- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Factor X Deficiency
Total 13811 results
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IRCCS San RaffaeleFondazione TelethonRecruitingChronic Granulomatous Disease X-linked (X-CGD)Italy
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Bio Products LaboratoryCompletedCommon Variable Immunodeficiency | Primary Immune Deficiency Disorders | Hyper-IgM Syndrome | X-linked AgammaglobulinaemiaUnited States, United Kingdom, Hungary
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PfizerCompletedFactor VIII Deficiency, Congenital | Hemophilia A, Congenital | Factor 8 Deficiency, Congenital | Autosomal Hemophilia A | Classic Hemophilia
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Great Ormond Street Hospital for Children NHS Foundation...National Institute for Health Research, United Kingdom; The Freya FoundationRecruitingPyruvate Dehydrogenase Complex Deficiency | Pyruvate Dehydrogenase E1 Alpha Deficiency | Pyruvate Dehydrogenase E1-Beta Deficiency | Pyruvate Dehydrogenase E2 Deficiency | Pyruvate Dehydrogenase Phosphatase DeficiencyUnited Kingdom
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Aarhus University HospitalLaboratory for Proteome Analysis and Protein Characterization, Aarhus UniversityUnknownDiabetes Complications | Polyneuropathies | Insulin-like Growth Factor I | Insulin-like Growth Factor II | Nerve Growth FactorsDenmark
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Region SkaneCompletedCoagulopathy, Consumption | Coagulation Factor Deficiency | Vitamin K DeficiencySweden
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IpsenCompletedGrowth Disorders | Insulin-Like Growth Factor-1 DeficiencyUnited States
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Bio Products LaboratoryCompletedCommon Variable Immunodeficiency | Primary Immune Deficiency Disorders | X-linked Agammaglobulinaemia | Hyperimmunoglobulin M SyndromeUnited States
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AryoGen Pharmed Co.CompletedFactor VII Deficiency | Hemophilia A With Inhibitor | Hemophilia B With Inhibitor | Glanzmann's ThrombastheniaIran, Islamic Republic of
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National Institute of Allergy and Infectious Diseases...RecruitingChronic Granulomatous Disease (CGD) | X-Linked Severe Combined Immune Deficiency (XSCID) | Leukocyte Adhesion Deficiency 1 (LAD) | Graft Versus Host Disease (cGvHD)United States
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University of PittsburghNational Institute of Neurological Disorders and Stroke (NINDS); Rare Diseases...RecruitingPyruvate Dehydrogenase Complex Deficiency DiseaseUnited States
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Cairo UniversityCompletedLeiden Factor V Deficiency,Preeclampsia | Doppler Examination | Palental Pathology
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Oslo University HospitalUniversity of OsloActive, not recruitingAortic Dissection | Factor X InhibitionNorway
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency, Type AUnited States, Spain, Israel, Norway, Turkey, United Kingdom
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Orphatech Pharmaceuticals, GmbHWithdrawnMolybdenum Cofactor Deficiency Type AAustralia
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Assiut UniversityNot yet recruitingVitiligo | CD25 Deficiency | Chemokine (C-X-C Motif) | Tregs
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency, Type AUnited States, Australia, Netherlands, United Kingdom, Tunisia
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Bioverativ, a Sanofi companyCompletedFactor VIII DeficiencyUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, France, Germany, Greece, Hungary, Italy, Japan, Korea, Republic of, Mexico, Netherlands, Spain, Taiwan, United Kingdom
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IpsenTerminatedPrimary Insulin-like Growth Factor-1 DeficiencyUnited States
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Fairview University Medical CenterTerminatedImmunologic Deficiency Syndromes | Common Variable Immunodeficiency | Severe Combined Immunodeficiency | Chronic Granulomatous Disease | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Graft Versus Host Disease | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | Virus-Associated... and other conditionsUnited States
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IpsenTerminatedrhGH and rhIGF-1 Combination Therapy in Children With Short Stature Associated With IGF-1 DeficiencyInsulin-like Growth Factor-1 DeficiencyUnited States
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Yale UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedHypophosphatemic Rickets, X Linked DominantUnited States
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INEFC-LleidaInstitut Català de la Salut; Universitat de Lleida; Fundacio d'Investigacio en...CompletedCardiovascular Risk Factor | Metabolic Syndrome X | Lifestyle-related Condition | Lifestyle Risk ReductionSpain
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Hubert Serve, Prof., MDUnknown
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University of Colorado, DenverThe University of Texas Health Science Center, Houston; Bayer; Emory University; Rush University Medical Center and other collaboratorsCompleted
