- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Epidermolysis Bullosa Dystrophica in United States
Total 670 results
-
Solid Biosciences Inc.Active, not recruitingDuchenne Muscular DystrophyUnited States
-
ML Bio Solutions, Inc.RecruitingLimb-Girdle Muscular Dystrophy Type 2I (LGMD2I)United States, Netherlands, United Kingdom, Denmark, Australia, Italy, Norway
-
Trefoil Therapeutics, Inc.CompletedFuchs' Endothelial Dystrophy | Fuchs Dystrophy | FuchsUnited States
-
Neurotech PharmaceuticalsCompletedRetinitis PigmentosaUnited States
-
Santen Inc.ActualEyes Inc.RecruitingFuchs Endothelial Corneal DystrophyUnited States
-
Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
-
Hugo W. Moser Research Institute at Kennedy Krieger...Johns Hopkins UniversityTerminatedDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States
-
Sarepta Therapeutics, Inc.University College, London; Catholic University of the Sacred Heart; University... and other collaboratorsCompletedDuchenne Muscular DystrophyUnited Kingdom, United States, France, Italy
-
University of OxfordCompleted
-
The Duchenne RegistryParent Project Muscular DystrophyRecruiting
-
Chelsea and Westminster NHS Foundation TrustUnknownBullous EmphysemaUnited Kingdom
-
Food and Drug Administration (FDA)National Eye Institute (NEI)RecruitingAge-Related Macular Degeneration | Retinal Degeneration | Retinitis Pigmentosa | Usher Syndromes | Cone Dystrophy | Rod Dystrophy | Cone Rod Dystrophy | Hydroxychloroquine Retinopathy | Late-Onset Retinal Degeneration | Rod Cone DystrophyUnited States
-
Bioblast Pharma Ltd.CompletedOculopharyngeal Muscular DystrophyUnited States, Israel, Canada
-
Massachusetts Eye and Ear InfirmaryCompletedGlaucoma | Retinitis Pigmentosa | Blindness | Hemianopsia | Hemianopia | Peripheral Visual Field DefectUnited States
-
Baylor College of MedicineUnknownHeart Failure | Muscular Dystrophy | Dilated CardiomyopathyUnited States
-
Columbia UniversityActive, not recruitingAge-related Macular Degeneration | Retinitis Pigmentosa | Vitelliform Macular Dystrophy | Choroidal Ischemia | Central Serous RetinopathyUnited States
-
Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
-
Nationwide Children's HospitalNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes...CompletedDuchenne Muscular DystrophyUnited States
-
Stanford UniversityBiogenActive, not recruitingMyotonic Dystrophy 1United States
-
Cure CMDCongenital Muscle Disease International RegistrWithdrawnLAMA2-MD (Merosin Deficient Congenital Muscular Dystrophy, MDC1A)United States
-
Avidity Biosciences, Inc.RecruitingPhase 1/2 Study of AOC 1020 in Adults With Facioscapulohumeral Muscular Dystrophy (FSHD) (FORTITUDE)Muscular Dystrophies | Muscular Dystrophy, Facioscapulohumeral | FSHD | Facio-Scapulo-Humeral Dystrophy | FMD | Facioscapulohumeral Muscular Dystrophy 1 | FSHD2 | FSHD1 | FMD2 | Fascioscapulohumeral Muscular Dystrophy | Fascioscapulohumeral Muscular Dystrophy Type 1 | Fascioscapulohumeral Muscular Dystrophy... and other conditionsUnited States, United Kingdom, Canada
-
Children's Healthcare of AtlantaWithdrawnScoliosis | Duchenne's Muscular DystrophyUnited States
-
Virginia Commonwealth UniversityUniversity of Western Ontario, Canada, Children's Health Research Institute; Fondazione Serena Onlus - Centro Clinico NeMO MilanoRecruitingCongenital Myotonic DystrophyUnited States, Italy, Canada
-
Epirium Bio Inc.CompletedBecker Muscular DystrophyUnited States
-
Nationwide Children's HospitalParent Project Muscular DystrophyCompletedBecker Muscular Dystrophy | Sporadic Inclusion Body MyositisUnited States
-
Oregon Health and Science UniversityEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsActive, not recruitingPantothenate Kinase-Associated NeurodegenerationUnited States
-
MD Stem CellsUnknownGlaucoma | Macular Degeneration | Retinal Disease | Hereditary Retinal Dystrophy | Optic Nerve DiseaseUnited States
-
Kevin FlaniganMuscular Dystrophy AssociationTerminated
-
University of OxfordMoorfields Eye Hospital NHS Foundation Trust; Oxford University Hospitals NHS...Completed
-
University of FloridaChildren's Hospital of Philadelphia; National Institute of Arthritis and Musculoskeletal... and other collaboratorsRecruitingDuchenne Muscular Dystrophy | Becker Muscular DystrophyUnited States
-
Second Sight Medical ProductsTerminatedRetinitis PigmentosaUnited States
-
Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy | GNE MyopathyUnited States, Israel
-
Pixium Vision SACompletedRetinitis Pigmentosa | Choroideremia | Cone Rod DystrophyAustria, Spain, United Kingdom, France, Germany
-
REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
-
Ultragenyx Pharmaceutical IncCompletedHereditary Inclusion Body Myopathy (HIBM)United States
-
Wake Forest University Health SciencesNational Institute of Neurological Disorders and Stroke (NINDS)RecruitingMyotonic Dystrophy Type 2United States
-
Vanderbilt University Medical CenterRecruitingDuchenne Muscular DystrophyUnited States
-
National Institute of Nursing Research (NINR)CompletedCerebral Palsy | Neuromuscular DiseaseUnited States
-
Jett Foundation, Inc.Pfizer; Hoffmann-La Roche; Italfarmaco; Nationwide Children's Hospital; Capricor... and other collaboratorsCompletedDuchenne Muscular Dystrophy | Rare Diseases | Disability Physical | Burden, Dependency | Impairment | Disease ManagementUnited States
-
Ohio State UniversityGilead SciencesCompletedMyotonic Dystrophy 1 | Myotonia Congenita | Paramyotonia CongenitaUnited States
-
National Cancer Institute (NCI)CompletedSkin Diseases | Virus Diseases | Healthy | Retinal Degeneration | Muscular DystrophyUnited States
-
Anne M. ConnollyAnn & Robert H Lurie Children's Hospital of Chicago; Children's Hospital Medical... and other collaboratorsRecruiting
-
Shriners Hospitals for ChildrenCompletedDuchenne Muscular DystrophyUnited States
-
Vanderbilt University Medical CenterRecruitingDuchenne Muscular DystrophyUnited States
-
National Institute of Neurological Disorders and...TerminatedMyotonic Dystrophy Type-1 | Myotonic Dystrophy Type-2United States
-
Spark Therapeutics, Inc.Children's Hospital of Philadelphia; University of IowaActive, not recruitingLeber Congenital Amaurosis | Inherited Retinal Dystrophy Due to RPE65 MutationsUnited States
-
Skulpt, Inc.National Institute of Neurological Disorders and Stroke (NINDS)CompletedDuchenne Muscular DystrophyUnited States
-
MeiraGTx UK II LtdSyne Qua Non LimitedCompletedEye Diseases | Retinal Diseases | Eye Diseases, Hereditary | Leber Congenital Amaurosis (LCA)United States, United Kingdom
-
National Eye Institute (NEI)CompletedRetinal Degeneration | Retinitis PigmentosaUnited States, India, Pakistan, China
-
Neurotech PharmaceuticalsCompletedRetinitis PigmentosaUnited States