- ICH GCP
- US Clinical Trials Registry
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Clinical Trials on Diseases Genetic, Genetic in Ireland
Total 8115 results
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Neurocrine BiosciencesCompletedTourette SyndromeUnited States
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Kowa Research Institute, Inc.CompletedFuchs' Endothelial Corneal DystrophyUnited States, Australia, Germany, Spain, Denmark
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Omeros CorporationTerminatedHuntington's DiseaseUnited States
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Hoffmann-La RocheChugai PharmaceuticalCompletedHemophilia AAustralia, Taiwan, Korea, Republic of, France, Germany, Italy, South Africa, Spain, United States, Japan, Ireland, Poland, United Kingdom, Costa Rica
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Vertex Pharmaceuticals IncorporatedTerminatedAlpha 1-Antitrypsin DeficiencyUnited States, Germany, Canada, Ireland
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Bioverativ, a Sanofi companyCompletedHemophilia ATurkey, Australia, Canada, France, Germany, Hungary, Ireland, Italy, Netherlands, Spain, Sweden, Switzerland, Taiwan, United Kingdom, United States
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American Thrombosis and Hemostasis NetworkTakedaActive, not recruiting
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OctapharmaCompleted
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Parion SciencesVertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited Kingdom, United States, France, Ireland
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BayerCompletedHaemophilia ASpain, Russian Federation, United States, Hungary, Italy, Mexico, Norway, Romania, Bulgaria, Canada, Argentina, Denmark, Israel, Poland, Ireland, Latvia, Lithuania
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Brown, Theodore R., M.D., MPHCompletedStroke | Multiple Sclerosis | Parkinson's Disease | Brain Injury | Amyotrophic Lateral Sclerosis | Alzheimer's Disease | Spinal Cord Injury | Huntington's DiseaseUnited States
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Cork University HospitalCompleted
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Insmed IncorporatedCompletedCystic FibrosisFrance, Poland, United Kingdom, Germany, Spain, Belgium, Bulgaria, Serbia, Denmark, Greece, Netherlands, Hungary, Ireland, Slovakia, Canada, Italy, Austria
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VA Office of Research and DevelopmentNot yet recruitingAmyotrophic Lateral Sclerosis | Muscular Dystrophy | Spinal Cord Injury | Brain Stem Infarctions | Locked-in SyndromeUnited States
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PfizerCompletedHyperlipidemia | Hypercholesterolemia, FamilialAustralia, Canada, United States, France, South Africa, Sweden, Norway, Denmark, Iceland
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Israel, Ireland, United Kingdom
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PfizerCompletedHemophilia AUnited States, Argentina, Austria, Colombia, Croatia, Jordan, Mexico, New Zealand, Oman, Peru, Poland, Romania, Turkey
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Novo Nordisk A/SActive, not recruitingShort Stature Children Born Small for Gestational Age (SGA)France, Russian Federation, United States, India, Spain, Estonia, Japan, Italy, Algeria, Austria, Hungary, Ireland, Israel, Latvia, Poland, Serbia, Thailand, Ukraine
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Boehringer IngelheimTerminatedTourette SyndromeUnited States, Germany
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Belgium, Netherlands, Australia, Germany, Ireland, United Kingdom
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Spain, Australia, United Kingdom, Germany, Ireland
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CSL BehringCompletedEmphysema | Alpha 1-proteinase Inhibitor DeficiencyAustralia, Canada, Czech Republic, Denmark, Estonia, Finland, Germany, Ireland, Poland, Romania, Sweden
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Regeneron PharmaceuticalsCompleted
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Cork University HospitalCompleted
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Mukoviszidose Institut gGmbHCompletedCystic FibrosisGermany, Italy, Ireland, Austria, Belgium, Hungary, Poland, Spain, Sweden
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Olatec Therapeutics LLCRecruitingArthritis | Joint Pain | Gout | Gout Flare | Gouty Arthritis | Acute Gout Flare | Gout AttackUnited States, Spain, France