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University of California, Los AngelesNational Heart, Lung, and Blood Institute (NHLBI); Boston Children's Hospital; California Institute for Regenerative Medicine (CIRM) and other collaboratorsRecruitingGranulomatous Disease, Chronic, X-linkedUnited States
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Baylor College of MedicineChildren's National Research InstituteRecruitingOrnithine Transcarbamylase Deficiency | Urea Cycle Disorder | Carbamyl Phosphate Synthetase Deficiency | Argininosuccinic Aciduria | Hyperargininemia | Citrullinemia 1 | ARGI Deficiency | ASL Deficiency | ASS Deficiency | NAGS DeficiencyUnited States
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University of PennsylvaniaTerminatedOrnithine Transcarbamylase Deficiency Disease
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Eunice Kennedy Shriver National Institute of Child...Children's National Research InstituteTerminatedPhase I Pilot Study of Liver-Directed Gene Therapy for Partial Ornithine Transcarbamylase DeficiencyOrnithine Transcarbamylase Deficiency Disease
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Kyowa Kirin Co., Ltd.Active, not recruiting
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American Thrombosis and Hemostasis NetworkSanofi; Pfizer; Genentech, Inc.; CSL Behring; Hemophilia of Georgia, Inc.; Hemab TherapeuticsRecruitingHemophilia | Thrombosis | Thrombophilia | Sickle Cell Disease | Thalassemia | Bleeding Disorder | Von Willebrand Diseases | Factor IX Deficiency | Connective Tissue Disorder | Factor VIII Deficiency | Hematologic Disorder | Rare Bleeding Disorder | Platelet DisorderUnited States
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Markus KnuppMerian Iselin Klinik; Basel Academy for Quality and Research in MedicineRecruiting
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University of MinnesotaEnrolling by invitationIron-deficiency | Anemia | Malaria | Iron Deficiency Anemia | Anemia, Iron Deficiency | Anemia in ChildrenUganda
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University of Sao Paulo General HospitalMerit Medical Systems, Inc.RecruitingHemophilia | Arthropathy | Synovitis | Hemarthrosis | Embolization | Clotting Factor DeficiencyBrazil
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Arcturus Therapeutics, Inc.RecruitingOTC Deficiency | Ornithine Transcarbamylase Deficiency | OTCDSpain, Belgium, United Kingdom, Sweden
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iECURE, Inc.RecruitingUrea Cycle Disorders, Inborn | Ornithine Transcarbamylase Deficiency | Ornithine Transcarbamylase Deficiency Disease | Ornithine Carbamoyltransferase Deficiency (Disorder)United Kingdom
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GenethonActive, not recruitingX-Linked Chronic Granulomatous DiseaseFrance
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Stanford UniversityNot yet recruitingLiver Failure | Liver Cirrhosis | Hemophilia A | Hemophilia B | Hemophilia | Liver Transplant Disorder | Coagulation Factor DeficiencyUnited States
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GenethonActive, not recruitingX-Linked Chronic Granulomatous DiseaseUnited Kingdom
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Joint Authority for Päijät-Häme Social and Health...Tampere UniversityActive, not recruiting
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University of California, DavisNational Institute of Mental Health (NIMH)CompletedFragile X PremutationUnited States
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Illumina, Inc.CompletedDetection and Genotyping of Factor V and Factor II Point Mutations
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Washington University School of MedicineRecruitingSevere Combined Immunodeficiency | Chronic Granulomatous Disease | DiGeorge Syndrome | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | X-linked Lymphoproliferative Syndrome | X-linked Agammaglobulinemia | Chediak-Higashi Syndrome | IPEX | Autoimmune Lymphoproliferative Syndrome | Common Variable... and other conditionsUnited States
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IpsenCompletedGrowth Disorders | Insulin-Like Growth Factor-1 DeficiencyUnited States
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedX-Linked HypophosphatemiaUnited States
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Kyowa Kirin Co., Ltd.Active, not recruitingX-linked Hypophosphatemia (XLH)China
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Kyowa Kirin Pharmaceutical Development LtdActive, not recruitingX-Linked HypophosphatemiaSpain, Italy, United Kingdom, France, Belgium, Denmark, Germany, Hungary, Portugal, Norway, Switzerland, Israel, Netherlands, Czechia, Bulgaria, Sweden, Slovenia, Ireland, Latvia, Slovakia
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VegaVect, Inc.National Eye Institute (NEI)Active, not recruiting
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Duke UniversityNational Institute of Allergy and Infectious Diseases (NIAID); University of... and other collaboratorsRecruitingCommon Variable Immunodeficiency | X-linked Agammaglobulinemia | Primary Immune Deficiency | Primary Antibody Deficiencies | CVID | XLA | Secondary HypogammaglobulinemiaUnited States
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Kyowa Kirin Pharmaceutical Development LtdRecruitingX-Linked HypophosphatemiaFrance, Netherlands, United Kingdom