- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Disorder of Lipid Storage and Metabolism
Total 48063 results
-
AdventHealth Translational Research InstituteTakeda; Sanford-Burnham Medical Research InstituteActive, not recruitingObesity | Lipid Metabolism Disorders | Disorder of Lipid Storage and Metabolism | Metabolic DisorderUnited States
-
Istanbul UniversityBiruni UniversityNot yet recruitingLipid Storage DiseaseTurkey
-
University of Texas Southwestern Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)RecruitingLipid Metabolism DisorderUnited States
-
Université de SherbrookeHospices Civils de LyonCompleted
-
Merck Sharp & Dohme LLCCompletedLipid Metabolism Disorder
-
Ankara UniversityAlexion PharmaceuticalsCompleted
-
Maastricht University Medical CenterCompletedNeutral Lipid Storage DiseaseNetherlands
-
Translational Research Center for Medical Innovation...TerminatedPrimary Triglyceride Deposit Cardiomyovasculopathy (TGCV) | Neutral Lipid Storage Disease With Myopathy (NLSD-M)Italy, Japan
-
Johns Hopkins UniversityVAP Diagnostics LabActive, not recruiting
-
Assiut UniversityNot yet recruitingPsychiatric Problem | Wolman Disease
-
Organon and CoCompleted
-
Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD)United States, United Kingdom, France, Canada, Czech Republic, Italy, Poland, Switzerland
-
Luye Pharma Group Ltd.CompletedLipid Metabolism DisorderUnited States
-
Hasselt UniversityRecruitingExercise | Sedentary Behavior | Lipid Metabolism DisorderBelgium
-
Children's Hospital Medical Center, CincinnatiNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); National... and other collaboratorsCompletedWolman Disease | Cholesterol Ester Storage Disease | Acid Cholesteryl Ester Hydrolase Deficiency, Type 2United States
-
Alexion PharmaceuticalsTerminatedLysosomal Acid Lipase DeficiencyUnited States
-
Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencyFrance, Poland, United Kingdom, Spain, Mexico, Turkey, Japan, Australia, Russian Federation, United States, Germany, Italy, Czechia, Argentina, Croatia
-
Massachusetts General HospitalAlexion PharmaceuticalsUnknownCholesterol Ester Storage Disease | Lysosomal Acid Lipase DeficiencyUnited States
-
National Heart, Lung, and Blood Institute (NHLBI)Completed
-
Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | Cholesterol Ester Storage Disease(CESD) | LAL-DeficiencyFrance, United States, United Kingdom, Czechia
-
Bellicum PharmaceuticalsNo longer availableHurler Syndrome | Inborn Errors of Metabolism | Metachromatic Leukodystrophy | Inherited Metabolic Disorder | Lysosomal Storage DisorderUnited States
-
Alexion PharmaceuticalsCompletedLysosomal Acid Lipase DeficiencySpain, Germany, Italy, United States, Croatia, Canada, Russian Federation, Denmark, United Kingdom, Belgium, Mexico, Australia, Netherlands, Brazil, Turkey
-
Alexion PharmaceuticalsTerminated
-
Alexion PharmaceuticalsNo longer availableLysosomal Acid Lipase Deficiency
-
Translational Research Center for Medical Innovation...RecruitingNeutral Lipid Storage DiseaseChina, United States, France, Austria, Germany, Italy, Japan, Netherlands, United Kingdom
-
Alexion PharmaceuticalsCompletedLysosomal Acid Lipase Deficiency | LAL-Deficiency | Cholesterol Ester Storage Disease (CESD)France, United Kingdom, United States, Canada, Czechia
-
University of AarhusThe Danish Dairy Research Foundation, DenmarkCompleted
-
National Human Genome Research Institute (NHGRI)Enrolling by invitationParkinson Disease | Gaucher Disease | Lysosomal Storage DisordersUnited States
-
Fondazione SISA (Societa Italiana per lo Studio...Recruiting
-
AlexionCompletedWolman Disease | Lysosomal Acid Lipase DeficiencyUnited States, Canada, United Kingdom, Italy, France
-
TakedaActive, not recruiting
-
CENTOGENE GmbH RostockActive, not recruiting
-
Lysosomal and Rare Disorders Research and Treatment...UnknownGaucher DiseaseUnited States
-
PfizerCompletedGaucher DiseaseIsrael, South Africa, Paraguay
-
PfizerCompletedGaucher DiseaseUnited States, Chile, United Kingdom, Israel, Canada, Spain, South Africa, Italy
-
Hospital St. Joseph, Marseille, FranceCompleted
-
Assistance Publique - Hôpitaux de ParisCompletedGaucher DiseaseFrance
-
Amicus TherapeuticsCompleted
-
Shandong Provincial HospitalRecruitingMetabolism and Nutrition Disorder | Rhythm Nodal | Metabolism Disorder, LipidChina
-
AstraZenecaCompletedUndertreatment of HypercholesterolaemiaSouth Africa
-
University of MinnesotaRecruitingGaucher DiseaseUnited States
-
TakedaNot yet recruiting
-
Duke UniversityRecruiting
-
TakedaCompletedGaucher DiseaseUnited States
-
ShireCompletedGaucher DiseaseIndia
-
PfizerCompleted
-
ShireQuintiles, Inc.Completed
-
ISU Abxis Co., Ltd.CompletedGaucher DiseaseAustralia