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Clinical Trials on Creatine Deficiency Syndrome Due to Gamt Deficiency
Total 5904 results
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Fondazione IRCCS Ca' Granda, Ospedale Maggiore...UnknownCeliac Disease | Iron Deficiency AnemiaItaly
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HaEmek Medical Center, IsraelCompletedIron Deficiency | MalabsorptionIsrael
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National Institute of Allergy and Infectious Diseases...Completed
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University Hospital, MontpellierTerminatedChronic Spotaneous Urticaria, Idiopathic Non Histaminergic Angioderma, Hereditary Angioedema With C1 Inhibitor DeficiencyFrance
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PATHBill and Melinda Gates Foundation; Centre National de Greffe de Moelle Osseuse and other collaboratorsNot yet recruitingPrimary Immunodeficiency DiseasesTunisia
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University Hospital Southampton NHS Foundation...Royal Marsden NHS Foundation Trust; University College London Hospitals; Cambridge... and other collaboratorsUnknownCOVID | Infection | Immune Deficiency | Immune Suppression | Children, AdultUnited Kingdom
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University of AarhusUniversity of CopenhagenCompletedIleostomy - Stoma | Short Bowel Syndrome | Nutritional Deficiency | Sodium DepletionDenmark
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IpsenTerminated
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UConn HealthCompletedAging | Vaccine Response Impaired | Age-Related ImmunodeficiencyUnited States
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Taif UniversityCompleted
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Charite University, Berlin, GermanyCompletedInflammatory Bowel Diseases | Restless Legs Syndrome | Iron-deficiency
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Icahn School of Medicine at Mount SinaiCompletedMetabolic Syndrome | Vitamin D Deficiency | PrediabetesUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedMitochondrial Disorders | Li-Fraumeni Syndrome | Carriers of p53 MutationUnited States
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University of Alabama at BirminghamNational Institutes of Health (NIH); Mereo BioPharmaCompletedEmphysema or COPD | Alpha-1 Antitrypsin Deficiency (AATD) | Pi*ZZ, Pi*SZ, Pi*Null, Another Rare Phenotype/Genotype Known to be Associated With Either Low or Functionally Impaired AAT Including F or I MutationsUnited States
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Hospital Civil Juan I. MenchacaNot yet recruitingMalnutrition | Peritoneal Dialysis | Oxidative Stress | Protein-Energy Malnutrition | Protein-Energy Wasting | Oral Nutritional Supplements
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Masonic Cancer Center, University of MinnesotaRecruitingCommon Variable Immunodeficiency | Chronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | X-linked Lymphoproliferative Disease | Langerhan's Cell Histiocytosis | Chediak-Higashi Syndrome | Griscelli Syndrome | Bare Lymphocyte Syndrome | SCID | Omenn's Syndrome | Reticular... and other conditionsUnited States
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University of Alabama at BirminghamJohns Hopkins University; Birmingham AIDS Outreach; AIDS UnitedCompletedHIV Infection | HIV Care Loss to Followup
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Pharvaris Netherlands B.V.CompletedHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsBulgaria, United States, Spain, Israel, Germany, Canada, Czechia, France, Hungary, Italy, Netherlands, Poland, United Kingdom
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Sparrow PharmaceuticalsActive, not recruitingCortisol; Hypersecretion | Cortisol Overproduction | Cushing's Syndrome I | Cushing Disease Due to Increased ACTH Secretion | Cortisol Excess | Ectopic ACTH SecretionUnited States, Bulgaria, Romania
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Providence Medical Research CenterProvidence Sacred Heart Medical Center & Children's HospitalTerminatedCeliac Disease | Iron Deficiency | Iron MalabsorptionUnited States
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Pharvaris Netherlands B.V.Active, not recruitingHereditary Angioedema | Hereditary Angioedema Type I | Hereditary Angioedema Type II | Hereditary Angioedema Types I and II | Hereditary Angioedema Attack | Hereditary Angioedema With C1 Esterase Inhibitor Deficiency | Hereditary Angioedema - Type 1 | Hereditary Angioedema - Type 2 | C1 Esterase Inhibitor... and other conditionsUnited States, Poland, Germany, Austria, Bulgaria, Canada, Ireland, Italy, United Kingdom
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Children's Hospitals and Clinics of MinnesotaCompletedIron Deficiency | Restless Leg SyndromeUnited States
