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Clinical Trials on Familial Hypercholesterolemias
Total 2100 results
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AstraZenecaCompletedDyslipidemia, Hypercholesterolemia, HypertriglyceridemiaUnited States
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Merck Sharp & Dohme LLCTerminatedMixed Dyslipidemia | Primary Hypercholesterolemia
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Daiichi Sankyo Europe, GmbH, a Daiichi Sankyo CompanyWithdrawnMixed Dyslipidemia | Primary Hypercholesterolemia
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AmgenTerminatedMixed Dyslipidemia | Primary HypercholesterolemiaChina
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AmgenCompletedMixed Dyslipidemia | Primary HypercholesterolemiaUnited States, Canada
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Kowa Research EuropeCompletedHypercholesterolemia or Combined DyslipidemiaDenmark, Israel, Netherlands, Germany, United Kingdom
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Instituto Aragones de Ciencias de la SaludUnknownArteriosclerosis | Aortic Stenosis | Familial Hypercholesterolemia | Conventional Transthoracic EchocardiogramSpain
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Novartis PharmaceuticalsNot yet recruitingMixed Dyslipidemia | Primary Hypercholesterolemia
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Boryung Pharmaceutical Co., LtdRecruitingMixed Dyslipidemia | Primary HypercholesterolemiaKorea, Republic of
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Orient Pharma Co., Ltd.CompletedPrimary Hypercholesterolemia | Mixed DyslipidemiasTaiwan, Australia, New Zealand
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Merck Sharp & Dohme LLCCompletedMixed Dyslipidemia | Primary Hypercholesterolemia
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Merck Sharp & Dohme LLCCompletedMixed Dyslipidemia | Primary Hypercholesterolemia
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CENTOGENE GmbH RostockAlnylam PharmaceuticalsRecruitingCardiomyopathies | Polyneuropathies | Transthyretin Amyloidosis | Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid PolyneuropathyGermany, Austria, Switzerland
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Novartis PharmaceuticalsActive, not recruitingPrimary Hypercholesterolemia or Mixed DyslipidemiaChina
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Hikma Pharmaceuticals LLCCompletedPrimary Hypercholesterolemia
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Boston UniversityNational Institute of Neurological Disorders and Stroke (NINDS); Food and Drug...CompletedFamilial Amyloid Polyneuropathy | Familial AmyloidosisUnited States, Italy, Japan, Sweden, United Kingdom
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PfizerCompletedTransthyretin Familial Amyloid PolyneuropathyJapan
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Eidos Therapeutics, a BridgeBio companyWithdrawnTransthyretin-Related (ATTR) Familial Amyloid Polyneuropathy
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Otsuka Beijing Research InstituteUnknownSevere HypercholesterolemiaChina
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Karo Bio ABCompleted
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AmgenCompletedHypercholesterolemia and High Risk for Cardiovascular EventsJapan
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Marcello ArcaPfizer; Göteborg University; University of HelsinkiNot yet recruitingFamilial Hypobetalipoproteinemia | Familial Hypobetalipoproteinemia - Heterozygous Form
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Purdue UniversityUnknownPhysical Inactivity | Nonfamilial HypercholesterolemiaUnited States
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Eidos Therapeutics, a BridgeBio companyWithdrawnTransthyretin-Related (ATTR) Familial Amyloid PolyneuropathyUnited States
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SOM Innovation Biotech SAHospital Vall d'HebronCompleted
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid PolyneuropathiesUnited States, Canada, Argentina, Australia, Bulgaria, Cyprus, Italy, Japan, Malaysia, Mexico, Netherlands, Portugal, Spain, Sweden, Germany, France, Brazil, Turkey, Korea, Republic of, Taiwan, United Kingdom
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Alnylam PharmaceuticalsApproved for marketingAmyloid Neuropathies | Amyloid Neuropathies, Familial | TTR-mediated Amyloidosis | Amyloidosis, Hereditary | Amyloidosis, Hereditary, Transthyretin-Related | Familial Amyloid Polyneuropathies
