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Clinical Trials on Dysautonomia, Familial
Total 1763 results
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DyAnsys, Inc.Completed
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University College, LondonNational Institutes of Health (NIH)Not yet recruitingEpilepsy | Vagus Nerve Diseases | Vagus Nerve Autonomic Disorder
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Vanderbilt University Medical CenterRecruitingSupine Hypertension | Autonomic FailureUnited States
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University of Southern CaliforniaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedObesity | Obesity, Childhood | Obesity; FamilialUnited States
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University of Colorado, DenverNational Institutes of Health (NIH)RecruitingRacially/Ethnically Diverse Families From Urban SettingsUnited States
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Meir Medical CenterRambam Health Care Campus; Hadassah Medical Organization; Assaf-Harofeh Medical... and other collaboratorsUnknownPatella, Familial Recurrent Dislocation OfIsrael
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Rambam Health Care CampusWithdrawnFamilial Mediterranean Fever (FMF )
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AstraZenecaRecruiting
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Washington University School of MedicineEnrolling by invitationMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Lou Gehrig Disease | Familial Amyotrophic Lateral Sclerosis | Motor Neuron Disease, FamilialUnited States
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Akcea TherapeuticsUnited BioSource, LLCRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, France, Greece, Italy, Spain, Canada, Germany, Portugal
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PfizerCompletedPolyneuropathy | Hereditary Transthyretin Amyloidosis (ATTRv)Spain
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Montreal Heart InstituteCanadian Institutes of Health Research (CIHR)Enrolling by invitationCardiomyopathies | Hypertrophic Cardiomyopathy | Hypertrophic Obstructive Cardiomyopathy | Familial Hypertrophic CardiomyopathyCanada
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PfizerCompletedTransthyretin Amyloidosis | Transthyretin Gene MutationsUnited States, France, Spain, Taiwan, Israel, Korea, Republic of, Denmark, Canada, Netherlands, Japan, Sweden, Brazil, Mexico, Argentina, Portugal, Belgium, Bulgaria, Cyprus, Germany, Italy, Malaysia, Romania, Saudi Arabia, Turkey, United...
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Chylomicronemia Syndrome | Lipoprotein Lipase Deficiency | Hyperlipoproteinemia Type 1United States, Canada, Germany, Israel, Italy, South Africa, Spain, United Kingdom, Brazil, France, Netherlands
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Chylomicronemia Syndrome | Lipoprotein Lipase Deficiency | Hyperlipoproteinemia Type 1Canada
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University of MichiganCompletedNAFLD | Nonalcoholic Steatohepatitis | Familial Partial LipodystrophyUnited States
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Institute of Liver and Biliary Sciences, IndiaKEM Hospital Research Centre; Apollo Hospital, New Delhi, India; Jaslok Hospital... and other collaboratorsRecruitingProgressive Familial Intrahepatic CholestasisIndia
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University Medical Center GroningenEnrolling by invitationProgressive Familial Intrahepatic CholestasisNetherlands
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Genetic Disease InvestigatorsCompletedVenous Insufficiency | Postural Orthostatic Tachycardia Syndrome | Dysautonomia | Ehlers Danlos Syndrome | External HydrocephalusUnited States
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University of MichiganNot yet recruitingPregnancy Related | Infant Behavior | Obesity; FamilialUnited States
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University of Alabama at BirminghamNational Institute on Minority Health and Health Disparities (NIMHD)Active, not recruitingObesity | Obesity, Childhood | Obesity; FamilialUnited States
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University of California, San FranciscoDestination: Home SV; Sí Se Puede Collective; Sacred Heart Community Service; County...RecruitingFamilies Experiencing Homelessness and/or Housing InstabilityUnited States
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University of California, Los AngelesVA Greater Los Angeles Healthcare SystemWithdrawnVeteran Families | Family Communications | Civilian Life ReintegrationUnited States
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AlbireoActive, not recruitingProgressive Familial Intrahepatic CholestasisUnited States, Spain, Netherlands, United Kingdom, Turkey, Canada, Italy, Germany, France, Israel, Australia, Belgium, Poland, Saudi Arabia, Sweden
