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Clinical Trials on Familial Aortopathies in New Zealand
Total 233 results
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Rhode Island HospitalUnited TherapeuticsTerminatedPulmonary Arterial HypertensionUnited States
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeUnited States, Canada, Sweden
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Amryt PharmaRecruitingHomozygous Familial HypercholesterolemiaItaly, United States, Argentina, Canada, France, Greece, Netherlands, United Kingdom
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis (ATTR) With CardiomyopathyUnited States, Australia, Brazil, Bulgaria, France, Italy, Japan, Mexico, Netherlands, Taiwan, United Kingdom, Belgium, Czechia, Denmark, New Zealand, Sweden, Korea, Republic of, Argentina, Chile, Hong Kong, Portugal
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Regeneron PharmaceuticalsSanofiCompletedHomozygous Familial HypercholesterolemiaUnited States, South Africa, Canada, Greece, Japan, Ukraine, Austria, Czechia, France, Germany, Italy, Taiwan, Turkey
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Northwell HealthCompletedPulmonary Arterial Hypertension | Pulmonary Hypertension | Interstitial Lung DiseaseUnited States
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Columbia UniversityAmgenTerminatedFamilial HypercholesterolemiaUnited States
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Novartis PharmaceuticalsActive, not recruitingFamilial Hypercholesterolemia - HeterozygousUnited States, Germany, South Africa, Greece, Italy, Czechia, Taiwan, Slovakia, Turkey, France, Russian Federation, Canada, Spain, Jordan, Switzerland, Hungary, Poland, Netherlands, Norway, United Kingdom, Lebanon, Argentina, Brazil, ... and more
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Capital Medical UniversityPeking University First Hospital; The First Affiliated Hospital of Anhui Medical... and other collaboratorsRecruitingAlzheimer Disease | Familial Alzheimer Disease (FAD)China
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PfizerCompletedHeterozygous Familial HypercholesterolemiaCanada, Netherlands, United Kingdom, United States, Spain, Poland, Finland, Norway, South Africa, Italy, Bulgaria
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Novartis PharmaceuticalsCompletedPulmonary Arterial HypertensionAustria, Germany, United States, United Kingdom
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Immunovia, Inc.CompletedPancreatic Ductal Adenocarcinoma | Familial Pancreatic Cancer | FAMMM - Familial Atypical Mole Malignant Melanoma SyndromeUnited States, Sweden, Canada, Spain, United Kingdom
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Merck Sharp & Dohme LLCActive, not recruitingHypercholesterolemia | Familial HypercholesterolemiaUnited States, Australia, Brazil, Canada, Chile, Colombia, Czechia, Finland, Hong Kong, Hungary, Israel, Netherlands, New Zealand, Norway, Singapore, Spain, Taiwan
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Eidos Therapeutics, a BridgeBio companyCompletedFamilial ATTR-CM (ATTRm-CM, or FAC) | Wild-type ATTR-CM (ATTRwt-CM)United States
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Respira Therapeutics, Inc.CompletedPulmonary Arterial HypertensionAustralia
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Novartis PharmaceuticalsTerminatedPulmonary Arterial HypertensionGermany, Belgium, United Kingdom, United States, Lithuania, Italy, Australia
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Yale UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedHypophosphatemic Rickets, X Linked DominantUnited States
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ActelionWithdrawnPulmonary Arterial HypertensionUnited States
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Kawut, Steven, MDNational Heart, Lung, and Blood Institute (NHLBI); Columbia UniversityCompletedHypertension, PulmonaryUnited States
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Medical University of South CarolinaOchsner Health SystemTerminatedPulmonary Arterial HypertensionUnited States
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Keros Therapeutics, Inc.RecruitingPulmonary Arterial HypertensionUnited States, Australia
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The Medicines CompanyCompletedElevated Cholesterol | Heterozygous Familial HypercholesterolemiaUnited States, Canada, Czechia, Denmark, Netherlands, South Africa, Spain, Sweden
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American Medical Association FoundationWithdrawnIdiopathic Pulmonary Arterial Hypertension.United States
