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Clinical Trials on Fibrinogen Deficiency, Congenital in United States
Total 8159 results
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OctapharmaCompletedCongenital Fibrinogen Deficiency | AfibrinogenemiaIran, Islamic Republic of, United States, Bulgaria, India, Switzerland, United Kingdom
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OctapharmaCompletedCongenital Fibrinogen DeficiencyUnited States, Bulgaria, India, Iran, Islamic Republic of, Lebanon, Russian Federation, Saudi Arabia, Turkey, United Kingdom
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CSL BehringCompletedCongenital Fibrinogen DeficiencyUnited States, Canada
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UCSF Benioff Children's Hospital OaklandUniversity of California, San FranciscoCompletedInflammatory Response | Self-regulation | Fibrinogen Abnormality | Telomere Length, Mean Leukocyte | Atopic | Acute InfectionUnited States
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Centers for Disease Control and PreventionCompleted
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QOL Medical, LLCCompletedCongenital Sucrase-Isomaltase DeficiencyUnited States
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CSL BehringCompleted
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University of MinnesotaRecruiting
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Northwestern UniversityCompletedCongenital Leptin Deficiency (Disorder)United States
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Maggie's Pearl, LLCActive, not recruitingPmm2-CDG | Phosphomannomutase 2 Deficiency | Phosphomannomutase 2 Congenital Disorder of Glycosylation | Phosphomannomutase II Congenital Disorder of Glycosylation | Phosphomannomutase II DeficiencyUnited States
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University of Alabama at BirminghamCompletedFolic Acid Deficiency | Neural Tube Defects | FortificationUnited States
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Cure CMDCongenital Muscle Disease International RegistrWithdrawnLAMA2-MD (Merosin Deficient Congenital Muscular Dystrophy, MDC1A)United States
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Hydrocephalus and Neuroscience InstituteCompletedFolic Acid Deficiency | Neural Tube Defects | Spina Bifida | Anencephaly-Spina BifidaUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyUnited Kingdom, Israel, United States
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Jerry Vockley, MD, PhDUltragenyx Pharmaceutical IncNo longer availableBarth Syndrome | Mitochondrial Trifunctional Protein Deficiency | Very Long-chain acylCoA Dehydrogenase (VLCAD) Deficiency | Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2) | Long-chain Hydroxyacyl-CoA Dehydrogenase Deficiency | Glycogen Storage Disorders | Pyruvate Carboxylase Deficiency... and other conditionsUnited States
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Boston Children's HospitalTerminatedFanconi Anemia | Dyskeratosis CongenitaUnited States
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QOL Medical, LLCJohns Hopkins University; Massachusetts General Hospital; Baylor College of Medicine and other collaboratorsCompletedCongenital Sucrase-isomaltase Deficiency (CSID)United States
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Emory UniversityChildren's Healthcare of AtlantaTerminatedSickle Cell Disease | Fanconi Anemia | Thalassemia | Severe Congenital Neutropenia | Wiskott-Aldrich Syndrome | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Glanzmann Thrombasthenia | Leukocyte Adhesion Deficiency | Dyskeratosis-congenita | Chediak-Higashi Syndrome | Chronic-granulomatous Disease | Schwachman-Diamond...United States
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Eva Morava-KoziczChildren's Hospital of Philadelphia; Seattle Children's HospitalNot yet recruiting
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Prometic Biotherapeutics, Inc.CompletedHypoplasminogenemia | Congenital Plasminogen DeficiencyUnited States, Norway
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University of Alabama at BirminghamGrifols Biologicals, LLCCompletedCongenital Heart Disease | HypogammaglobulinemiaUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyUnited States, Israel, United Kingdom
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University of Mississippi, OxfordCompletedMalaria | Glucose 6 Phosphate Dehydrogenase DeficiencyUnited States
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Agios Pharmaceuticals, Inc.TerminatedAnemia | Anemia, Hemolytic | Pyruvate Kinase Deficiency | Pyruvate Kinase Deficiency AnemiaUnited States, United Kingdom, Italy, Spain, Netherlands
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OctapharmaRecruitingCongenital Antithrombin DeficiencySpain, United States, Italy, France, Hungary, Austria, Germany, United Kingdom
