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Clinical Trials on Duchenne Muscular Dystrophy in United Kingdom
Total 17713 results
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ML Bio Solutions, Inc.Virginia Commonwealth UniversityCompletedMuscular Dystrophies | Limb Girdle Muscular DystrophyUnited States, Denmark
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Bionano GenomicsColumbia University; University of Iowa; Medical College of Wisconsin; Augusta... and other collaboratorsRecruitingIntellectual Disability | Autism Spectrum Disorder | Fragile X Syndrome | Developmental Disability | Congenital Anomaly | Facioscapulohumeral Muscular Dystrophy 1United States
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Lupin Ltd.Active, not recruitingMyotonic DystrophyFrance, Germany, United Kingdom
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Indiana University School of MedicineMuscular Dystrophy AssociationCompletedMuscular Dystrophy | Arrhythmia | Sudden Cardiac DeathUnited States
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National Eye Institute (NEI)CompletedMacular DegenerationUnited States
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Oxford University Hospitals NHS TrustRecruitingRetinal Degeneration | Retinal Dystrophies | Retinal DiseaseUnited Kingdom
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Astellas Institute for Regenerative MedicineCompletedStargardt's Macular DystrophyUnited States
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Astellas Institute for Regenerative MedicineCompletedStargardt's Macular DystrophyUnited States
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Stanford UniversityUnknownMyotonic Dystrophy Type 1United States
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Great Ormond Street Hospital for Children NHS Foundation...CompletedIdiopathic Scoliosis | Spine Deformities | Neuromuscular DystrophyUnited Kingdom
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University of RochesterCompletedMyotonic DystrophyUnited States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); Imsmed IncorporatedCompleted
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Massachusetts General HospitalRecruiting
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Virginia Commonwealth UniversityUniversity of Western Ontario, Canada, Children's Health Research Institute; Fondazione Serena Onlus - Centro Clinico NeMO MilanoRecruitingCongenital Myotonic DystrophyUnited States, Italy, Canada
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Johns Hopkins UniversityNational Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationHypertrophic Cardiomyopathy (HCM) | Long QT Syndrome (LQTS) | Catecholaminergic Polymorphic Ventricular Tachycardia (CPVT) | Inherited Cardiac Arrythmias | Brugada Syndrome (BrS) | Early Repolarization Syndrome (ERS) | Arrhythmogenic Cardiomyopathy (AC, ARVD/C) | Dilated Cardiomyopathy (DCM) | Muscular... and other conditionsUnited States
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National Institute of Nursing Research (NINR)CompletedCerebral Palsy | Neuromuscular DiseaseUnited States
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University of Kansas Medical CenterHoffmann-La Roche; Seattle Children's Hospital; University of Rochester; University... and other collaboratorsRecruitingFSHDUnited States, Canada, United Kingdom
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Manhattan Eye, Ear & Throat HospitalNorthwell HealthWithdrawnPattern Dystrophy of MaculaUnited States
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University of RochesterNational Institute of Neurological Disorders and Stroke (NINDS); University... and other collaboratorsCompletedMyotonic Dystrophy Type 1United States
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Moorfields Eye Hospital NHS Foundation TrustCompletedRetinal Degeneration | Diabetic Retinopathy | Retinal Dystrophies | AMDUnited Kingdom
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University of OxfordCompletedAge-related Macular Degeneration | Retinitis Pigmentosa | Inherited Retinal Dystrophies | Optic Nerve PathologyUnited Kingdom
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Legacy Health SystemDevers Eye Institute; Lions Eye Bank of Oregon Vision Research Laboratory; Fischer...UnknownFuchs' Corneal Endothelial DystrophyUnited States
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Ionis Pharmaceuticals, Inc.CompletedMyotonic Dystrophy Type 1United States
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Stanford UniversityBiogenActive, not recruitingMyotonic Dystrophy 1United States
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Cure CMDRecruitingEmery-Dreifuss Muscular Dystrophy | Congenital Myasthenic Syndrome | Limb-Girdle Muscular Dystrophy | Congenital Muscular Dystrophy With ITGA7 (Integrin Alpha-7) Deficiency | Alpha-Dystroglycanopathy (Congenital Muscular Dystrophy and Abnormal Glycosylation of Dystroglycan With Severe Epilepsy) and other conditionsUnited States
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Gillette Children's Specialty HealthcareUniversity of MinnesotaCompletedSpinal Muscular Dystrophy | Neuromuscular DisabilityUnited States
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Wake Forest University Health SciencesNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMyotonic Dystrophy Type 2United States
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AMO Pharma LimitedRecruitingCongenital Myotonic DystrophyUnited States, Canada, Australia, New Zealand
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Pixium Vision SACompletedRetinitis Pigmentosa | Choroideremia | Cone Rod DystrophyAustria, Spain, United Kingdom, France, Germany
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Boston Children's HospitalMuscular Dystrophy AssociationRecruitingCentronuclear Myopathy | Myotubular Myopathy | Nemaline Myopathy | Central Core Disease | Congenital Fiber Type Disproportion | Multiminicore Disease | Rigid Spine Muscular Dystrophy | Undefined Congenital MyopathyUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedCardiomyopathy, Hypertrophic | Muscular Dystrophy, OculopharyngealUnited States
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Insmed IncorporatedMuscular Dystrophy AssociationCompleted
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Acceleron Pharma Inc. (a wholly owned subsidiary...TerminatedCharcot-Marie-Tooth Disease | Facioscapulohumeral Muscular DystrophyUnited States, Spain, Canada
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State University of New York at BuffaloActive, not recruitingFuchs DystrophyUnited States
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Harmony Biosciences, LLCActive, not recruitingMyotonic Dystrophy 1 | Excessive Daytime SleepinessUnited States, Canada
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Medical College of WisconsinCompletedCataract | Fuchs' Corneal DystrophyUnited States
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Wake Forest University Health SciencesTerminatedFuchs Dystrophy | Cystoid Macular EdemaUnited States
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GlaxoSmithKlineCompleted
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FDA Office of Orphan Products DevelopmentCompletedMuscular DystrophiesUnited States
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Cornea Research Foundation of AmericaCompletedBullous Keratopathy | Fuchs' Endothelial Corneal Dystrophy | Iridocorneal Endothelial Syndrome | Posterior Polymorphous DystrophyUnited States
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University College, LondonRecruitingNon-Dystrophic MyotoniaUnited Kingdom
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Edgewise Therapeutics, Inc.CompletedMuscular DystrophiesUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Terminated
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University of Texas Southwestern Medical CenterWithdrawnCorneal Epithelial DystrophyUnited States
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Wake Forest University Health SciencesCompleted
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Massachusetts Eye and Ear InfirmaryRecruitingFuchs' Endothelial Corneal DystrophyUnited States
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Katherine MathewsNational Institute of Neurological Disorders and Stroke (NINDS)Recruiting
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King's College LondonUnknownRecessive Dystrophic Epidermolysis BullosaUnited Kingdom
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King's College LondonUniversity College, LondonCompletedRecessive Dystrophic Epidermolysis BullosaUnited Kingdom