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Clinical Trials on Familial Paroxysmal Ataxia
Total 2071 results
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BioCryst PharmaceuticalsCompletedParoxysmal Nocturnal HemoglobinuriaUnited Kingdom, Austria, South Africa
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Alexion PharmaceuticalsCMIC Co, Ltd. JapanCompletedParoxysmal Nocturnal Hemoglobinuria
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Peking Union Medical College HospitalUnknownParoxysmal Nocturnal HemoglobinuriaChina
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Eidos Therapeutics, a BridgeBio companyWithdrawnTransthyretin-Related (ATTR) Familial Amyloid Polyneuropathy
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Eidos Therapeutics, a BridgeBio companyWithdrawnTransthyretin-Related (ATTR) Familial Amyloid PolyneuropathyUnited States
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SOM Innovation Biotech SAHospital Vall d'HebronCompleted
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Firat UniversityRecruitingIndividuals With Multiple Sclerosis | With Ataxia Symptoms | No Secondary Disease Affecting BalanceTurkey
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Augusta UniversityNational Institutes of Health (NIH)CompletedConstipation | Dyssynergia
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Hospices Civils de LyonCompletedDetrusor Striated Sphincter Dyssynergia (DSSD)France
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Marcello ArcaPfizer; Göteborg University; University of HelsinkiNot yet recruitingFamilial Hypobetalipoproteinemia | Familial Hypobetalipoproteinemia - Heterozygous Form
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Novartis PharmaceuticalsRecruitingHeterozygous or Homozygous Familial HypercholesterolemiaNetherlands, Israel, Hungary, Italy, Germany, Spain, United States, France, Norway, Russian Federation, South Africa, Turkey, United Kingdom, Canada, Switzerland, Brazil, Lebanon, Slovenia, Poland, Taiwan, Malaysia
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Intellia TherapeuticsRecruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisUnited Kingdom, New Zealand, Sweden
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Intellia TherapeuticsActive, not recruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisFrance, United Kingdom, New Zealand, Sweden
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid PolyneuropathiesUnited States, Canada, Argentina, Australia, Bulgaria, Cyprus, Italy, Japan, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Germany, France, Brazil, Turkey, Korea, Republic of, Taiwan, United Kingdom
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Riphah International UniversityCompletedBenign Paroxysmal Positional Vertigo (Disorder)Pakistan
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Chiang Mai UniversityUnknown
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Assistance Publique - Hôpitaux de ParisLeeds Cancer Centre at St. James's University HospitalCompleted
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Alexion PharmaceuticalsCompletedParoxysmal Nocturnal HemoglobinuriaUnited Kingdom
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Apellis Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal HemoglobinuriaUnited States, France, Russian Federation, Korea, Republic of, Canada, Germany, Australia, Japan, Spain, Belgium, United Kingdom
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BiocadCompletedParoxysmal Nocturnal HemoglobinuriaRussian Federation
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Apellis Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal HemoglobinuriaHong Kong, Thailand, New Zealand, Malaysia
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AO GENERIUMCompletedParoxysmal Nocturnal HemoglobinuriaRussian Federation
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Alexion PharmaceuticalsCompletedHemoglobinuria, ParoxysmalUnited States
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Meshalkin Research Institute of Pathology of CirculationUnknownParoxysmal Atrial Fibrillation, Coronary Artery DiseaseRussian Federation
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Chonbuk National UniversityUnknownBenign Paroxysmal Positional Vertigo (BPPV)Korea, Republic of
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University of UtahNational Institutes of Health (NIH)CompletedHemoglobinuria, ParoxysmalUnited States
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National Heart, Lung, and Blood Institute (NHLBI)Completed
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Alnylam PharmaceuticalsNo longer availableAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid Polyneuropathies
