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Clinical Trials on Familial Hemophagocytic Lymphocytosis
Total 1243 results
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Institut National de la Santé Et de la Recherche...Not yet recruitingAutoimmune Diseases | Systemic Lupus Erythematosus | Primary Immunodeficiency | Autoimmune Hepatitis | Juvenile Idiopathic Arthritis | IBD | Autoimmune Rheumatologic Disease | Autoimmune Diabetes | APECED | IPEX | Hemophagocytic Lymphohistiocytoses | Autoimmune Lymphoproliferative Syndrome | Autoimmune Thrombocytopenia and other conditions
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Institute of Liver and Biliary Sciences, IndiaKEM Hospital Research Centre; Apollo Hospital, New Delhi, India; Jaslok Hospital... and other collaboratorsRecruitingProgressive Familial Intrahepatic CholestasisIndia
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University Medical Center GroningenEnrolling by invitationProgressive Familial Intrahepatic CholestasisNetherlands
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Yale UniversityNational Institute on Alcohol Abuse and Alcoholism (NIAAA)RecruitingFamilial Alcoholism VulnerabilityUnited States
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AlbireoApproved for marketingProgressive Familial Intrahepatic CholestasisUnited States
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Novartis PharmaceuticalsCompletedNon Familial Chylocmicronemia Syndrome (Non-FCS)United States, Canada, Russian Federation
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National Liver Institute, EgyptUnknownProgressive Familial Intrahepatic CholestasisEgypt
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Baylor College of MedicineThe Methodist Hospital Research Institute; Center for Cell and Gene Therapy...RecruitingHaploidentical Hematopoietic Cell Transplantation Using TCR Alpha/Beta and CD19 Depletion (HAPLOTAB)Myelodysplastic Syndromes | Primary Immunodeficiency Diseases | Hemoglobinopathies | Chronic Myeloid Leukemia | Cytopenia | Severe Aplastic Anemia | Bone Marrow Failure Syndrome | Acute Myeloid Leukemia in Remission | Hemophagocytic Lymphohistiocytoses | Acute Lymphoblastic Leukemia in Remission | Severe...United States
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Alnylam PharmaceuticalsCompletedFamilial Amyloidotic Cardiomyopathy (FAC)United States, France, Spain, United Kingdom, Belgium, Brazil
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Novartis PharmaceuticalsCompletedColchicine Resistant/Intolerant Familial Mediterranean FeverIsrael
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Immunovia, Inc.CompletedPancreatic Ductal Adenocarcinoma | Familial Pancreatic Cancer | FAMMM - Familial Atypical Mole Malignant Melanoma SyndromeUnited States, Sweden, Canada, Spain, United Kingdom
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Massachusetts General HospitalPfizer; Akcea Therapeutics; Alnylam Pharmaceuticals; Eidos Therapeutics, a BridgeBio...RecruitingHeart Failure | Amyloidosis | Heart Failure, Diastolic | Transthyretin AmyloidosisUnited States
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Elif OralCompletedFatty Liver | Hypertriglyceridemia | NASH - Nonalcoholic Steatohepatitis | Familial Partial LipodystrophyUnited States
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NYU Langone HealthWithdrawnNausea | Vomiting | Familial DysautonomiaUnited States
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NYU Langone HealthCompletedFamilial Dysautonomia
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Daiichi Sankyo, Inc.TerminatedAtherosclerosis | Heterozygous Familial HypercholesterolemiaUnited States, United Kingdom, Spain, South Africa, Israel, Canada, Netherlands, Norway, Sweden
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M.D. Anderson Cancer CenterCompletedAttenuated Familial Adenomatous Polyposis | Deleterious Familial Adenomatous PolyposisUnited States
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Arizona State UniversityArizona Health Care Cost Containment SystemEnrolling by invitation
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Memorial Sloan Kettering Cancer CenterUniversity of Southern California; Weill Medical College of Cornell University and other collaboratorsActive, not recruiting
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University of ChicagoTerminatedOsteoporosis | Osteopenia | Hypercalciuria | Hypercalciuria, Familial IdiopathicUnited States
