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Clinical Trials on Gaucher Disease
Total 380056 results
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseUnited States
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseUnited States, Sweden, India, Netherlands, Austria, Japan, China, Serbia, France, Croatia, Australia, Portugal, Canada, Brazil, Greece, Romania, Russian Federation
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ISU Abxis Co., Ltd.Completed
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TakedaActive, not recruiting
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CENTOGENE GmbH RostockActive, not recruiting
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Lysosomal and Rare Disorders Research and Treatment...UnknownGaucher DiseaseUnited States
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PfizerCompletedGaucher DiseaseIsrael, South Africa, Paraguay
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PfizerCompletedGaucher DiseaseUnited States, Chile, United Kingdom, Israel, Canada, Spain, South Africa, Italy
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Hospital St. Joseph, Marseille, FranceCompleted
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Assistance Publique - Hôpitaux de ParisCompletedGaucher DiseaseFrance
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Amicus TherapeuticsCompleted
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Shoshana VilkGenzyme, a Sanofi CompanyCompletedGaucher Disease | Patient Reported OutcomeIsrael
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National Taiwan University HospitalActelionUnknown
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CENTOGENE GmbH RostockCompletedLysosomal Storage Diseases | Sphingolipidoses | Gaucher DiseaseAlbania, Greece, India, Israel, Morocco, Pakistan, Spain
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National Institute of Neurological Disorders and...CompletedGaucher DiseaseUnited States
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NYU Langone HealthGenzyme, a Sanofi CompanyCompleted
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Lysosomal and Rare Disorders Research and Treatment...RecruitingBone Diseases | Gaucher DiseaseUnited States
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SanofiCompletedGaucher DiseaseUnited States
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University of California, San FranciscoRecruitingMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VI | Wolman Disease | Pompe Disease Infantile-Onset | Mucopolysaccharidosis IV A | Mucopolysaccharidosis VII | Neuronopathic Gaucher DiseaseUnited States
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Assiut UniversityNot yet recruiting
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SanofiCompletedGaucher Disease | SplenomegalyFrance
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Rambam Health Care CampusUnknown
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GE HealthcareCompletedGather Feasibility Data and User Feedback on Use of a Device in Vivo on Pregnant Volunteers in Their 2nd and 3rd TrimesterUnited States
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Rabin Medical CenterGenzyme, a Sanofi CompanyUnknown
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PfizerNo longer availableGaucher DiseaseUnited States, Israel
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National Human Genome Research Institute (NHGRI)CompletedParkinson Disease | Gaucher DiseaseUnited States
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CENTOGENE GmbH RostockWithdrawnSplenomegaly | HepatomegalyGermany, India, Sri Lanka
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Lysosomal and Rare Disorders Research and Treatment...UnknownParkinson Disease | Gaucher DiseaseUnited States
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Genzyme, a Sanofi CompanyRecruitingGaucher Disease | Cerebroside Lipidosis Syndrome | Glucocerebrosidase Deficiency Disease | Glucosylceramide Beta-Glucosidase Deficiency DiseaseHungary, Croatia, United States, Australia, Belgium, Brazil, Bulgaria, Canada, Denmark, Germany, Greece, Hong Kong, India, Indonesia, Italy, Jordan, Korea, Republic of, Kuwait, Lebanon, Malaysia, Pakistan, Philippines, Poland, Saudi Arabia and more
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HaEmek Medical Center, IsraelTerminatedLiver Fibrosis | Gaucher Disease | Spleen; FibrosisIsrael
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Shaare Zedek Medical CenterRecruitingParkinson Disease | Gaucher Disease | GBA Gene MutationIsrael
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Pacific Parkinson's Research CentreUniversity of British Columbia; Oregon Health and Science University; University... and other collaboratorsRecruitingParkinson Disease | Gaucher Disease | GBA Gene MutationUnited States, Canada
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New York Stem Cell Foundation Research InstituteSilverstein FoundationRecruitingHealthy | Parkinson Disease | Gaucher Disease | GBA Gene MutationUnited States
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National Human Genome Research Institute (NHGRI)Enrolling by invitationParkinson Disease | Gaucher Disease | Lysosomal Storage DisordersUnited States
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Chung-Hsing WangSanofiNot yet recruiting
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Universidad de Zaragozafundación española para el estudio y tratamiento de la Enfermedad de Gaucher... and other collaboratorsCompleted
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Shaare Zedek Medical CenterUnknownHepatitis C | Gaucher DiseaseIsrael
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Mansoura University Children HospitalUnknownHCV | Gaucher DiseaseEgypt
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M.A.G.I.C. Clinic LTDHanalytics Solutions Inc.RecruitingMitochondrial Diseases | Fabry Disease | Metabolic Disease | Gaucher Disease | Pompe DiseaseCanada
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University of MinnesotaGE HealthcareCompletedParkinson Disease | Gaucher Disease | Idiopathic Rapid Eye Movement Sleep DisorderUnited States
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Masonic Cancer Center, University of MinnesotaCompletedNiemann-Pick Disease | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | GM1 Gangliosidosis | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Tay Sachs Disease | Sandhoff DiseaseUnited States
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Fairview University Medical CenterUnknownMucopolysaccharidosis I | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Metachromatic Leukodystrophy | Pulmonary Complications | Fucosidosis | Globoid Cell Leukodystrophy | Gaucher's Disease | Mannosidosis | I Cell DiseaseUnited States
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Fundación Española de Hematología y HemoterapíaRecruitingNiemann-Pick Diseases | Gaucher Disease | Splenomegaly | Acid SphingoMyelinase Deficiency | ASMDSpain
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Melbourne HealthSanofiWithdrawnLysosomal Storage Diseases | Fabry Disease | Niemann-Pick Disease, Type C | Gaucher DiseaseAustralia
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New York Medical CollegeCompletedMucopolysaccharidosis I | Myelodysplastic Syndrome | Acute Lymphocytic Leukemia | Acute Myelogenous Leukemia | Niemann-Pick Disease | Mucopolysaccharidosis VI | Wolman Disease | Adrenoleukodystrophy | Batten Disease | Metachromatic Leukodystrophy | Diamond-Blackfan Anemia | Severe Aplastic Anemia | Fucosidosis | Gaucher... and other conditionsUnited States
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Fundación Española de Hematología y HemoterapíaRecruitingGaucher Disease | Acid SphingoMyelinase DeficiencySpain
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National Human Genome Research Institute (NHGRI)CompletedCancer | Myelofibrosis | Pulmonary Fibrosis | Gaucher Disease | Hermansky-Pudlak Syndrome (HPS)United States
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O & O Alpan LLCUnknownFabry Disease | Niemann-Pick Disease | Gaucher Disease | Pompe Disease | Lysosomal Storage DisordersUnited States