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Clinical Trials on Fragile X Syndrome
Total 35146 results
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University of ValenciaFundación para la Investigación del Hospital Clínico de ValenciaCompletedQuality of Life | Frail Elderly Syndrome | Cognitive Decline | Adherence, Patient | Mood | Social InteractionSpain
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National Human Genome Research Institute (NHGRI)National Institute of Allergy and Infectious Diseases (NIAID); National Institute...CompletedCGD | Wiskott-Aldrich Syndrome | Primary Immunodeficiencies | APECED | SCIDUnited States
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Rigel PharmaceuticalsRecruitingLow Risk Myelodysplastic SyndromesUnited States
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Bristol-Myers SquibbActive, not recruitingLower-risk Myelodysplastic SyndromesJapan
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AkesoRecruitingHigher-risk Myelodysplastic SyndromesUnited States, China
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Nuwacell Biotechnologies Co., Ltd.The First Affiliated Hospital of University of Science and Technology of...Not yet recruitingRelapsed / Refractory Myelodysplastic Syndromes
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Wake Forest University Health SciencesNational Cancer Institute (NCI)TerminatedPreviously Treated Myelodysplastic SyndromesUnited States
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University of SalamancaExcelentísimo Ayuntamiento de SalamancaCompleted
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University of ManitobaTerminated
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McMaster UniversityCanadian Frailty NetworkCompleted
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National University of SingaporeSingapore General Hospital; Duke-NUS Graduate Medical SchoolCompleted
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Health Center of the City of JoensuuUnknown
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University of Colorado, DenverActive, not recruitingHigh Grade Myelodysplastic SyndromesUnited States
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ALX Oncology Inc.Active, not recruitingHigher Risk Myelodysplastic SyndromesKorea, Republic of, United States, Spain
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The University of QueenslandRoyal Brisbane and Women's HospitalUnknown
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Thomas Jefferson UniversityCompleted
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US Department of Veterans AffairsCompleted
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Lund UniversityCompleted
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University Hospital, Basel, SwitzerlandCompleted
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PfizerTerminated
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Mitsubishi Tanabe Pharma America Inc.RecruitingErythropoietic Protoporphyria (EPP) | X-Linked Protoporphyria (XLP)United States, Spain, France, United Kingdom, Japan, Italy, Australia, Bulgaria, Czechia, Netherlands, Poland
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Edimer PharmaceuticalsCompletedX Linked Hypohidrotic Ectodermal DysplasiaUnited States
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Université Catholique de LouvainFonds National de la Recherche ScientifiqueCompletedFrail Elderly InpatientBelgium
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National Cancer Institute (NCI)RecruitingFanconi Anemia | Dyskeratosis Congenita | Diamond Blackfan Anemia | Shwachman Diamond Syndrome | Inherited Bone Marrow Failure Syndrome, Aplastic AnemiaUnited States
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National Heart, Lung, and Blood Institute (NHLBI)CompletedHeart Diseases | Cardiovascular Diseases | Obesity | Atherosclerosis | Hypertriglyceridemia | Metabolic Syndrome X
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The University of Texas Health Science Center,...RecruitingNeuropsychiatric SyndromesUnited States
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Edimer PharmaceuticalsActive, not recruitingX-linked Hypohidrotic Ectodermal DysplasiaUnited States, United Kingdom, France, Germany, Italy
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Helsinki University Central HospitalUniversity of Helsinki; City of EspooCompletedQuality of Life | Frail Elderly Syndrome | Fall | Hospital Readmission | Length of Stay | Patient AdmissionFinland
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Yeovil District Hospital NHS Foundation TrustUniversity of Southampton; University Hospital Southampton NHS Foundation Trust and other collaboratorsUnknownEmergencies | Frail Elderly Syndrome | Sarcopenia | SurgeryUnited Kingdom
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Groupe Francophone des MyelodysplasiesUnknownAnemia in Myelodysplastic SyndromesFrance
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Sumitomo Pharma America, Inc.TerminatedAnemia in Myelodysplastic SyndromesUnited States
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Viking Therapeutics, Inc.RecruitingAdrenomyeloneuropathy Form (AMN) of X-linked Adrenoleukodystrophy (X-ALD)United States, France, Germany, Italy, United Kingdom
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Maastricht University Medical CenterZonMw: The Netherlands Organisation for Health Research and Development; Netherlands...CompletedDiabetes Mellitus, Type 2 | Mild Cognitive Impairment | Metabolic Syndrome XNetherlands
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EspeRare FoundationIqvia Pty Ltd; Pierre Fabre MedicamentRecruitingX-Linked Hypohidrotic Ectodermal Dysplasia (XLHED)United States, Spain, France, Germany, Italy, United Kingdom
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National Institute of Allergy and Infectious Diseases...CompletedGenetic Diseases, X-Linked | Lymphoproliferative Disease | X-Linked Lymphoproliferative DiseaseUnited States
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Denali Therapeutics Inc.CompletedMucopolysaccharidosis IIUnited Kingdom, United States, Italy, Netherlands
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ShireCompleted
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TakedaTakeda Development Center Americas, Inc.Active, not recruitingHunter SyndromeUnited States, Germany, Malaysia, Philippines, Thailand, Dominican Republic, Serbia, Vietnam
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University of Maryland, BaltimoreChildren's Hospital of PhiladelphiaWithdrawnOsteoporosis Pseudoglioma SyndromeUnited States
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Peking University Third HospitalCompletedParaneoplastic Neurological SyndromeChina
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Brian JonasNational Cancer Institute (NCI); Celgene; Pharmacyclics LLC.CompletedPreviously Treated Myelodysplastic Syndrome | Myelodysplastic Syndrome | Therapy-Related Myelodysplastic Syndrome | Secondary Myelodysplastic Syndrome | Refractory High Risk Myelodysplastic SyndromeUnited States
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The Champ FoundationChildren's Hospital of Philadelphia; The Cleveland ClinicRecruitingPearson Syndrome | Single Large Scale Mitochondrial DNA Deletion Syndromes (SLSMDS)United States
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Denali Therapeutics Inc.Active, not recruitingMucopolysaccharidosis IIUnited States, Netherlands, Canada, United Kingdom
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Zimmer BiometMaisonneuve-Rosemont HospitalCompletedTotal Knee Arthroplasty / Position of Customized X-Ray PSI Guides Using Optical Navigation
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argenxRecruitingCongenital Myasthenic SyndromeUnited States, Canada, France
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Catalyst Pharmaceuticals, Inc.CompletedMyasthenic Syndromes, CongenitalUnited States
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Erasme University HospitalBrussel Medical Device Center (BMDC)RecruitingBlind Loop Syndrome Postoperative | Candy Cane SyndromeBelgium
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University of ZurichCompletedFocus of the Study: DNA Damage Due to Medical Diagnostic X-raySwitzerland
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University of WashingtonNational Heart, Lung, and Blood Institute (NHLBI)CompletedHeart Diseases | Cardiovascular Diseases | Coronary Disease | Diabetes Mellitus | Insulin Resistance | Metabolic Syndrome X | Diabetes Mellitus, Non-insulin Dependent