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Clinical Trials on Familial Hemophagocytic Lymphohistiocytosis
Total 1235 results
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UniQure Biopharma B.V.CompletedLipoprotein Lipase Deficiency | Familial Hyperlipoproteinemia Type 1 | Familial HyperchylomicronemiaGermany
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Brazil, Canada, France, Germany, Hungary, Israel, Italy, Netherlands, South Africa, Spain, United Kingdom
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Organon and CoCompletedPrimary Hypercholesterolemia and Homozygous Familial Hypercholesterolemia (HoFH)
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REGENXBIO Inc.CompletedHomozygous Familial Hypercholesterolemia (HoFH)United States
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Fondazione Policlinico Universitario Agostino Gemelli...RecruitingHereditary Transthyretin AmyloidosisItaly
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Cambridge University Hospitals NHS Foundation TrustRecruitingDiabetes | Diet Modification | LipodystrophyUnited Kingdom
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National Jewish HealthUniversity of Colorado, Denver; Vanderbilt University; Landspitali University...RecruitingIdiopathic Pulmonary Fibrosis | Idiopathic Interstitial Pneumonia | Familial Pulmonary Fibrosis | Familial Interstitial PneumoniaUnited States, Iceland
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Alnylam PharmaceuticalsActive, not recruitingTransthyretin Amyloidosis | Amyloidosis, HereditaryUnited States, Argentina, Australia, Belgium, Brazil, Bulgaria, Canada, Cyprus, France, Germany, Greece, Italy, Japan, Korea, Republic of, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Taiwan, United Kingdom
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New French Society of AtherosclerosisAkcea TherapeuticsCompletedFamilial Chylomicronemia Syndrome | Multifactorial Chylomicronemia SyndromeFrance
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Boston Medical CenterEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedLow Income Families Basic Social NeedsUnited States
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University of UtahNational Institute on Aging (NIA)CompletedDementia, FamilialUnited States
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University of NottinghamUniversity of OxfordCompletedFamilial Breast CancerUnited Kingdom
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Katarzyna HolcmanRecruitingTransthyretin AmyloidosisPoland
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University Hospital, BordeauxUniversity of BordeauxCompletedAmyloid Neuropathies, FamilialFrance
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Centre Hospitalier Universitaire de NīmesCompletedTransthyretin AmyloidosisFrance
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NYU Langone HealthWithdrawnFamilial DysautonomiaUnited States
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Medical University InnsbruckUnknownFamilial Hypobetalipoproteinaemia - Heterozygous Form | Low-LDL-syndromeAustria
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Yonsei UniversityCompletedFamilial Hypertrophic CardiomyopathyKorea, Republic of
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John Paul II Hospital, KrakowRecruitingTransthyretin AmyloidosisPoland
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University of MichiganNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)RecruitingPregnancy Related | Obesity; FamilialUnited States
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University of Southern CaliforniaEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsCompletedObesity | Obesity, Childhood | Obesity; FamilialUnited States
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Hospices Civils de LyonCompletedFamilial Chylomicronemia Syndrome | Multifactorial Chylomicronemia SyndromeFrance
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Aegerion Pharmaceuticals, Inc.WithdrawnHomozygous Familial Hypercholesterolemia
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University of Sao PauloMerck Sharp & Dohme LLCUnknownHeterozigous Familial HypercholesterolemiaBrazil
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Rambam Health Care CampusWithdrawnFamilial Mediterranean Fever (FMF )
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Akcea TherapeuticsUnited BioSource, LLCRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, France, Greece, Italy, Spain, Canada, Germany, Portugal
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PfizerCompletedPolyneuropathy | Hereditary Transthyretin Amyloidosis (ATTRv)Spain
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Montreal Heart InstituteCanadian Institutes of Health Research (CIHR)Enrolling by invitationCardiomyopathies | Hypertrophic Cardiomyopathy | Hypertrophic Obstructive Cardiomyopathy | Familial Hypertrophic CardiomyopathyCanada
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PfizerCompletedTransthyretin Amyloidosis | Transthyretin Gene MutationsUnited States, France, Spain, Taiwan, Israel, Korea, Republic of, Denmark, Canada, Netherlands, Japan, Sweden, Brazil, Mexico, Argentina, Portugal, Belgium, Bulgaria, Cyprus, Germany, Italy, Malaysia, Romania, Saudi Arabia, Turkey, United...
