- ICH GCP
- US Clinical Trials Registry
- Search trials
Clinical Trials on Genetic Disorder
Total 151205 results
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PfizerCompletedHemophilia BUnited States, Spain, Croatia, Serbia, Russian Federation, Canada, Hungary, Italy, Romania
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Wyeth is now a wholly owned subsidiary of PfizerCompleted
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National Human Genome Research Institute (NHGRI)Completed
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Rady Pediatric Genomics & Systems Medicine InstituteEnrolling by invitation
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NewAmsterdam PharmaActive, not recruitingDyslipidemias | Hypercholesterolemia | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Familial Hypercholesterolemia | Metabolic Disease | High Cholesterol | Genetic Disease, Inborn | Lipid Metabolism DisorderUnited States, Canada, Czechia, Georgia, Netherlands, Norway, Poland, South Africa, Spain, United Kingdom
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Hacettepe UniversityCompletedDuchenne Muscular Dystrophy | Ambulation Difficulty | Ambulation Disorder, NeurologicTurkey
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Hospices Civils de LyonRecruiting
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BiocadRecruitingStudy of the Safety, Pharmacodynamics and Efficacy of ANB-002 in Patients With Hemophilia B (SAFRAN)Hemophilia BRussian Federation
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St. Jude Children's Research HospitalNot yet recruiting
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Bahçeşehir UniversityRecruitingHemophilia A | Hemophilia BTurkey
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Institute of Hematology & Blood Diseases HospitalNot yet recruiting
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Institute of Hematology & Blood Diseases HospitalRecruiting
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PfizerRecruitingHemophilia A | Hemophilia BHong Kong, Spain, Serbia, Turkey, United States, China, Mexico, South Africa, India, Japan, Croatia, Korea, Republic of, Oman, Taiwan, Italy, Canada, France
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McMaster UniversityRecruiting
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CSL BehringActive, not recruiting
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PfizerActive, not recruitingHemophilia A | Hemophilia BUnited States, Canada, Spain, Australia, Korea, Republic of, Taiwan, Brazil, Italy, Japan, Turkey, Germany, United Kingdom, Saudi Arabia, France, Sweden, Belgium, Greece, Israel
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CSL BehringEnrolling by invitation
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PfizerActive, not recruitingHemophilia BUnited States, Canada, Australia, Turkey
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McMaster UniversityEnrolling by invitationWeb Accessible Population Pharmacokinetics Service - Hemophilia: Sources of Variability (WAPPS-Hemo)Hemophilia A | Hemophilia BCanada
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Baxalta now part of ShireBaxalta Innovations GmbH, now part of ShireCompleted
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CSL BehringCompletedHemophilia BUnited States, Australia, Japan, France, Philippines, Spain, Czechia, Israel, Canada, Germany, Austria, Bulgaria, Italy, Malaysia, South Africa
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Baxalta now part of ShireCompletedHemophilia BRussian Federation, Ukraine, India, Poland, Romania, United Kingdom
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OPKO Health, Inc.CompletedHemophilia A | Hemophilia BUnited States
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Baxalta now part of ShireCompletedHemophilia BTaiwan, Colombia, Argentina, Brazil, Bulgaria, Chile, Czechia, India, Ireland, Italy, Japan, Poland, Romania, Russian Federation, Sweden, Ukraine, United Kingdom
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Medexus Pharma, Inc.TerminatedHemophilia BUnited States, United Kingdom, India
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National Taiwan University HospitalUnknown
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Grifols Biologicals, LLCCompleted
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Cangene CorporationWithdrawnHemophilia BUnited Kingdom, United States
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PfizerCompleted
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CSL BehringCompletedHemophilia BBulgaria, Israel
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BayerCompletedHemophilia A | Hemophilia BSouth Africa, Poland, United Kingdom
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PfizerCompletedHemophilia BKorea, Republic of
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Weill Medical College of Cornell UniversityUniversity of Pennsylvania; CSL BehringCompletedHemophilia A | Hemophilia BUnited States, Puerto Rico
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Weill Medical College of Cornell UniversityBayer; University Hospital, BonnCompletedHemophilia A | Hemophilia BUnited States, Israel, Australia, Italy, Sweden, Germany, Japan, Netherlands, Taiwan
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Wyeth is now a wholly owned subsidiary of PfizerCompleted
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Wyeth is now a wholly owned subsidiary of PfizerCompletedHemophilia BBelgium, Spain, Italy, Austria, United Kingdom, Netherlands, Sweden, Germany, Portugal, France
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Wyeth is now a wholly owned subsidiary of PfizerCompleted
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Wyeth is now a wholly owned subsidiary of PfizerCompletedHemophilia A | Hemophilia B
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Wyeth is now a wholly owned subsidiary of PfizerCompleted
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Prothya BiosolutionsCompletedHemophilia BNetherlands
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Seoul National University HospitalMinistry of Health & Welfare, KoreaCompletedGenetic High Risk for SchizophreniaKorea, Republic of
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Menarini Biomarkers SingaporeRecruitingPregnancy Related | Genetic Disease | Prenatal ScreeningItaly
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Novo Nordisk A/SCompletedChronic Kidney Disease | Turner Syndrome | Chronic Renal Insufficiency | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic Disorder | Delivery Systems | Foetal Growth Problem | Small for Gestational AgeFrance
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Novo Nordisk A/SCompletedChronic Kidney Disease | Turner Syndrome | Chronic Renal Insufficiency | Growth Hormone Disorder | Growth Hormone Deficiency in Children | Genetic Disorder | Delivery Systems | Foetal Growth Problem | Small for Gestational AgeFrance
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Dana-Farber Cancer InstituteBrigham and Women's HospitalCompletedHemophilia A | Hemophilia BUnited States
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Queen Fabiola Children's University HospitalCenter of Human Genetics - ULB in Brussels; Interuniversity Institute of Bioinformatics...UnknownGenodermatosis | Rare Genetic Disease With Cutaneous ExpressionBelgium
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Retina Foundation of the SouthwestDSM Nutritional Products, Inc.; Foundation Fighting BlindnessCompletedRetinitis Pigmentosa | X-linked Genetic DiseasesUnited States
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Children's Hospital of PhiladelphiaNational Institutes of Health (NIH); National Human Genome Research Institute...Recruiting
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The Leeds Teaching Hospitals NHS TrustGenomic Medicine Services AllianceCompletedGenetic Disease | Bereavement | Fetal AnomalyUnited Kingdom