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PfizerCompletedHypertriglyceridemia | Hyperlipoproteinemia Type IVUnited States, Canada
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Vertex Pharmaceuticals IncorporatedCompletedAlpha1-Antitrypsin DeficiencyUnited States, Germany, Canada, Ireland, Sweden, United Kingdom
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Boehringer IngelheimCompletedTourette SyndromeUnited States, Germany
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Genzyme, a Sanofi CompanyActive, not recruitingHemophiliaChina, Hungary, Turkey, Canada, Korea, Republic of, United States, Australia, Denmark, France, Germany, India, Ireland, Israel, Italy, Japan, Malaysia, South Africa, Taiwan, Ukraine, United Kingdom
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Jiangsu Atom Bioscience and Pharmaceutical Co.,...Enrolling by invitationGoutUnited States, Georgia, Australia, Guatemala, Taiwan
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Australia, Canada, United Kingdom, Germany, Belgium, Austria, Ireland, Italy, France
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Jiangsu Atom Bioscience and Pharmaceutical Co.,...RecruitingGoutUnited States, Georgia, Australia, Guatemala, Taiwan
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CSL BehringCompletedEmphysema | Alpha1-proteinase Inhibitor DeficiencyAustralia, Russian Federation, United States, Denmark, Estonia, Finland, Germany, Ireland, Poland, Romania, Sweden, Canada, Czech Republic
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Germany, United Kingdom, Canada, Australia, Switzerland, France, Ireland, Belgium, Denmark, Poland
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BioCryst PharmaceuticalsCompleted
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National University of Ireland, Galway, IrelandRecruitingMyocardial Ischemia | Heart Diseases | Cardiovascular Diseases | Vascular Diseases | Coronary Artery Disease | Coronary Disease | Arterial Occlusive DiseasesIreland
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Royal College of Surgeons, IrelandUniversity College Dublin; Connolly Hospital BlanchardstownCompletedChronic Obstructive Pulmonary DiseaseIreland
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Genzyme, a Sanofi CompanyRecruitingFabry DiseaseCroatia, United States, Argentina, Australia, Belgium, Bulgaria, Canada, Germany, Hong Kong, India, Indonesia, Korea, Republic of, Kuwait, Malaysia, Philippines, Poland, Romania, Singapore, Slovakia, Taiwan, Thailand, United Kingdom, Vietn... and more
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Beaumont HospitalRoyal College of Surgeons, IrelandCompletedChronic Obstructive Pulmonary Disease (COPD)Ireland
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Agios Pharmaceuticals, Inc.RecruitingSickle Cell DiseaseUnited Kingdom, United States, Belgium, Netherlands, Germany, Canada, Brazil, France, Israel, Italy, Lebanon, Oman, Ghana, Kenya, Nigeria, Saudi Arabia, Turkey
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Ardea Biosciences, Inc.CompletedGoutPoland, United States, Spain, Canada, Ukraine, United Kingdom
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Western Vascular Institute, IrelandRecruitingPeripheral Arterial Occlusive DiseaseIreland
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Beaumont HospitalGlaxoSmithKline; Health Research Board, Ireland; Asthma Society Ireland; Irish... and other collaboratorsCompletedChronic Obstructive Pulmonary Disease | Asthma | Airways DiseaseIreland
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BioMarin PharmaceuticalTerminatedLate-onset Pompe Patients Untreated or Treated With rhGAASpain, Slovenia, Serbia, Korea, Republic of, Greece, Australia, Singapore, Brazil, Canada, Taiwan, Ireland, Poland, Romania
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MedImmune LLCCompletedChronic Obstructive Pulmonary DiseaseIreland
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National Cancer Institute (NCI)Not yet recruitingFamilial Adenomatous Polyposis | Colorectal Carcinoma | Colorectal Adenomatous Polyp | Multiple Adenomatous PolypsUnited States
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Beaumont HospitalAerogenCompletedChronic Obstructive Pulmonary Disease (COPD)Ireland
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University College DublinCompletedInflammatory Bowel DiseaseIreland
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Mid Western Regional Hospital, IrelandUnknownPeripheral Vascular DiseaseIreland