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Emory UniversityCompletedSickle Cell Disease | Fanconi Anemia | Hurler Syndrome | Chronic Granulomatous Disease | Severe Congenital Neutropenia | Hemophagocytic Lymphohistiocytosis | Wiskott-Aldrich Syndrome | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Glanzmann Thrombasthenia | Shwachman-Diamond Syndrome | Thalassemia Major | Leukocyte... and other conditionsUnited States
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QOL Medical, LLCRecruitingCongenital Sucrase-Isomaltase Deficiency | CSID | Sucrase Isomaltase DeficiencyUnited States
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencyUnited States
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University of California, San FranciscoCompletedSickle Cell Disease | Hemoglobinopathies | Fanconi Anemia | Thalassemia | Hematologic Malignancies | Immune Deficiency | Nonmalignant Diseases | Genetic Inborn Errors of MetabolismUnited States
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Gary M Brittenham, MDActive, not recruitingRespiratory Tract Infections | Respiratory Tract Diseases | Respiration Disorders | Lung Diseases | Nutrition Disorders | Vitamin D Deficiency | Asthma | Sickle Cell Disease | Anemia, Sickle Cell | Anemia, Hemolytic, Congenital | Acute Chest Syndrome | Deficiency Diseases VitaminUnited States
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PATHFred Hutchinson Cancer CenterCompletedG6PD DeficiencyUnited States
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PATHCompletedG6PD DeficiencyUnited States
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National Center for Research Resources (NCRR)Completed
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Columbia UniversityNew York Blood CenterCompleted
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Congenital FXIII DeficiencySpain, United States, Canada, Italy, United Kingdom, Hungary
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University of Mississippi, OxfordUniversity of Colorado, Denver; Southern Research InstituteUnknown
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Kyowa Hakko Kirin UK, Ltd.CompletedCongenital Antithrombin DeficiencyFrance, Germany, Italy, Sweden, United Kingdom
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University of North Carolina, Chapel HillCompletedDevelopmental Cochlear Nerve Deficiency | Acquired Cochlear Nerve Deficiency | Cochlear Aplasia | Post-meningitis Cochlear Ossification | Cochlear MalformationUnited States
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Northwell HealthStaten Island University HospitalCompletedVitamin B12 DeficiencyUnited States
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Rhythm Pharmaceuticals, Inc.CompletedBardet-Biedl Syndrome | POMC Deficiency Obesity | PCSK1 Deficiency Obesity | LEPR Deficiency ObesityUnited States, Australia, Spain, United Kingdom
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Congenital FXIII DeficiencyUnited Kingdom
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Congenital FXIII DeficiencyUnited Kingdom
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Johnson & Johnson Pharmaceutical Research & Development...Completed21-hydroxylase DeficiencyUnited States
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St. Jude Children's Research HospitalBaylor College of Medicine; Children's Hospital of Philadelphia; Dana-Farber... and other collaboratorsRecruitingMyelodysplastic Syndromes | Sickle Cell Disease | Fanconi Anemia | Severe Congenital Neutropenia | Bone Marrow Failure Syndromes | Blood Coagulation Disorder | Erythrocyte Disorder | Leukocyte Disorder | Hemostasis | Dyskeratosis Congenita | Diamond-Blackfan Anemia | Congenital Thrombocytopenia | Myeloproliferative...United States
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Prothelia, Inc.Cure CMD; The Bönnemann Laboratory, NINDS, National Institutes of Health; Oscar... and other collaboratorsCompletedMerosin Deficient Congenital Muscular DystrophyUnited States
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Maria I. NewNational Center for Research Resources (NCRR); Office of Rare Diseases (ORD)Completed21-hydroxylase DeficiencyUnited States, Brazil
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Baebies, Inc.CompletedG6PD Deficiency | G6PDUnited States
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Children's Hospital of PhiladelphiaPenn State University; Newcastle UniversityCompletedSickle Cell Anemia in Children | Vitamin A Deficiency in ChildrenUnited States
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Novo Nordisk A/SCompletedHealthy | Congenital Bleeding Disorder | Congenital FXIII DeficiencyUnited Kingdom
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rEVO BiologicsCompletedAntithrombin Deficiency, CongenitalFrance, United Kingdom, Germany, United States, Sweden, Italy