingdom
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Shanton Pharma Co., Ltd.CompletedHyperuricemia | GoutUnited States
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AmgenCompletedSevere Familial HypercholesterolemiaItaly, Czechia, United States, Israel, New Zealand, South Africa, France, Spain, Australia, Belgium, Canada, Netherlands, Hong Kong, Brazil, United Kingdom, Greece, Japan, Lebanon
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Novartis PharmaceuticalsCompletedTransfusion-dependent Iron OverloadEgypt, Greece, Hong Kong, Taiwan, Germany, United Kingdom, Belgium, Italy, Spain, France, Israel, Korea, Republic of, Turkey, China, Australia, Denmark, Austria, Switzerland, Netherlands, South Africa, Lebanon, Malaysia, Thailand
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BayerCompletedBronchiectasisItaly, Spain, Germany, United Kingdom, France
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Grifols Therapeutics LLCCompletedAlpha 1-Antitrypsin DeficiencyUnited States
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Novartis PharmaceuticalsActive, not recruitingSickle Cell Disease (SCD)United States, United Kingdom, Germany, Spain, Greece, Italy, Brazil, Lebanon, Turkey, Belgium, France, Jordan, India, Finland, Canada, Colombia, Netherlands, Oman, South Africa, Panama, Ghana
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Children's Hospital Medical Center, CincinnatiRecruitingHypoplastic Left Heart Syndrome (HLHS)United States, United Kingdom, Canada
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Eisai LimitedCompletedCognitive ImpairmentUnited States, Spain, Australia
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Neuren Pharmaceuticals LimitedCompleted
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PfizerActive, not recruitingMuscular Dystrophy, DuchenneUnited States, Australia
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Novo Nordisk A/SRecruitingHaemophilia A With or Without InhibitorsKorea, Republic of, India, China, Canada, Spain, Netherlands, South Africa, United States, Israel, Japan, Poland, United Kingdom, Italy, Lithuania, Portugal, Switzerland, Taiwan
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PfizerRecruitingHemophilia A | Hemophilia BHong Kong, Spain, Serbia, Turkey, United States, China, Mexico, South Africa, India, Japan, Croatia, Korea, Republic of, Oman, Taiwan, Italy, Canada, France
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Genzyme, a Sanofi CompanyActive, not recruitingHemophiliaChina, Hungary, Turkey, Canada, Korea, Republic of, United States, Australia, Denmark, France, Germany, India, Ireland, Israel, Italy, Japan, Malaysia, South Africa, Taiwan, Ukraine, United Kingdom
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Horizon Health NetworkMcGill University; University of Michigan; Carilion Clinic; Lawson Health Research... and other collaboratorsCompleted
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Genentech, Inc.Completed