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Clinical Trials on Familial Hemophagocytic Lymphohistiocytosis in United States
Total 599 results
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NYU Langone HealthNot yet recruitingFamilial DysautonomiaUnited States
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NYU Langone HealthNot yet recruiting
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NYU Langone HealthCompletedFamilial DysautonomiaUnited States
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NYU Langone HealthCompletedFamilial DysautonomiaUnited States
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NYU Langone HealthCompletedFamilial DysautonomiaUnited States
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Mayo ClinicUniversity of California, San Francisco; University of MinnesotaCompletedFamilial Pancreatic CancerUnited States
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Partial LipodystrophyUnited States
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University of PennsylvaniaUniversity of Amsterdam; University of Cape Town; University of Witwatersrand...RecruitingHomozygous Familial HypercholesterolemiaUnited States, Netherlands, South Africa
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Intellia TherapeuticsRecruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisUnited Kingdom, New Zealand, Sweden
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Novartis PharmaceuticalsRecruitingHeterozygous or Homozygous Familial HypercholesterolemiaNetherlands, Israel, Hungary, Italy, Germany, Turkey, Spain, United States, France, Norway, Russian Federation, South Africa, United Kingdom, Canada, Switzerland, Brazil, Lebanon, Slovenia, Poland, Taiwan, Malaysia
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, Canada
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University of MichiganAvailable
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Novartis PharmaceuticalsCompletedFamilial Chylomicronemia Syndrome (FCS)South Africa, Spain, France, Germany, United Kingdom, United States, Canada, Netherlands
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Intellia TherapeuticsActive, not recruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisFrance, United Kingdom, New Zealand, Sweden
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Abhimanyu GargCompletedFamilial Partial LipodystrophyUnited States
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Mirum Pharmaceuticals, Inc.CompletedProgressive Familial Intrahepatic Cholestasis (PFIC)United States, United Kingdom, Poland, France
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PfizerCompletedFamilial Amyloid PolyneuropathyUnited Kingdom, Spain, United States, Argentina, Brazil, France, Germany, Portugal, Sweden
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid PolyneuropathiesUnited States, Canada, Argentina, Australia, Bulgaria, Cyprus, Italy, Japan, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Germany, France, Brazil, Turkey, Korea, Republic of, Taiwan, United Kingdom
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NYU Langone HealthRecruitingHereditary Sensory and Autonomic Neuropathies | Familial Dysautonomia (Riley-Day Syndrome) | Hereditary Sensory and Autonomic Neuropathy 3United States, Israel
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedHypercholesterolemia, FamilialUnited States, Netherlands
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REGENXBIO Inc.CompletedHomozygous Familial Hypercholesterolemia (HoFH)United States
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Ionis Pharmaceuticals, Inc.CompletedAmyloidosis | Familial Amyloid Polyneuropathy | FAP | TTR | TransthyretinUnited States, Spain, Argentina, Brazil, France, Germany, Italy, Portugal, United Kingdom
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NYU Langone HealthWithdrawnFamilial DysautonomiaUnited States
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Ionis Pharmaceuticals, Inc.CompletedAmyloidosis | Familial Amyloid Polyneuropathy | FAP | TTR | TransthyretinNew Zealand, United States, Spain, Argentina, Brazil, France, Germany, Italy, Portugal, United Kingdom
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Mirum Pharmaceuticals, Inc.Active, not recruitingProgressive Familial Intrahepatic Cholestasis (PFIC)United States, Argentina, France, Singapore, United Kingdom, Belgium, Turkey, Austria, Brazil, Canada, Colombia, Germany, Italy, Lebanon, Mexico, Poland
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Cerenis Therapeutics, SACompletedHomozygous Familial HypercholesterolemiaUnited States, Canada, Italy, Netherlands, United Kingdom
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University of Texas Southwestern Medical CenterNational Heart, Lung, and Blood Institute (NHLBI); Columbia University; The Cleveland... and other collaboratorsRecruitingAmyloidosis, Familial | Amyloidosis, Hereditary | Amyloidosis Cardiac | Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin Gene MutationUnited States
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Regeneron PharmaceuticalsSanofiTerminatedHeterozygous Familial Hypercholesterolemia | Non-familial HypercholesterolemiaUnited States, Bulgaria, Estonia, Russian Federation, South Africa, Ukraine
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University of UtahNational Institute on Aging (NIA)CompletedDementia, FamilialUnited States
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Yale UniversityCompletedFamilial Alcoholism VulnerabilityUnited States
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Mirum Pharmaceuticals, Inc.CompletedProgressive Familial Intrahepatic Cholestasis (PFIC)Italy, United States, Argentina, France, Singapore, United Kingdom, Austria, Brazil, Mexico, Lebanon, Germany, Turkey, Poland, Belgium, Canada, Colombia, Hungary
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University of MichiganCompletedNAFLD | Nonalcoholic Steatohepatitis | Familial Partial LipodystrophyUnited States
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CENTOGENE GmbH RostockAlnylam PharmaceuticalsRecruitingCardiomyopathies | Polyneuropathies | Transthyretin Amyloidosis | Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid PolyneuropathyGermany, Austria, Switzerland
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University of Southern CaliforniaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedObesity | Obesity, Childhood | Obesity; FamilialUnited States
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University of MichiganNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingPregnancy Related | Obesity; FamilialUnited States
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Arrowhead PharmaceuticalsActive, not recruitingHomozygous Familial HypercholesterolemiaAustralia, Canada, United States, South Africa
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National Jewish HealthUniversity of Colorado, Denver; Vanderbilt University; Landspitali University...RecruitingIdiopathic Pulmonary Fibrosis | Idiopathic Interstitial Pneumonia | Familial Pulmonary Fibrosis | Familial Interstitial PneumoniaUnited States, Iceland
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University of Colorado, DenverNational Institutes of Health (NIH)RecruitingRacially/Ethnically Diverse Families From Urban SettingsUnited States
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University of Alabama at BirminghamNational Institute on Minority Health and Health Disparities (NIMHD)Active, not recruitingObesity | Obesity, Childhood | Obesity; FamilialUnited States
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Boston Medical CenterEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedLow Income Families Basic Social NeedsUnited States
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M.D. Anderson Cancer CenterCompletedAttenuated Familial Adenomatous Polyposis | Deleterious Familial Adenomatous PolyposisUnited States
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Washington University School of MedicineEnrolling by invitationMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Lou Gehrig Disease | Familial Amyotrophic Lateral Sclerosis | Motor Neuron Disease, FamilialUnited States
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedHypercholesterolemia, FamilialUnited States, Netherlands
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REGENXBIO Inc.Active, not recruitingHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Netherlands
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University of ChicagoTerminatedOsteoporosis | Osteopenia | Hypercalciuria | Hypercalciuria, Familial IdiopathicUnited States
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University of MichiganNot yet recruitingPregnancy Related | Infant Behavior | Obesity; FamilialUnited States
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LIB Therapeutics LLCMedpace, Inc.CompletedHeterozygous Familial HypercholesterolemiaUnited States, Israel, Norway, South Africa, Turkey
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Yale UniversityNational Institute on Alcohol Abuse and Alcoholism (NIAAA)RecruitingFamilial Alcoholism VulnerabilityUnited States
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AlbireoApproved for marketingProgressive Familial Intrahepatic CholestasisUnited States
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University of California, San FranciscoDestination: Home SV; Sí Se Puede Collective; Sacred Heart Community Service; County...RecruitingFamilies Experiencing Homelessness and/or Housing InstabilityUnited States