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Intellia TherapeuticsRegeneron PharmaceuticalsRecruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, United Kingdom, New Zealand, Canada
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Massachusetts General HospitalBroad InstituteRecruitingPrion Diseases | Familial Fatal Insomnia | CJD (Creutzfeldt Jakob Disease) | GSS | FFIUnited States
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, Brazil, Bulgaria, France, Italy, Japan, Mexico, Netherlands, Taiwan, United Kingdom, Belgium, Czechia, Denmark, New Zealand, Sweden, Korea, Republic of, Argentina, Chile, Hong Kong, Portugal
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Poland, Argentina, Australia, Belgium, France, Germany, Japan, Netherlands, Portugal, Spain, Sweden, United Kingdom, Canada, Czechia, Denmark, Hungary, Ireland, Norway, Korea, Republic of, Austria, Croatia, Israel, Latvia, Lithuan... and more
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedCoronary Artery Disease | Heterozygous Familial HypercholesterolemiaUnited States, Canada
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Duke UniversityCompletedFamilies Experiencing Homelessness With Children Under 48 Months of AgeUnited States
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Lev-Hasharon Mental Healtlh CenterUnknown
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Centre Medico-Chirurgicale et Obstetrique Cote...UnknownLumbar Stenosis, FamilialFrance
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Assistance Publique - Hôpitaux de ParisCompletedThoracic Aortic AneurysmFrance
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National Human Genome Research Institute (NHGRI)Completed
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NYU Langone HealthCompletedDysautonomia, Familial | Baroreflex Failure SyndromeUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHomozygous Familial HypercholesterolemicUnited States
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Virginia Commonwealth UniversityNot yet recruitingAmyloidosis, HereditaryUnited States
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University Hospital, MontpellierCompletedOppositional Defiant Disorder With Familial SettingFrance
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AstraZenecaRecruitingTransthyretin Amyloidosis Cardiomyopathy, Heart Failure With Preserved Ejection FractionRussian Federation
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Eidos Therapeutics, a BridgeBio companyCompletedFamilial ATTR-CM (ATTRm-CM, or FAC) | Wild-type ATTR-CM (ATTRwt-CM)United States
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University Hospital, MontpellierSoroptimist association of MonacoRecruitingSolid Tumor, Childhood | Pediatric Tumor | Familial Cancer | Hematological TumorFrance
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Fondazione IRCCS Istituto Nazionale dei Tumori,...CompletedFamilial Adenomatous Polyposis (FAP)Italy
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Ionis Pharmaceuticals, Inc.Approved for marketingAmyloidosis, Hereditary
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University Hospital, Strasbourg, FranceUnknownFamilial Lipomatosis | Very Rare Dermatologic DiseasesFrance
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University Hospital, MontpellierTerminated
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Alnylam PharmaceuticalsNot yet recruitingCerebral Amyloid Angiopathy
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Shenzhen Second People's HospitalNot yet recruitingCerebral Amyloid Angiopathy
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Centre Hospitalier Universitaire de NīmesCompletedCerebral Amyloid Angiopathy | Hypertensive ArteriopathyFrance
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Anna OlczakCompletedCerebral Amyloid AngiopathyPoland
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Fondazione I.R.C.C.S. Istituto Neurologico Carlo...RecruitingCerebral Amyloid AngiopathyItaly
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PfizerCompletedHereditary Transthyretin Amyloidosis (ATTRv) Cardiomyopathy (CM), Mixed PhenotypeUnited States
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PfizerCompletedCerebral Amyloid AngiopathyCanada, United States, Netherlands, France, United Kingdom
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Amydis Inc.National Institutes of Health (NIH); National Institute on Aging (NIA)Recruiting
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Leiden University Medical CenterRecruiting