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Clinical Trials on Erythropoietic Protoporphyria
Total 83 results
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Zymenex A/SCompleted
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Nordlandssykehuset HFUniversity of Oslo; Norwegian University of Science and Technology; The University... and other collaboratorsRecruitingPorphyria, Acute IntermittentNorway
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Alnylam PharmaceuticalsCompletedAcute Intermittent PorphyriaUnited States, United Kingdom, Sweden
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Digna Biotech S.L.University of Navarra; Porphyria Centre Sweden; UniQure N.V.; Nationales Centrum...CompletedAcute Intermittent PorphyriaSpain
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Digna Biotech S.L.University of Navarra; Porphyria Centre Sweden; UniQure N.V.Completed
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Alnylam PharmaceuticalsApproved for marketingAcute Hepatic Porphyria
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The University of Texas Medical Branch, GalvestonCompletedPorphyria Cutanea TardaUnited States
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Assistance Publique - Hôpitaux de ParisAssociation pour l'Etude des Fonctions Digestives (AEFD)UnknownPorphyria Cutanea TardaFrance
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National Center for Research Resources (NCRR)University of TexasCompleted
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Association pour la Recherche en Medecine InterneNot yet recruitingAcute Hepatic Porphyria
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Alnylam PharmaceuticalsRecruitingAcute Hepatic PorphyriaBelgium, France, Germany, United Kingdom, United States, Italy, Switzerland, Sweden
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The University of Texas Medical Branch, GalvestonCompletedAcute PorphyriasUnited States
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The University of Texas Medical Branch, GalvestonTerminatedHereditary Coproporphyria | Acute Intermittent Porphyria | Variegate PorphyriaUnited States
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Icahn School of Medicine at Mount SinaiRecruiting
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University of South FloridaUniversity of Miami; University of Alabama at Birmingham; Icahn School of Medicine... and other collaboratorsCompletedPorphyriasUnited States
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Protagonist Therapeutics, Inc.CompletedChronic Anemia | β-thalassemia | Ineffective ErythropoiesisUnited States, Malaysia, Turkey, Thailand, United Kingdom, Italy, Lebanon, Tunisia, Greece
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Icahn School of Medicine at Mount SinaiRecruitingAcute Intermittent Porphyria (AIP)United States
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Fundación Grupo de Investigación en Cuidados Intensivos...Recordati Rare DiseasesActive, not recruiting
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Alnylam PharmaceuticalsCompletedAcute Hepatic PorphyriaUnited States, Belgium, Bulgaria, France, Italy, Mexico, Spain, Taiwan, United Kingdom, Netherlands, Korea, Republic of, Switzerland, Czechia, Poland, Finland, Australia, Germany, Israel, Norway, South Africa
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Protagonist Therapeutics, Inc.Completedβ-thalassemia | Ineffective ErythropoiesisMalaysia, Thailand, United States, Greece, United Kingdom, Turkey, Lebanon, Tunisia
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Nordlandssykehuset HFThe Royal Norwegian Ministry of HealthActive, not recruitingAcute Intermittent PorphyriaNorway
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The University of Texas Medical Branch, GalvestonActive, not recruitingHereditary Coproporphyria | Acute Intermittent Porphyria | Variegate PorphyriaUnited States
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University of California, San FranciscoNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... and other collaboratorsCompletedAcute Intermittent Porphyria (AIP) | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP)United States
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National Institute of Cardiology, Warsaw, PolandInstitute of Hematology and Transfusion Medicine, WarsawCompletedPorphyrias, HepaticPoland
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Asociación para Evitar la Ceguera en MéxicoRecruitingMethylprednisolone | Treatment | Erythropoietin | Toxic Optic NeuropathyMexico
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Fondazione Policlinico Universitario Agostino Gemelli...CompletedIron-deficiency | Anemia | Iron Deficiency Anemia | Iron Deficiency Anemia Treatment | Blood Loss Anemia | Erythropoiesis AbnormalItaly
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Alnylam PharmaceuticalsCompletedPorphyria, Acute Intermittent | Acute Intermittent Porphyria (AIP) | Acute Hepatic Porphyria (AHP) | Acute PorphyriaSweden
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Wake Forest University Health SciencesNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); Gilead... and other collaboratorsCompleted
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Alnylam PharmaceuticalsCompletedAcute Hepatic Porphyria | Acute Intermittent Porphyria | Porphyria, Acute Intermittent | Acute Porphyria | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP) | ALA Dehydratase Deficient Porphyria (ADP)United States, Spain, United Kingdom, Korea, Republic of, Australia, Bulgaria, Canada, Denmark, Finland, France, Germany, Italy, Japan, Mexico, Netherlands, Poland, Sweden, Taiwan
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Alnylam PharmaceuticalsTerminatedAcute Hepatic Porphyria | Acute Intermittent Porphyria (AIP) | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP) | ALA Dehydratase Deficient Porphyria (ADP) | Hepatic Porphyrias | Porphyria AcuteUnited States
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Vanderbilt University Medical CenterRecruitingPostural Orthostatic Tachycardia Syndrome | Acute Hepatic PorphyriaUnited States
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National Center for Research Resources (NCRR)Icahn School of Medicine at Mount SinaiCompletedMetabolism, Inborn Errors | Leukodystrophy, Globoid Cell | Tay-Sachs Disease | Porphyria, ErythropoieticUnited States
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Atlantic Health SystemTerminatedBrain Injury | Intraventricular Hemorrhage | Randomized Clinical Trial | Infant, Premature | Periventricular Leukomalacia | Neurodevelopmental Outcomes | ErythropoietinUnited States