- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Familial Dysbetalipoproteinemia
Total 1157 results
-
Mario Negri Institute for Pharmacological ResearchFondazione TelethonCompleted
-
REGENXBIO Inc.Active, not recruitingHomozygous Familial Hypercholesterolemia (HoFH)United States, Canada, Netherlands
-
Karo Bio ABTerminatedHeterozygous Familial Hypercholesterolaemia
-
Fundació Institut de Recerca de l'Hospital de la...Hospital Clinic of BarcelonaCompletedFamilial Hypocalciuric HypercalcemiaSpain
-
University of MichiganAvailable
-
NYU Langone HealthCompletedFamilial DysautonomiaUnited States
-
NYU Langone HealthCompletedFamilial DysautonomiaUnited States
-
Visirna Therapeutics HK LimitedNot yet recruitingFamilial Chylomicronemia Syndrome
-
Ionis Pharmaceuticals, Inc.Active, not recruitingFamilial Chylomicronemia SyndromeSpain, United Kingdom, France, Canada, United States, Italy, Netherlands, Norway, Portugal, Slovakia, Sweden
-
Ionis Pharmaceuticals, Inc.AvailableFamilial Chylomicronemia Syndrome
-
Jiangsu HengRui Medicine Co., Ltd.CompletedMixed Hyperlipidemia | Non-familial HypercholesterolemiaChina
-
Abhimanyu GargCompletedFamilial Partial LipodystrophyUnited States
-
UniQure Biopharma B.V.CompletedLipoprotein Lipase Deficiency | Familial Hyperlipoproteinemia Type 1 | Familial HyperchylomicronemiaGermany
-
Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Brazil, Canada, France, Germany, Hungary, Israel, Italy, Netherlands, South Africa, Spain, United Kingdom
-
Organon and CoCompletedPrimary Hypercholesterolemia and Homozygous Familial Hypercholesterolemia (HoFH)
-
REGENXBIO Inc.CompletedHomozygous Familial Hypercholesterolemia (HoFH)United States
-
Regeneron PharmaceuticalsCompletedGenetic Diseases, Inborn | Familial Cold Autoinflammatory Syndrome (FCAS) | Familial Cold Urticaria | Muckle-Wells Syndrome (MWS)United States
-
NYU Langone HealthNot yet recruitingFamilial DysautonomiaUnited States
-
NYU Langone HealthNot yet recruiting
-
University of Texas Southwestern Medical CenterNational Heart, Lung, and Blood Institute (NHLBI); Columbia University; The Cleveland... and other collaboratorsRecruitingAmyloidosis, Familial | Amyloidosis, Hereditary | Amyloidosis Cardiac | Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin Gene MutationUnited States
-
Regeneron PharmaceuticalsCompletedFamilial Partial Lipodystrophy | Metabolic AbnormalitiesUnited States, France, Spain, Turkey, United Kingdom
-
NYU Langone HealthCompletedFamilial DysautonomiaUnited States
-
Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Partial LipodystrophyUnited States
-
IRCCS Policlinico S. MatteoCompletedTransthyretin AmyloidosisItaly
-
University of GeorgiaCompletedSAAF-T | FUEL for Families
-
New French Society of AtherosclerosisAkcea TherapeuticsCompletedFamilial Chylomicronemia Syndrome | Multifactorial Chylomicronemia SyndromeFrance
-
Katarzyna HolcmanRecruitingTransthyretin AmyloidosisPoland
-
University Hospital, BordeauxUniversity of BordeauxCompletedAmyloid Neuropathies, FamilialFrance
-
Centre Hospitalier Universitaire de NīmesCompletedTransthyretin AmyloidosisFrance
-
NYU Langone HealthWithdrawnFamilial DysautonomiaUnited States
-
Medical University InnsbruckUnknownFamilial Hypobetalipoproteinaemia - Heterozygous Form | Low-LDL-syndromeAustria
-
Fondazione Policlinico Universitario Agostino Gemelli...RecruitingHereditary Transthyretin AmyloidosisItaly
-
Cambridge University Hospitals NHS Foundation TrustRecruitingDiabetes | Diet Modification | LipodystrophyUnited Kingdom
-
National Jewish HealthUniversity of Colorado, Denver; Vanderbilt University; Landspitali University...RecruitingIdiopathic Pulmonary Fibrosis | Idiopathic Interstitial Pneumonia | Familial Pulmonary Fibrosis | Familial Interstitial PneumoniaUnited States, Iceland
-
Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis | Amyloidosis, HereditaryUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Cyprus, France, Germany, Greece, Italy, Japan, Korea, Republic of, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Taiwan, United Kingdom
-
University of NottinghamUniversity of OxfordCompletedFamilial Breast CancerUnited Kingdom
-
University of MichiganNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingPregnancy Related | Obesity; FamilialUnited States
-
Boston Medical CenterEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedLow Income Families Basic Social NeedsUnited States
-
Yonsei UniversityCompletedFamilial Hypertrophic CardiomyopathyKorea, Republic of
-
University of UtahNational Institute on Aging (NIA)CompletedDementia, FamilialUnited States
-
Hospices Civils de LyonCompletedFamilial Chylomicronemia Syndrome | Multifactorial Chylomicronemia SyndromeFrance
-
Aegerion Pharmaceuticals, Inc.WithdrawnHomozygous Familial Hypercholesterolemia
-
University of Sao PauloMerck Sharp & Dohme LLCUnknownHeterozigous Familial HypercholesterolemiaBrazil
-
John Paul II Hospital, KrakowRecruitingTransthyretin AmyloidosisPoland
-
University of Southern CaliforniaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedObesity | Obesity, Childhood | Obesity; FamilialUnited States
-
Meir Medical CenterRambam Health Care Campus; Hadassah Medical Organization; Assaf-Harofeh Medical... and other collaboratorsUnknownPatella, Familial Recurrent Dislocation OfIsrael
-
University of Colorado, DenverNational Institutes of Health (NIH)RecruitingRacially/Ethnically Diverse Families From Urban SettingsUnited States
-
Rambam Health Care CampusWithdrawnFamilial Mediterranean Fever (FMF )
-
AstraZenecaRecruiting
-
Washington University School of MedicineEnrolling by invitationMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Lou Gehrig Disease | Familial Amyotrophic Lateral Sclerosis | Motor Neuron Disease, FamilialUnited States