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National Cheng-Kung University HospitalCompletedObesity | Metabolic Syndrome | Vitamin D Deficiency | Insulin Resistance | Sarcopenia | Osteoporosis | Elderly | OstreocalcinTaiwan
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Ain Shams Maternity HospitalUnknownPolycystic Ovary Syndrome | Vitamin D Deficiency | Insulin ResistanceEgypt
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TESS Research FoundationBrown University; Stanford University; University of Texas Southwestern Medical...RecruitingEpilepsy | Movement Disorders | Rare Diseases | Genetic Disorder | Citrate Transporter Deficiency | SLC13A5 Deficiency | EIEE25 | Kohlschutter-Tonz Syndrome (Non-ROGDI) | Citrate Transporter Disorder | DEE25United States
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Assistance Publique - Hôpitaux de ParisCompletedGitelman Syndrome | Potassium DepletionFrance
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SandozCompleted
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SandozCompletedHIV Infections | DiarrheaUnited States
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Radboud University Medical CenterCompletedPregnancy | HIV-infection | Mother to Child TransmissionZambia, Tanzania
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Bürgerspital SolothurnUnknownOrthostatic Hypotension | Vasoplegic Syndrome | Sirs Due to Noninfectious Process Without Organ Dysfunction
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Fred Hutchinson Cancer CenterNational Cancer Institute (NCI); National Heart, Lung, and Blood Institute...CompletedPreviously Treated Myelodysplastic Syndrome | Fanconi Anemia | de Novo Myelodysplastic Syndrome | Acute Myeloid Leukemia in RemissionUnited States, Brazil
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Yang LiRuijin HospitalRecruitingPediatric Cancer | Li-Fraumeni Syndrome | p53 MutationsChina
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Lebanese UniversityCompletedPolycystic Ovary Syndrome | Endometriosis | Ectopic Pregnancy | Premature Ovarian Failure | Female Infertility Endocrine | Female Infertility | Fibroids | Salpingitis | Hydrosalpinx | Female Infertility Due to Ovulatory Disorder | Female Infertility of Tubal Origin | Female Infertility Due to Tubal Block | Female... and other conditionsLebanon
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Maimonides Medical CenterCompletedPolycystic Ovary Syndrome | Vitamin D DeficiencyUnited States
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University of California, San FranciscoNational Cancer Institute (NCI)CompletedMyelodysplastic Syndromes | Leukemia | Congenital Amegakaryocytic Thrombocytopenia | Severe Congenital NeutropeniaUnited States
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Christian HvasCompletedShort Bowel Syndrome | Nutritional Deficiency | Ileostomy; Functional Disturbance | Absorption; Disorder, ProteinDenmark
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Massachusetts General HospitalCompleted
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Beth Israel Deaconess Medical CenterTerminatedIrritable Bowel Syndrome | Abdominal Pain | Vitamin D DeficiencyUnited States
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University of PecsCompletedSepsis | Acute Kidney Injury Due to SepsisHungary
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IntraBio IncRecruitingAtaxia Telangiectasia | Louis Bar SyndromeSpain, United States, Germany, United Kingdom
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King's College LondonUniversity of Sheffield; University of Manchester; National Health Service, United... and other collaboratorsRecruiting
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National Heart, Lung, and Blood Institute (NHLBI)Recruiting
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David WilliamsUniversity of California, Los Angeles; Boston Children's Hospital; Children's...CompletedSevere Combined ImmunodeficiencyUnited States
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St. Jude Children's Research HospitalCompletedSevere Combined ImmunodeficiencyUnited States
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Emory UniversityGrady Health SystemCompleted
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National Institute of Allergy and Infectious Diseases...Eunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedHIV InfectionsUnited States, Puerto Rico
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University of Sao PauloCompleted
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Oslo University HospitalCompleted
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National Heart, Lung, and Blood Institute (NHLBI)CompletedNeoplasms | Myelodysplastic Syndromes | Hematologic Diseases | Leukemia | Severe Combined Immunodeficiency | Fanconi Anemia | Anemia, Aplastic | Hematopoietic Stem Cell Transplantation
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Jasper Therapeutics, Inc.Recruiting