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Chylomicronemia Syndrome | Lipoprotein Lipase Deficiency | Hyperlipoproteinemia Type 1United States, Canada, Germany, Israel, Italy, South Africa, Spain, United Kingdom, Brazil, France, Netherlands
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.CompletedFamilial Chylomicronemia Syndrome | Lipoprotein Lipase Deficiency | Hyperlipoproteinemia Type 1Canada
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University of MichiganCompletedNAFLD | Nonalcoholic Steatohepatitis | Familial Partial LipodystrophyUnited States
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University of Colorado, DenverNational Institutes of Health (NIH)RecruitingRacially/Ethnically Diverse Families From Urban SettingsUnited States
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Meir Medical CenterRambam Health Care Campus; Hadassah Medical Organization; Assaf-Harofeh Medical... and other collaboratorsUnknownPatella, Familial Recurrent Dislocation OfIsrael
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AlbireoActive, not recruitingProgressive Familial Intrahepatic CholestasisUnited States, Spain, Netherlands, United Kingdom, Turkey, Canada, Italy, Germany, France, Israel, Australia, Belgium, Poland, Saudi Arabia, Sweden
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Yale UniversityCompletedFamilial Alcoholism VulnerabilityUnited States
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Institute of Liver and Biliary Sciences, IndiaKEM Hospital Research Centre; Apollo Hospital, New Delhi, India; Jaslok Hospital... and other collaboratorsRecruitingProgressive Familial Intrahepatic CholestasisIndia
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University Medical Center GroningenEnrolling by invitationProgressive Familial Intrahepatic CholestasisNetherlands
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AstraZenecaRecruiting
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Washington University School of MedicineEnrolling by invitationMotor Neuron Disease | Amyotrophic Lateral Sclerosis | Lou Gehrig Disease | Familial Amyotrophic Lateral Sclerosis | Motor Neuron Disease, FamilialUnited States
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University of MichiganNot yet recruitingPregnancy Related | Infant Behavior | Obesity; FamilialUnited States
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University of Alabama at BirminghamNational Institute on Minority Health and Health Disparities (NIMHD)Active, not recruitingObesity | Obesity, Childhood | Obesity; FamilialUnited States
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Alnylam PharmaceuticalsCompletedFamilial Amyloidotic Cardiomyopathy (FAC)United States, France, Spain, United Kingdom, Belgium, Brazil
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University of California, San FranciscoDestination: Home SV; Sí Se Puede Collective; Sacred Heart Community Service; County...RecruitingFamilies Experiencing Homelessness and/or Housing InstabilityUnited States
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University of California, Los AngelesVA Greater Los Angeles Healthcare SystemWithdrawnVeteran Families | Family Communications | Civilian Life ReintegrationUnited States
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Verve Therapeutics, Inc.Not yet recruitingHypercholesterolemia | Atherosclerotic Cardiovascular Disease | Heterozygous Familial HypercholesterolemiaNew Zealand, United Kingdom
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Akcea TherapeuticsRecruitingHereditary Transthyretin Amyloidosis With PolyneuropthyUnited States, Canada
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Verve Therapeutics, Inc.Active, not recruitingHypercholesterolemia | Atherosclerotic Cardiovascular Disease | Heterozygous Familial HypercholesterolemiaNew Zealand, United Kingdom
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University of MessinaUniversità degli Studi di Ferrara; University of Pavia; Careggi Hospital; Fondazione...UnknownPatient-Reported Outcome Measures in Wild-Type and Variant Cardiac Transthyretin Amyloidosis (ITALY)Transthyretin AmyloidosisItaly
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Novartis PharmaceuticalsCompletedColchicine Resistant/Intolerant Familial Mediterranean FeverIsrael