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Clinical Trials on Diseases Genetic, Genetic in Ireland
Total 8123 results
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University Hospital FreiburgCompletedMyelodysplastic Syndromes | Fanconi Anemia | Dyskeratosis Congenita | Pearson Marrow-pancreas Syndrome | Shwachman-diamond SyndromeSpain, Germany, Switzerland, Austria, Netherlands, Italy, Czech Republic, Belgium, Denmark, Ireland
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Royal College of Surgeons, IrelandThe Hospital for Sick Children; Imperial College London; Erasmus Medical Center; University College Dublin and other collaboratorsActive, not recruitingCystic Fibrosis | Adherence, Medication | Cystic Fibrosis Gastrointestinal Disease | Cystic Fibrosis in Children | Cystic Fibrosis Liver DiseaseUnited Kingdom, Ireland
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ASLAN PharmaceuticalsRecruitingAtopic DermatitisUnited States, Canada
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AstraZenecaCompletedAtopic DermatitisUnited States, Germany, Australia, Spain, United Kingdom, Poland
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Ionis Pharmaceuticals, Inc.CompletedCystic Fibrosis | Healthy SubjectsUnited Kingdom, Germany
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SanofiRecruiting
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Swedish Orphan BiovitrumIQVIA Pvt. LtdTerminatedHemophilia A | Hemophilia BBulgaria, Croatia, Czechia, France, Hungary, Ireland, Italy, Romania, Slovenia, Spain, United Kingdom
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Daiichi Sankyo, Inc.CompletedAtopic DermatitisUnited States
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ShionogiCompletedAtopic DermatitisUnited States
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Q32 Bio Inc.RecruitingAtopic DermatitisUnited States
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, United Arab Emirates, United Kingdom
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Nationwide Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health... and other collaboratorsNot yet recruitingSickle Cell DiseaseUnited States
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Novartis PharmaceuticalsTerminatedAtopic DermatitisUnited Kingdom, Germany, Russian Federation, Taiwan, Belgium, Netherlands, Japan, Finland, Slovakia, United States, Iceland, Canada, Poland
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PfizerRecruitingAtopic DermatitisUnited States, Canada
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Daiichi Sankyo, Inc.CompletedAtopic DermatitisUnited States
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Eli Lilly and CompanyActive, not recruiting
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Ralexar Therapeutics, Inc.CompletedAtopic Dermatitis | Eczema, AtopicUnited States
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Seaside Therapeutics, Inc.TerminatedFragile X SyndromeUnited States
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Bioverativ, a Sanofi companySwedish Orphan BiovitrumCompletedHemophilia BUnited States, Italy, Ireland, New Zealand, United Kingdom, Australia, Netherlands, Denmark, Poland, Sweden, France
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PharmaxisCompletedCystic FibrosisIreland, United Kingdom, Australia
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Catabasis PharmaceuticalsCompletedMuscular Dystrophy, DuchenneUnited States, Canada, Australia, United Kingdom, Germany, Ireland, Israel, Sweden
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Eli Lilly and CompanyDermira, Inc.CompletedAtopic DermatitisUnited States
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Incyte CorporationCompletedAtopic DermatitisUnited States, Canada
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Actavis Inc.CompletedAtopic DermatitisUnited States
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GlaxoSmithKlineCompletedDermatitis, AtopicUnited States, Canada, Japan
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Sarepta Therapeutics, Inc.Active, not recruitingMuscular Dystrophy, DuchenneUnited States, Korea, Republic of, India, Slovenia, Turkey, United Kingdom, Germany, Switzerland, Spain, Czechia, France, Serbia, Taiwan, Netherlands, Mexico, Colombia, Denmark, New Zealand, Norway, Greece, Hungary, Ireland, Italy, Jo... and more
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Acrotech Biopharma Inc.Active, not recruitingAtopic DermatitisUnited States
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Eli Lilly and CompanyDermira, Inc.CompletedAtopic DermatitisUnited States, Canada, Germany, Poland
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Kamada, Ltd.Syneos HealthRecruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom, Sweden, Ireland, Netherlands, Belgium, Finland
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Dermavant Sciences GmbHCompletedAtopic DermatitisUnited States, Canada
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Eli Lilly and CompanyIncyte CorporationTerminatedAtopic DermatitisUnited States, Puerto Rico, Canada
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AbbVieEnrolling by invitationAtopic DermatitisUnited States, Australia, Austria, Belgium, Canada, China, Czechia, France, Germany, Greece, Hong Kong, Hungary, Ireland, Israel, Italy, Japan, Netherlands, New Zealand, Norway, Puerto Rico, Slovakia, Spain, Sweden, United Kingdom
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CSL BehringActive, not recruitingHemophilia BUnited States, Belgium, Netherlands, Denmark, Germany, Ireland, Sweden, United Kingdom
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CelgeneCompletedEczema | Dermatitis, AtopicUnited States, Canada, Japan, Poland, China, Czechia
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PedNet Haemophilia Research FoundationLund University HospitalRecruitingFactor IX Deficiency | Factor VIII DeficiencyNorway, Austria, Belgium, Canada, Czechia, Denmark, Finland, France, Germany, Greece, Ireland, Israel, Italy, Netherlands, Portugal, Spain, Sweden, Switzerland, United Kingdom
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Seaside Therapeutics, Inc.CompletedFragile X SyndromeUnited States
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Eli Lilly and CompanyTerminatedAtopic DermatitisSpain, Puerto Rico, United States, Canada, Japan, Italy, Argentina, Austria, Czechia, France, Germany, Hungary, Mexico
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PfizerCompletedAtopic DermatitisUnited States, Canada, Australia, Germany, Hungary
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ASLAN PharmaceuticalsCompletedAtopic DermatitisUnited States, Australia, Singapore, India, Canada, New Zealand, Dominican Republic, Poland
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Eli Lilly and CompanyCompletedAtopic DermatitisUnited States
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AbbVieCompletedA Study to Evaluate Risankizumab in Adults and Adolescents With Moderate to Severe Atopic DermatitisDermatitisUnited States, Australia, Canada, Japan, Puerto Rico
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PfizerCompletedAtopic DermatitisGermany, United States, Canada, Denmark, Hungary, Australia, Latvia, Poland, Bulgaria, Japan
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LEO PharmaTerminatedAtopic DermatitisUnited States, Netherlands, United Kingdom, France, Canada, Ireland, Austria, Germany, Poland
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Zynerba Pharmaceuticals, Inc.RecruitingFragile X SyndromeUnited States, Australia, United Kingdom, Ireland
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Eli Lilly and CompanyIncyte CorporationCompletedAtopic DermatitisUnited States, Puerto Rico, Canada
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Regeneron PharmaceuticalsSanofiCompletedAtopic DermatitisHungary, Netherlands, Spain, United Kingdom, United States, Australia, Austria, Belgium, Bulgaria, Canada, China, Czechia, Denmark, Estonia, Finland, France, Germany, Ireland, Italy, Japan, Korea, Republic of, Lithuania, New Zealand, ... and more
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia A | Haemophilia BBelgium, Germany, France, United Kingdom, Italy, Hungary, Austria, Sweden, Iran, Islamic Republic of, Argentina, Ireland, Poland, Portugal, Slovakia
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Arcutis Biotherapeutics, Inc.CompletedAtopic Dermatitis EczemaUnited States, Canada
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AbbVieCompletedAtopic DermatitisUnited States, Australia, Canada, Croatia, Czechia, Finland, France, Germany, Hungary, Ireland, Israel, Italy, Malaysia, Netherlands, New Zealand, Norway, Poland, Singapore, Spain, Taiwan, Ukraine, United Kingdom