- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Disability in United Kingdom
Total 698 results
-
Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationObstructive Sleep Apnea | Down SyndromeUnited States
-
National Institute of Mental Health (NIMH)CompletedSchizophrenia | Bipolar Disorder | Attention Deficit Disorder With Hyperactivity | Mental Retardation | Mental Disorder Diagnosed in ChildhoodUnited States
-
University of Alabama at BirminghamUniversity of Colorado, Denver; Eunice Kennedy Shriver National Institute of... and other collaboratorsCompletedRett Syndrome, Preserved Speech Variant | Mecp2 Duplication Syndrome | Rett-related DisordersUnited States
-
Hoffmann-La RocheCompleted
-
Eunice Kennedy Shriver National Institute of Child...RecruitingAutism Spectrum Disorder | Fragile X Syndrome | Developmental Delay | Genetic Disorder | Asperger DisorderUnited States
-
Lundquist Institute for Biomedical Innovation at...Active, not recruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
-
Tetra Discovery PartnersRecruitingFragile X SyndromeUnited States
-
Tetra Discovery PartnersEnrolling by invitationFragile X SyndromeUnited States
-
Rocket Pharmaceuticals Inc.Recruiting
-
Brigham and Women's HospitalChildren's Hospital of Philadelphia; University of Michigan; University of Texas... and other collaboratorsCompletedSleep Disordered Breathing | Down SyndromeUnited States
-
University of MiamiUniversity of Pennsylvania; National Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health (NIH) and other collaboratorsRecruiting
-
University of South FloridaUniversity of California, Los Angeles; Temple UniversityCompletedGeneralized Anxiety Disorder | Social Phobia | Separation Anxiety Disorder | Specific Phobia | Autism | Autism Spectrum Disorders | Obsessive-compulsive Disorder | Asperger's Syndrome | Pervasive Developmental Disability - Not Otherwise SpecifiedUnited States
-
Carelon ResearchNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health...CompletedDown Syndrome | Congenital Heart DiseaseUnited States, Canada
-
Neuren Pharmaceuticals LimitedCompleted
-
Zynerba Pharmaceuticals, Inc.CompletedFragile X SyndromeUnited States, New Zealand, Australia
-
Rocket Pharmaceuticals Inc.Active, not recruitingDanon DiseaseUnited States
-
Cindy CisnerosCompletedDown Syndrome | Aneuploidy | Trisomy 21 | Trisomy 18 | Trisomy 13United States
-
REGENXBIO Inc.Withdrawn
-
Oregon Health and Science UniversityActive, not recruitingObstructive Sleep Apnea of ChildUnited States
-
Stanford UniversityTerminatedFragile X Syndrome (FXS) | Idiopathic Intellectual Developmental Disorder (IDD)United States
-
Seaside Therapeutics, Inc.Completed
-
Rocket Pharmaceuticals Inc.RecruitingDanon DiseaseUnited States
-
National Heart, Lung, and Blood Institute (NHLBI)CompletedHypertension | Cardiovascular Disease | Williams Syndrome | Multisystem Developmental Disorder | Elastin Gene DeletionUnited States
-
National Human Genome Research Institute (NHGRI)CompletedMental Retardation | Sleep Disorders, Circadian Rhythm | Developmental Delay Disorders | Chromosome Deletion | Self Injurious BehaviorUnited States
-
Children's Hospital of PhiladelphiaCompletedObstructive Sleep Apnea Syndrome | Down SyndromeUnited States
-
University of California, San FranciscoNational Human Genome Research Institute (NHGRI)CompletedEpilepsy | Cerebral Palsy | Intellectual Disability | Developmental Delay | Metabolic Disease | Neuro-Degenerative Disease | Encephalopathy | Birth Defect | Multiple Congenital Anomaly | Developmental DefectUnited States
-
ArmaGen, IncCompletedMucopolysaccharidosis IIUnited States, Germany, Philippines
-
Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
-
Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
-
Children's Oncology GroupNational Cancer Institute (NCI)CompletedMyeloid Proliferations Associated With Down SyndromeUnited States, Canada, Australia, Puerto Rico
-
Maimonides Medical CenterFoundation for Prader-Willi ResearchRecruitingBody Weight | Hyperphagia | Prader-Willi Syndrome | Mood | Behavior | Excessive Daytime SleepinessUnited States
-
Maimonides Medical CenterRecruitingAggression | Behavioral Symptoms | Pathologic Processes | Nervous System Diseases | Obesity | Neurologic Manifestations | Neurobehavioral Manifestations | Congenital Abnormalities | Overnutrition | Nutrition Disorders | Genetic Diseases, Inborn | Intellectual Disability | Self-Injurious Behavior | Abnormalities, Multiple and other conditionsUnited States
-
Duke UniversityRecruiting
-
Christopher Hartnick, M.D.University of Pittsburgh; Emory University; Children's Hospital Medical Center... and other collaboratorsCompletedSleep Apnea, Obstructive | Down SyndromeUnited States
-
Lundquist Institute for Biomedical Innovation at...TerminatedMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
-
Novo Nordisk A/SCompletedHealthy | Prader-Willi Syndrome | Genetic Disorder | Growth Disorder | Idiopathic Short StatureUnited States
-
Jirair Krikor BedoyanUltragenyx Pharmaceutical IncRecruitingPyruvate Dehydrogenase Complex DeficiencyUnited States
-
Cyprium Therapeutics, Inc.Enrolling by invitation
-
Eunice Kennedy Shriver National Institute of Child...Completed
-
Lundquist Institute for Biomedical Innovation at...CompletedMucopolysaccharidosis Type I | Mucopolysaccharidosis Type II | Mucopolysaccharidosis Type VIUnited States
-
Sangamo TherapeuticsTerminatedMucopolysaccharidosis II | MPS IIUnited States
-
International Rett Syndrome FoundationBaylor College of Medicine; Children's Hospital of Philadelphia; University of... and other collaboratorsRecruitingNervous System Diseases | Neurologic Manifestations | Neurobehavioral Manifestations | Genetic Diseases, X-Linked | Intellectual Disability | Neurodevelopmental Disorders | Neurologic Disorder | Rett Syndrome | Genetic Disease | Rett Syndrome, AtypicalUnited States
-
Psyadon PharmaCompletedLesch-Nyhan DiseaseUnited States
-
University of California, San DiegoBioMarin PharmaceuticalWithdrawnBehavioral Manifestations of Lesch-Nyhan DiseaseUnited States
-
Women and Infants Hospital of Rhode IslandNatera, Inc.CompletedTrisomy 21 | Trisomy 18 | Trisomy 13 | Monosomy XUnited States
-
LuMind IDSC FoundationAlzheimer's Disease Cooperative Study (ADCS)Active, not recruitingAlzheimer's Disease in Down SyndromeUnited States
-
National Heart, Lung, and Blood Institute (NHLBI)RecruitingCardiovascular Disease | Williams Syndrome | Supravalvular Aortic StenosisUnited States
-
Denali Therapeutics Inc.Enrolling by invitationMucopolysaccharidosis IIUnited States, Canada, Belgium, Czechia, Netherlands
-
Brigham and Women's HospitalChildren's Hospital of Philadelphia; University of Michigan; University of Southern... and other collaboratorsRecruitingObstructive Sleep Apnea | Down SyndromeUnited States