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University Hospital, LilleRecruitingFamilial Partial Lipodystrophy Type 2France
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Novartis PharmaceuticalsCompletedElevated Cholesterol | Homozygous Familial Hypercholesterolemia | Heterozygous Familial Hypercholesterolemia | ASCVDUnited States, Canada, Czechia, Denmark, Germany, Hungary, Netherlands, Poland, South Africa, Spain, Sweden, Ukraine, United Kingdom
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Cairo UniversityRecruitingMedulloblastoma | AtaxiaEgypt
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Ablacon, Inc.RecruitingAtrial Fibrillation | Arrhythmias, Cardiac | Arrhythmia | Atrial Flutter | Atrial Fibrillation, Persistent | Atrial Tachycardia | Atrial Arrhythmia | Atrial Fibrillation Paroxysmal | Atrial Fibrillation, Paroxysmal or PersistentUnited States, Belgium, Netherlands, Czechia
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AlexionCompletedParoxysmal Nocturnal HemoglobinuriaFrance, United Kingdom, Norway, Russian Federation, Netherlands, United States
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AlexionAchillion, a wholly owned subsidiary of AlexionCompletedParoxysmal Nocturnal HemoglobinuriaNew Zealand, Korea, Republic of, Italy
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Kira Pharmacenticals (US), LLC.CompletedParoxysmal Nocturnal HemoglobinuriaAustralia
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Apellis Pharmaceuticals, Inc.CompletedParoxysmal Nocturnal HemoglobinuriaHong Kong, Thailand, Malaysia, Singapore, Serbia, Peru, Philippines, Colombia, Mexico, Poland
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AKARI TherapeuticsTerminatedParoxysmal Nocturnal HemoglobinuriaPoland
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Alexion PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria
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Alexion PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria | PNHKorea, Republic of, Canada, France, Germany, Spain, Taiwan, United Kingdom
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Apellis Pharmaceuticals, Inc.Completed
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Alexion PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria | PNHAustralia, France, United Kingdom, Belgium, Germany, Netherlands, Ireland, United States, Switzerland, Italy
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Novartis PharmaceuticalsCompletedParoxysmal Nocturnal Hemoglobinuria (PNH) With Signs of Active HemolysisItaly, Germany, France
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Mirum Pharmaceuticals, Inc.CompletedProgressive Familial Intrahepatic Cholestasis (PFIC)Italy, United States, Argentina, France, Singapore, United Kingdom, Austria, Brazil, Mexico, Lebanon, Germany, Turkey, Poland, Belgium, Canada, Colombia, Hungary
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TakedaActive, not recruitingProgressive Familial Intrahepatic Cholestasis (PFIC)Japan
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Mirum Pharmaceuticals, Inc.Active, not recruitingProgressive Familial Intrahepatic Cholestasis (PFIC)United States, Argentina, France, Singapore, United Kingdom, Belgium, Turkey, Austria, Brazil, Canada, Colombia, Germany, Italy, Lebanon, Mexico, Poland
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Mirum Pharmaceuticals, Inc.WithdrawnProgressive Familial Intrahepatic Cholestasis (PFIC)
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CENTOGENE GmbH RostockWithdrawnTransthyretin Amyloidosis | Transthyretin Amyloid Cardiopathy | Transthyretin-Related (ATTR) Familial Amyloid PolyneuropathyIndia, Germany
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University of British ColumbiaVancouver Coastal Health Research Institute; Genome British ColumbiaRecruitingAcute Coronary Syndrome | Familial Hypercholesterolemia | STEMI | NSTEMI - Non-ST Segment Elevation MI | Familial Hypercholesterolemia - Heterozygous | Familial Hypercholesterolemia Due to Genetic Defect of Apolipoprotein B | Familial Hypercholesterolemia Due to Heterozygous LDL Receptor Mutation and other conditionsCanada
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Norfolk and Norwich University Hospitals NHS Foundation...Guy's and St Thomas' NHS Foundation Trust; University Hospitals, Leicester; University... and other collaboratorsRecruitingVestibular Migraine | Benign Paroxysmal Positional Vertigo (BPPV) | Ménière's DiseaseUnited Kingdom
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Radboud University Medical CenterCompletedParoxysmal Nocturnal Hemoglobinuria | Eculizumab | PK-PDNetherlands