- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Durability
Total 1520 results
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Assistance Publique - Hôpitaux de ParisUnknownPrader-Willi Syndrome | Silver Russell SyndromeFrance
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Children's Healthcare of AtlantaCompleted
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Green Cross CorporationCompletedMucopolysaccharidosis IIKorea, Republic of
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University of South FloridaJohns Hopkins All Children's HospitalCompletedObsessive-compulsive Disorder | Prader Willi SyndromeUnited States
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Janssen-Ortho Inc., CanadaCompletedAutistic Disorder | Developmental Disabilities | Rett Syndrome | Asperger Syndrome | DCild Development Disorders, Pervasive
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National Institute on Aging (NIA)UnknownDown Syndrome | Alzheimer's DiseaseUnited States
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Eunice Kennedy Shriver National Institute of Child...University of MinnesotaCompleted
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Holland Bloorview Kids Rehabilitation HospitalCanadian Institutes of Health Research (CIHR)RecruitingStroke | Cerebral Palsy | Autism Spectrum Disorder | Spinal Cord Injuries | Acquired Brain Injury | Developmental Disability | Developmental Coordination Disorder | Motor Skills DisordersCanada
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Eunice Kennedy Shriver National Institute of Child...RecruitingEpilepsy | Obesity | Intellectual Disability | Microcephaly | Nervous System Malformations | HypogonadismsUnited States
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AO GENERIUMRecruitingMetabolic Diseases | Mucopolysaccharidosis Type IIRussian Federation
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Nova Mentis Life Science CorpFourthWall TestingRecruitingAutism Spectrum Disorder | Fra(X) SyndromeUnited States
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JCR Pharmaceuticals Co., Ltd.RecruitingMucopolysaccharidosis IIUnited States, Germany, Spain, France, Brazil, Argentina, Turkey, United Kingdom, Poland, Italy
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Nelly PitteloudRecruitingDown Syndrome | Cognitive Decline | Alzheimer Disease, Early Onset | Olfaction DisordersSwitzerland
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University of MiamiUniversity of Pennsylvania; National Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health (NIH) and other collaboratorsRecruiting
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Denali Therapeutics Inc.Active, not recruitingMucopolysaccharidosis IIUnited States, Netherlands, Canada, United Kingdom
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Denali Therapeutics Inc.Enrolling by invitationMucopolysaccharidosis IIUnited States, Canada, Belgium, Czechia, Netherlands
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JCR Pharmaceuticals Co., Ltd.Enrolling by invitationMucopolysaccharidosis IIUnited States
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Children's Hospital of PhiladelphiaCompletedCardiac Surgery | Congenital Heart Disease | Fetal Neuroprotection | Periventricular Leucomalacia | Brain Development | Neurodevelopmental DisabilityUnited States
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Rocket Pharmaceuticals Inc.Active, not recruitingDanon DiseaseUnited States
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JCR Pharmaceuticals Co., Ltd.Completed
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Fundación Pública Andaluza para la Investigación...Delos ClinicalCompleted
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REGENXBIO Inc.CompletedMucopolysaccharidosis IIBrazil, United States, United Kingdom
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Christopher Hartnick, M.D.University of Pittsburgh; Emory University; Children's Hospital Medical Center... and other collaboratorsCompletedSleep Apnea, Obstructive | Down SyndromeUnited States
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REGENXBIO Inc.Enrolling by invitation
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Cindy CisnerosCompletedDown Syndrome | Aneuploidy | Trisomy 21 | Trisomy 18 | Trisomy 13United States
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National Human Genome Research Institute (NHGRI)CompletedAutism | Asperger's Syndrome | Rett's DisorderUnited States
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ArmaGen, IncCompletedMucopolysaccharidosis IIUnited States, Germany, Philippines
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CHU de Quebec-Universite LavalCanadian Institutes of Health Research (CIHR); Laval University; Genome British... and other collaboratorsCompletedTrisomy 21 | Trisomy 18 | Trisomy 13Canada
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Federal University of São PauloUnknownDepressive Disorder | Obesity | Obsessive-Compulsive Disorder | Prader-Willi SyndromeBrazil
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University of Mississippi Medical CenterCompletedAutistic Disorder | Rett Syndrome | Asperger Syndrome | Pervasive Developmental Disorder | Childhood Disintegrative DisorderUnited States
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Children's Hospital Medical Center, CincinnatiEunice Kennedy Shriver National Institute of Child Health and Human Development...RecruitingAutism Spectrum Disorder | Autistic Disorder | Fragile X Syndrome | Asperger SyndromeUnited States
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Rocket Pharmaceuticals Inc.RecruitingDanon DiseaseUnited States
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University of ManchesterManchester University NHS Foundation Trust; Great Ormond Street Hospital for... and other collaboratorsRecruiting
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GC Biopharma CorpRecruitingMucopolysaccharidosis II | Hunter SyndromeKorea, Republic of
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Murdoch Childrens Research InstituteNational Health and Medical Research Council, Australia; Royal Children's Hospital and other collaboratorsRecruitingCommunicable Diseases | Quality of Life | Inflammation | Obesity | Congenital Abnormalities | Genetics | Healthy Aging | Child Development | Diet | Mental Health | Disability | Injuries | Cognition | Child Health | Environmental Exposure | Noncommunicable Diseases | Physical Fitness | Intergenerational Relations | Social Determinants... and other conditionsAustralia
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Denali Therapeutics Inc.RecruitingMucopolysaccharidosis IIUnited States, Spain, United Kingdom, Czechia, France, Canada, Italy, Belgium, Netherlands, Germany, Argentina, Sweden, Turkey, Colombia, Brazil
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Vanderbilt University Medical CenterVanderbilt Kennedy CenterRecruitingAlzheimer Disease | Down Syndrome | Down Syndrome, Partial Trisomy 21United States
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Inspire Medical Systems, Inc.National Institutes of Health (NIH); National Institute on Deafness and Other...RecruitingObstructive Sleep Apnea | Down SyndromeUnited States
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Taipei Tzu Chi Hospital, Buddhist Tzu Chi Medical...CompletedBody Weight Changes | Sarcopenia | Prader Labhart Willi SyndromeTaiwan
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Children's Hospital Medical Center, CincinnatiNational Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationObstructive Sleep Apnea | Down SyndromeUnited States
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Natera, Inc.CompletedTrisomy 21 | Trisomy 18 | Trisomy 13 | Vanishing TwinUnited States
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Homology Medicines, IncWithdrawnMucopolysaccharidosis IIUnited States, Canada
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JCR Pharmaceuticals Co., Ltd.Active, not recruitingMucopolysaccharidosis IIBrazil
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University Hospital, GrenobleCompletedSleep Apnea, Obstructive | Down Syndrome | PolysomnographyFrance
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ShireCompletedMucopolysaccharidosis IIUnited States, United Kingdom, Brazil, Germany
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AO GENERIUMCompletedA Multi-cohort Study of the Tolerance, Safety, and Pharmacokinetics of GNR-055 in Healthy VolunteersMetabolic Diseases | Mucopolysaccharidosis Type IIRussian Federation
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Hacettepe UniversityCompletedChewing Problem | Swallowing DisorderTurkey
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Hospices Civils de LyonUnknownWilliams-Beuren Syndrome | Micro-duplication 7q11.23 Syndrome | VasculopathyFrance
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University Hospital, ToursCompletedHealthy Volunteers | Autism | Fragile-X Syndrome (FXS)France
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GlaxoSmithKlineCompletedMucopolysaccharidosis IIJapan