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Yale UniversityCompleted
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Yale UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedHyperparathyroidism | Hypophosphatemia, FamilialUnited States
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United TherapeuticsCompletedPulmonary Arterial HypertensionUnited States
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Novartis PharmaceuticalsCompletedPulmonary Arterial HypertensionGermany, Belgium, United States, Lithuania, United Kingdom, Italy, Australia
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ActelionTerminated
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Kyowa Hakko Kirin Pharma, Inc.Completed
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Regeneron PharmaceuticalsCompletedGenetic Diseases, Inborn | Familial Cold Autoinflammatory Syndrome (FCAS) | Familial Cold Urticaria | Muckle-Wells Syndrome (MWS)United States
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Insmed IncorporatedTerminatedPulmonary Arterial HypertensionUnited States
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United TherapeuticsAsian Clinical TrialsTerminatedPulmonary Arterial HypertensionIndia
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeSpain, United Kingdom, France, Canada, United States, Italy, Netherlands, Norway, Portugal, Slovakia, Sweden
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State University of New York - Upstate Medical...TerminatedFamilial Encephalopathy With Neuroserpin Inclusion Bodies | X-linked Mental Retardation | Congenital Vertical Talus | Idiopathic Generalised Epilepsy | Familial DementiaUnited States
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United TherapeuticsTerminatedPulmonary Arterial HypertensionUnited States
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Bellus Health IncNational Institute of Neurological Disorders and Stroke (NINDS)CompletedStroke | Neurologic Diseases, GeneralUnited States
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Israel, Spain, Italy, United Kingdom, Netherlands, Canada, Hungary, Sweden, France, Norway, Portugal, Slovakia
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White Plains HospitalActive, not recruitingPancreatic Cancer | Pancreatic Adenocarcinoma | Lynch Syndrome | Pancreas Cancer | HNPCC | Familial Pancreatic Cancer | Hereditary Pancreatitis | BRCA 1/2 | FAMMM | Familial Atypical Multiple Mole Melanoma | Peutz Jeghers SyndromeUnited States
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Brazil, Canada, France, Germany, Hungary, Israel, Italy, Netherlands, South Africa, Spain, United Kingdom
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Shape Medical Systems, Inc.National Heart, Lung, and Blood Institute (NHLBI)Not yet recruitingPulmonary Arterial HypertensionUnited States
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Kyowa Hakko Kirin Pharma, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Canada
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PfizerCompletedTransthyretin Amyloidosis | Transthyretin Gene MutationsUnited States, France, Spain, Taiwan, Israel, Korea, Republic of, Denmark, Canada, Netherlands, Japan, Sweden, Brazil, Mexico, Argentina, Portugal, Belgium, Bulgaria, Cyprus, Germany, Italy, Malaysia, Romania, Saudi Arabia, Turkey, United...
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Alnylam PharmaceuticalsCompletedFamilial Amyloidotic Cardiomyopathy (FAC)United States, France, Spain, United Kingdom, Belgium, Brazil
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Kyowa Kirin, Inc.CompletedX-Linked HypophosphatemiaUnited States
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United TherapeuticsCompleted
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Kyowa Hakko Kirin Pharma, Inc.Kyowa Kirin Co., Ltd.CompletedX-linked HypophosphatemiaUnited States, Canada
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Washington University School of MedicineEli Lilly and Company; Hoffmann-La Roche; Avid Radiopharmaceuticals; National Institute... and other collaboratorsCompletedDementia | Alzheimers Disease | Alzheimers Disease, FamilialUnited States, Canada, France, Spain, Ireland, Australia, Puerto Rico, United Kingdom
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ActelionCompletedPulmonary Arterial HypertensionUnited States, France, Netherlands, Italy, Germany, Switzerland, United Kingdom
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PfizerCompletedCerebral Amyloid AngiopathyCanada, United States, Netherlands, France, United Kingdom
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedCoronary Artery Disease | Heterozygous Familial HypercholesterolemiaUnited States, Canada