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Yale UniversityCompletedFamilial Alcoholism VulnerabilityUnited States
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Hacettepe UniversityCompletedGastrointestinal Diseases | Autonomic Nervous System DiseaseTurkey
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Verve Therapeutics, Inc.Not yet recruitingHypercholesterolemia | Atherosclerotic Cardiovascular Disease | Heterozygous Familial HypercholesterolemiaNew Zealand, United Kingdom
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Akcea TherapeuticsRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, Canada
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Verve Therapeutics, Inc.Active, not recruitingHypercholesterolemia | Atherosclerotic Cardiovascular Disease | Heterozygous Familial HypercholesterolemiaNew Zealand, United Kingdom
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University of MessinaUniversità degli Studi di Ferrara; University of Pavia; Careggi Hospital; Fondazione...UnknownPatient-Reported Outcome Measures in Wild-Type and Variant Cardiac Transthyretin Amyloidosis (ITALY)Transthyretin AmyloidosisItaly
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RWTH Aachen UniversityCompletedCognitive Impairment | Postural Tachycardia Syndrome | Dysautonomia | Pure Autonomic Failure | Ehlers-Danlos Syndrome | Autonomic FailureGermany
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Royal Adelaide HospitalCompletedAutonomic Nervous System Diseases | Blood Pressure | Hypotension | Baroreflex Failure
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Federal University of MaranhaoCompletedBreast Neoplasms | Autonomic Nervous System Diseases
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Yale UniversityNational Institute on Alcohol Abuse and Alcoholism (NIAAA)RecruitingFamilial Alcoholism VulnerabilityUnited States
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AlbireoApproved for marketingProgressive Familial Intrahepatic CholestasisUnited States
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Novartis PharmaceuticalsCompletedNon Familial Chylocmicronemia Syndrome (Non-FCS)United States, Canada, Russian Federation
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National Liver Institute, EgyptUnknownProgressive Familial Intrahepatic CholestasisEgypt
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Alnylam PharmaceuticalsCompletedFamilial Amyloidotic Cardiomyopathy (FAC)United States, France, Spain, United Kingdom, Belgium, Brazil
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Novartis PharmaceuticalsCompletedColchicine Resistant/Intolerant Familial Mediterranean FeverIsrael
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M.D. Anderson Cancer CenterCompletedAttenuated Familial Adenomatous Polyposis | Deleterious Familial Adenomatous PolyposisUnited States
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Bahçeşehir UniversityCompletedLong Covid19 | Autonomic DysfunctionTurkey
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Federal University of Health Science of Porto AlegreCompletedVertebra; Degeneration | Other Disorders of the Autonomic Nervous SystemBrazil
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University Hospital, GrenobleCompletedSleep | Autonomic Nervous System DiseasesFrance
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Immunovia, Inc.CompletedPancreatic Ductal Adenocarcinoma | Familial Pancreatic Cancer | FAMMM - Familial Atypical Mole Malignant Melanoma SyndromeUnited States, Sweden, Canada, Spain, United Kingdom
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National Institute of Neurological Disorders and...Terminated
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Massachusetts General HospitalPfizer; Akcea Therapeutics; Alnylam Pharmaceuticals; Eidos Therapeutics, a BridgeBio...RecruitingHeart Failure | Amyloidosis | Heart Failure, Diastolic | Transthyretin AmyloidosisUnited States
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Elif OralCompletedFatty Liver | Hypertriglyceridemia | NASH - Nonalcoholic Steatohepatitis | Familial Partial LipodystrophyUnited States
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Daiichi Sankyo, Inc.TerminatedAtherosclerosis | Heterozygous Familial HypercholesterolemiaUnited States, United Kingdom, Spain, South Africa, Israel, Canada, Netherlands, Norway, Sweden
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Taipei Tzu Chi Hospital, Buddhist Tzu Chi Medical...UnknownOSA | Adherence, Patient | Autonomic Dysfunction | PAPTaiwan
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National Institute of Neurological Disorders and...CompletedHypertension | Healthy | Autonomic Nervous System DiseaseUnited States