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Clinical Trials on Familial Aortopathies in United States
Total 569 results
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University of ArizonaUnited TherapeuticsCompletedPulmonary Arterial HypertensionUnited States
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Mayo ClinicCompletedPulmonary Arterial Hypertension | Pulmonary HypertensionUnited States
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Mayo ClinicCompletedPulmonary Arterial HypertensionUnited States
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Children's Mercy Hospital Kansas CityWithdrawn
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Northwestern UniversityUniversity of Pennsylvania; Family Heart FoundationEnrolling by invitationFamilial HypercholesterolemiaUnited States
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Columbia UniversityAmgenTerminatedFamilial HypercholesterolemiaUnited States
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University of PennsylvaniaCompletedHypercholesterolemia, FamilialUnited States
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Brigham and Women's HospitalGilead SciencesTerminatedPulmonary Arterial HypertensionUnited States
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Emory UniversityKaneka Medical America LLCCompletedFamilial HypercholesterolemiaUnited States
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University of PennsylvaniaCompletedPulmonary Arterial HypertensionUnited States
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Regeneron PharmaceuticalsSanofiCompletedHeterozygous Familial HypercholesterolemiaUnited Kingdom, Netherlands, Czech Republic, Norway
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Poudre Valley Health SystemEnrolling by invitationFamilial HyperlipidemiaUnited States
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University of PennsylvaniaAstraZeneca; Ionis Pharmaceuticals, Inc.Active, not recruitingHereditary Amyloidosis, Transthyretin-RelatedUnited States
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University of PennsylvaniaNorthwestern University; Family Heart FoundationEnrolling by invitationFamilial HypercholesterolemiaUnited States
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Poudre Valley Health SystemActive, not recruiting
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Amydis Inc.National Institutes of Health (NIH); National Institute on Aging (NIA)Recruiting
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Israel, Spain, Italy, United Kingdom, Netherlands, Canada, Hungary, Sweden, France, Norway, Portugal, Slovakia
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PhaseBio Pharmaceuticals Inc.CompletedPulmonary Arterial HypertensionUnited States
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Brigham and Women's HospitalGilead SciencesCompletedExercise-induced Pulmonary Arterial HypertensionUnited States
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Brigham and Women's HospitalCompletedPulmonary Arterial Hypertension | Exercise Associated Pulmonary Arterial HypertensionUnited States
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Regeneron PharmaceuticalsCompletedGenetic Diseases, Inborn | Familial Cold Autoinflammatory Syndrome (FCAS) | Familial Cold Urticaria | Muckle-Wells Syndrome (MWS)United States
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Geisinger ClinicNational Heart, Lung, and Blood Institute (NHLBI)Enrolling by invitationFamilial HypercholesterolemiaUnited States
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Brazil, Canada, France, Germany, Hungary, Israel, Italy, Netherlands, South Africa, Spain, United Kingdom
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Vanderbilt University Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)RecruitingFamilial HypercholesterolemiaUnited States
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Northwestern UniversityUniversity of Pennsylvania; Family Heart FoundationCompletedFamilial HypercholesterolemiaUnited States
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West Penn Allegheny Health SystemJohns Hopkins University; University of Colorado, Denver; Massachusetts General... and other collaboratorsWithdrawnPulmonary Arterial Hypertension | Pulmonary Hypertension | PAH WHO Group IUnited States
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Megan BallingerCompleted
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Sidney Kimmel Comprehensive Cancer Center at Johns...ChiRhoClin, Inc.; The V Foundation for Cancer ResearchCompletedEarly Pancreatic Neoplasia | Familial Pancreatic NeoplasiaUnited States
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Aires Pharmaceuticals, Inc.CompletedPulmonary Arterial Hypertension | Pulmonary HypertensionUnited States
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Auburn UniversityCompletedAlzheimer Disease | Cerebral Amyloid AngiopathyUnited States
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Inozyme PharmaEngage Health Inc.; GACI GlobalCompletedGeneralized Arterial Calcification in Infancy | Autosomal Recessive Hypophosphatemic Rickets Type 2United States
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Northwell HealthCompletedPulmonary Arterial HypertensionUnited States
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Boston Children's HospitalWellth Inc.; MMAS-8 with permission from Dr Donald Morisky. as written belowRecruitingAdherence, Medication | Familial HypercholesterolemiaUnited States
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ActelionTerminatedPulmonary Arterial HypertensionUnited States
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Seattle Children's HospitalCompletedLimited English Proficient Patients and FamiliesUnited States
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Redwood Dermatology SciencesUltragenyx Pharmaceutical IncCompletedPain, Chronic | Hypophosphatemia | Hypophosphatemic RicketsUnited States
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Indiana UniversityCompletedAutosomal Dominant Hypophosphatemic RicketsUnited States
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Mayo ClinicUnited TherapeuticsCompletedPulmonary Arterial HypertensionUnited States
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National Institute of Dental and Craniofacial Research...RecruitingOsteomalacia | Tumor Induced Osteomalcia | Familial Tumoral CalcinosisUnited States
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In His ImageKos PharmaceuticalsCompletedDyslipidemia | Hyperlipidemia | Mixed HyperlipidemiaUnited States
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Acceleron Pharma Inc. (a wholly owned subsidiary...CompletedPulmonary Arterial HypertensionUnited States
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Idorsia Pharmaceuticals Ltd.TerminatedPulmonary Arterial HypertensionUnited States, Japan, France
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Memorial Sloan Kettering Cancer CenterUniversity of Southern California; Weill Medical College of Cornell University and other collaboratorsActive, not recruiting
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Medical University of South CarolinaOchsner Health SystemTerminatedPulmonary Arterial HypertensionUnited States
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ActelionWithdrawnPulmonary Arterial HypertensionUnited States
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Kawut, Steven, MDNational Heart, Lung, and Blood Institute (NHLBI); Columbia UniversityCompletedHypertension, PulmonaryUnited States
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The Familial Hypercholesterolemia FoundationRecruitingHypercholesterolemiaUnited States
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University of PennsylvaniaLancaster General Hospital; The Familial Hypercholesterolemia FoundationCompleted
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Children's Mercy Hospital Kansas CityCompletedHypophosphatemic Rickets, X-Linked DominantUnited States
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Yale UniversityNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)CompletedHypophosphatemic Rickets, X Linked DominantUnited States