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University Hospital, LilleRecruitingFamilial Partial Lipodystrophy Type 2France
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Intellia TherapeuticsRecruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisUnited Kingdom, New Zealand, Sweden
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Intellia TherapeuticsActive, not recruitingTransthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy | Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy | Wild-Type Transthyretin Cardiac AmyloidosisFrance, United Kingdom, New Zealand, Sweden
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Boryung Pharmaceutical Co., LtdCompletedHypertension | Hyperlipidemia (E.G., Hypercholesterolemia)Korea, Republic of
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NovartisCompletedHYPERTENSION | HYPERCHOLESTEROLEMIAUnited States
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Mirum Pharmaceuticals, Inc.Active, not recruitingProgressive Familial Intrahepatic Cholestasis (PFIC)United States, Argentina, France, Singapore, United Kingdom, Belgium, Turkey, Austria, Brazil, Canada, Colombia, Germany, Italy, Lebanon, Mexico, Poland
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Mirum Pharmaceuticals, Inc.CompletedProgressive Familial Intrahepatic Cholestasis (PFIC)Italy, United States, Argentina, France, Singapore, United Kingdom, Austria, Brazil, Mexico, Lebanon, Germany, Turkey, Poland, Belgium, Canada, Colombia, Hungary
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TakedaActive, not recruitingProgressive Familial Intrahepatic Cholestasis (PFIC)Japan
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Mirum Pharmaceuticals, Inc.WithdrawnProgressive Familial Intrahepatic Cholestasis (PFIC)
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CENTOGENE GmbH RostockWithdrawnTransthyretin Amyloidosis | Transthyretin Amyloid Cardiopathy | Transthyretin-Related (ATTR) Familial Amyloid PolyneuropathyIndia, Germany
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Seoul National University HospitalRecruitingFamilial Exudative VitreoretinopathiesKorea, Republic of
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Boryung Pharmaceutical Co., LtdCompletedEssential Hypertension | Primary HypercholesterolemiaKorea, Republic of
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Boryung Pharmaceutical Co., LtdRecruitingEssential Hypertension | Primary HypercholesterolemiaKorea, Republic of
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Boryung Pharmaceutical Co., LtdRecruitingEssential Hypertension | Primary HypercholesterolemiaKorea, Republic of
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Hanlim Pharm. Co., Ltd.UnknownHypertension | Primary HypercholesterolemiaKorea, Republic of
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PfizerCompletedTransthyretin Familial Amyloidosis Polyneuropathy (TTR-FAP) | Transthyretin Cardiomyopathy (TTR-CM) | Familial Amyloid Cardiomyopathy | Senile Systemic Amyloidosis (SSA)
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Alnylam PharmaceuticalsCompletedAmyloid Neuropathies | Amyloid Neuropathies, Familial | Amyloidosis, Hereditary | Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC) | Amyloidosis, Hereditary, Transthyretin-Related | Familial Transthyretin Cardiac AmyloidosisUnited States, France, Italy, Spain, Canada, Germany, Belgium, Sweden, United Kingdom
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Novartis PharmaceuticalsCompletedFamilial Chylomicronemia Syndrome (FCS)South Africa, Spain, France, Germany, United Kingdom, United States, Canada, Netherlands
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Washington University School of MedicineIncyte CorporationNo longer available
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Ionis Pharmaceuticals, Inc.CompletedAmyloidosis | Familial Amyloid Polyneuropathy | FAP | TTR | TransthyretinUnited States, Spain, Argentina, Brazil, France, Germany, Italy, Portugal, United Kingdom
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Ionis Pharmaceuticals, Inc.CompletedAmyloidosis | Familial Amyloid Polyneuropathy | FAP | TTR | TransthyretinNew Zealand, United States, Spain, Argentina, Brazil, France, Germany, Italy, Portugal, United Kingdom
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Novartis PharmaceuticalsTerminatedFamilial Chylomicronemia Syndrome (FCS) (HLP Type I)South Africa, Germany, United Kingdom, France, United States, Canada, Netherlands