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Clinical Trials on Familial Transthyretin Amyloidosis in United States
Total 817 results
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University of ChicagoTerminatedOsteoporosis | Osteopenia | Hypercalciuria | Hypercalciuria, Familial IdiopathicUnited States
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Elif OralCompletedFatty Liver | Hypertriglyceridemia | NASH - Nonalcoholic Steatohepatitis | Familial Partial LipodystrophyUnited States
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Bristol-Myers SquibbTerminatedPrimary Familial Dilated CardiomyopathyUnited States, Germany, Spain, United Kingdom
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Duke UniversityCompletedFamilies Experiencing Homelessness With Children Under 48 Months of AgeUnited States
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LIB Therapeutics LLCCompletedHomozygous Familial HypercholesterolemiaUnited States, Israel, Norway, South Africa, Turkey, India
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National Human Genome Research Institute (NHGRI)Completed
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.TerminatedFamilial Partial LipodystrophyUnited States, Netherlands, Belgium, Brazil, Canada, Germany, Russian Federation
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHomozygous Familial HypercholesterolemicUnited States
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Australia, Austria, Netherlands, Taiwan, Ukraine
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NYU Langone HealthCompletedDysautonomia, Familial | Baroreflex Failure SyndromeUnited States
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National Eye Institute (NEI)CompletedEye Diseases | Exudatiaon | Avascular Retina | Retina Fold | Familial Exudative Vitreoretinopathy | FEVRCanada, United Kingdom
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Herbert Irving Comprehensive Cancer CenterCompleted
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Washington University School of MedicineNational Institutes of Health (NIH); National Institute on Aging (NIA)Completed
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Regeneron PharmaceuticalsSanofiCompletedHypercholesterolemia | Heterozygous Familial HypercholesterolemiaUnited States, Canada
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Janssen Research & Development, LLCActive, not recruitingAmyloidosisUnited States, Netherlands, Belgium, Korea, Republic of, France, Sweden, Israel, Turkey, United Kingdom, Brazil, Canada, Mexico, Australia, Germany, Japan, Spain, Denmark, Italy, China, Greece, Poland, Hungary
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Virginia Commonwealth UniversityTerminated
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Regeneron PharmaceuticalsCompletedFamilial Partial Lipodystrophy | Metabolic AbnormalitiesUnited States, France, Spain, Turkey, United Kingdom
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Janssen Research & Development, LLCRecruitingRelapsed or Refractory Multiple Myeloma | Previously Treated Amyloid Light-chain (AL) AmyloidosisBelgium, United States, United Kingdom, Spain, France, Netherlands
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Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeUnited States, Canada, Sweden
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Regeneron PharmaceuticalsSanofiCompletedHomozygous Familial HypercholesterolemiaUnited States, South Africa, Canada, Greece, Japan, Ukraine, Austria, Czechia, France, Germany, Italy, Taiwan, Turkey
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AmgenCompletedFamilial HypercholesterolemiaCanada, Italy, Norway, Belgium, United States, Turkey, Australia, Austria, South Africa, Poland, Switzerland, Spain, Portugal, Slovenia, Brazil, Russian Federation, Hungary, United Kingdom, Colombia, Czechia, Netherlands, Greece, Ma...
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, Australia, Austria, Canada, France, Greece, Italy, Japan, South Africa, Ukraine
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AmgenCompletedHomozygous Familial HypercholesterolemiaNew Zealand, South Africa, France, United States, Spain, Belgium, Czechia, Italy, Netherlands, Hong Kong, Canada, Lebanon
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Novartis PharmaceuticalsActive, not recruitingFamilial Hypercholesterolemia - HeterozygousUnited States, Germany, South Africa, Greece, Italy, Czechia, Taiwan, Slovakia, Turkey, France, Russian Federation, Canada, Spain, Jordan, Switzerland, Hungary, Poland, Netherlands, Norway, United Kingdom, Lebanon, Argentina, Brazil, ... and more
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Washington University School of MedicineNational Institute of Neurological Disorders and Stroke (NINDS)Completed
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Mayo ClinicNot yet recruitingPulmonary Arterial HypertensionUnited States
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Vanderbilt University Medical CenterNational Heart, Lung, and Blood Institute (NHLBI)RecruitingPulmonary Arterial HypertensionUnited States
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Stephen Y. ChanNational Heart, Lung, and Blood Institute (NHLBI); BayerRecruiting
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National Institutes of Health Clinical Center (CC)National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK); University... and other collaboratorsRecruiting
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Mayo ClinicCompletedPulmonary Arterial HypertensionUnited States
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Gladwin, Mark, MDNational Heart, Lung, and Blood Institute (NHLBI); Complexa, Inc.Terminated
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University of PennsylvaniaTerminated
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Lundquist Institute for Biomedical Innovation at...Lung Biotechnology PBCCompletedPulmonary Arterial HypertensionUnited States
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Massachusetts General HospitalCompletedPulmonary Arterial HypertensionUnited States
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The Cleveland ClinicCompleted
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Massachusetts General HospitalActelionWithdrawn
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NYU Langone HealthCompletedAnxiety Disorders | Familial Dysautonomia | Dysthymia | Paroxysmal Hypertension | Autosomal Recessive DiseaseUnited States
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AmgenCompletedSevere Familial HypercholesterolemiaItaly, Czechia, United States, Israel, New Zealand, South Africa, France, Spain, Australia, Belgium, Canada, Netherlands, Hong Kong, Brazil, United Kingdom, Greece, Japan, Lebanon
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PfizerRecruitingPulmonary Arterial HypertensionUnited States
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University of CincinnatiRecruitingPulmonary Arterial HypertensionUnited States
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University of MinnesotaCompletedPulmonary Arterial HypertensionUnited States
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University of PittsburghBoston University; National Heart, Lung, and Blood Institute (NHLBI); Northeastern...CompletedPathologic Processes | Heart Diseases | Atrial Fibrillation | Arrythmia, Cardiac | Familial Atrial FibrillationUnited States
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Stanford UniversityCompletedPulmonary Arterial HypertensionUnited States
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University of Texas Southwestern Medical CenterCompletedPulmonary Arterial HypertensionUnited States
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University of MinnesotaTerminated
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University of PennsylvaniaCompletedPulmonary Arterial HypertensionUnited States
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Virginia Commonwealth UniversityGlaxoSmithKlineCompletedPulmonary Arterial HypertensionUnited States
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Edda SpiekerkoetterStanford UniversityCompletedPulmonary Arterial HypertensionUnited States
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University of ChicagoBayerCompletedPulmonary Arterial HypertensionUnited States
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Avid RadiopharmaceuticalsNational Institute of Neurological Disorders and Stroke (NINDS); National Institutes...CompletedParkinson's DiseaseUnited States