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Clinical Trials on Genetic Alteration in Australia
Total 961 results
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Bayside HealthUniversity of MelbourneCompletedCystic Fibrosis | Chronic Obstructive Pulmonary Disease (COPD)Australia
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The University of New South WalesRecruitingHealthy | Obstructive Sleep Apnea | Cystic Fibrosis | Hirschprung's DiseaseAustralia
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Michael FrassCompleted
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PfizerRecruitingHemophilia A | Hemophilia BAustralia, United States, Turkey
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Arrowhead PharmaceuticalsActive, not recruitingHomozygous Familial HypercholesterolemiaAustralia, Canada, United States, South Africa
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Murdoch Childrens Research InstituteNational Health and Medical Research Council, Australia; Royal Children's Hospital and other collaboratorsRecruitingCommunicable Diseases | Quality of Life | Inflammation | Obesity | Congenital Abnormalities | Genetics | Healthy Aging | Child Development | Diet | Mental Health | Disability | Injuries | Cognition | Child Health | Environmental Exposure | Noncommunicable Diseases | Physical Fitness | Intergenerational Relations | Social Determinants... and other conditionsAustralia
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PharmaxisCompletedCystic FibrosisAustralia, United Kingdom
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Pixium Vision SACompletedRetinitis Pigmentosa | Choroideremia | Cone Rod DystrophyAustria, France, Germany
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Medical University of ViennaCompleted
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Medical University of ViennaMedical University of GrazUnknownFabry Disease | Left Ventricular HypertrophyAustria
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Tyra Biosciences, IncRecruitingSolid Tumor | Bladder Cancer | Advanced Solid Tumor | Urothelial Carcinoma | Metastatic Urothelial Carcinoma | Solid Tumor, Adult | FGFR3 Gene Mutation | Urinary Tract Cancer | Locally Advanced Urothelial Carcinoma | Advanced Urothelial Carcinoma | Non-muscle-invasive Bladder Cancer | FGFR3 Gene Alteration | Urinary... and other conditionsAustralia, United States, France, Spain
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Neuren Pharmaceuticals LimitedRecruiting
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Medical University of ViennaUnknown
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Austrian Academic Institute for Clinical NutritionMedical University of ViennaCompletedHeterozygous Familial HypercholesterolemiaAustria
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Eloxx Pharmaceuticals, Inc.CompletedCystic FibrosisIsrael, Australia, Germany
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AVROBIOTerminatedFabry DiseaseAustralia, Brazil
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Medical University of ViennaUniversity of Vienna; Griffith UniversityRecruiting
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Medical University of ViennaUnknown
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Australia, Austria, Netherlands, Taiwan, Ukraine
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Sciotec Diagnostic Technologies GmbHNot yet recruitingFructose IntoleranceAustria
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Nacuity Pharmaceuticals, Inc.Foundation Fighting BlindnessActive, not recruitingUsher SyndromesAustralia
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FH Campus Wien, University of Applied SciencesMedical University of Vienna; ShireCompleted
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AOP Orphan Pharmaceuticals AGCompletedCystic FibrosisAustria
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Ascendis Pharma Growth Disorders A/SRecruitingAchondroplasiaUnited States, Australia
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AbbVieCompletedA Study to Evaluate Risankizumab in Adults and Adolescents With Moderate to Severe Atopic DermatitisDermatitisUnited States, Australia, Canada, Japan, Puerto Rico
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University Children's Hospital, ZurichRecruitingInborn Errors of Metabolism | TransitionSwitzerland, Austria
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Medical University of ViennaActive, not recruitingBone Diseases, Metabolic | Bone | HypophosphatasiaAustria
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Amicus TherapeuticsApproved for marketingPhysician Initiated Expanded Access Request for Migalastat in Individual Patients With Fabry DiseaseFabry DiseaseUnited States, Australia
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PfizerAvailableAtopic DermatitisTaiwan, United States, Australia, Austria, Belgium, Canada, Greece, Mexico, Netherlands, Russian Federation, Spain, Switzerland
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bluebird bioCompletedCerebral Adrenoleukodystrophy (CALD)United States, Germany, Argentina, Australia, France, United Kingdom
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Ascendis Pharma Growth Disorders A/SEnrolling by invitationAchondroplasiaUnited States, Australia, Denmark, Ireland, Austria, Germany, New Zealand
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Reata, a wholly owned subsidiary of BiogenAbbVie; Friedreich's Ataxia Research AllianceActive, not recruitingFriedreich AtaxiaUnited States, Australia, Austria, Italy, United Kingdom
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Western Sydney Local Health DistrictWestmead Institute for Medical ResearchCompletedHypertension | Endothelial Dysfunction | Autosomal Dominant Polycystic KidneyAustralia
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Medical University of ViennaUnknownGraves Ophthalmopathy | Graves Disease | Graves' Ophthalmopathy WorsenedAustria
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Weill Medical College of Cornell UniversityBayer; University Hospital, BonnCompletedHemophilia A | Hemophilia BUnited States, Israel, Australia, Italy, Sweden, Germany, Japan, Netherlands, Taiwan
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Murdoch Childrens Research InstituteRoyal Children's HospitalCompletedPrimary Immunodeficiency | Invasive Pneumococcal Disease, Protection Against | Invasive Pneumococcal Disease, Recurrent Isolated, 1 | Invasive Pneumococcal Disease, Recurrent Isolated, 2Australia, New Zealand
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Kirby InstituteGilead Sciences; Melanoma Institute Australia; St Vincent's Hospital, Sydney; Royal... and other collaboratorsActive, not recruitingCOVID-19 | Cancer | Primary Immune Deficiency Disorder | HIV-1-infection | Immunosuppression DisordersAustralia
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Scioderm, Inc.Amicus TherapeuticsTerminatedEpidermolysis BullosaPoland, Spain, Serbia, Netherlands, United States, Austria, Australia, Israel, Germany, France, United Kingdom, Lithuania
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Anavex Life Sciences Corp.Anavex Australia Pty Ltd.; Anavex Germany GmbHCompletedRett SyndromeCanada, Australia, United Kingdom
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Timber Pharmceuticals LLCCompletedCongenital IchthyosisUnited States, Australia
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AbbVieCompletedAtopic DermatitisUnited States, Australia, Canada, Finland, Germany, Japan, Netherlands, Spain
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Tirol Kiniken GmbHLFB BIOMEDICAMENTSUnknown
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency, Type AUnited States, Australia, Netherlands, United Kingdom, Tunisia
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Medical University of GrazCompletedSkin Cancer | Basal Cell Nevus Syndrome | Xeroderma PigmentosumAustria
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Arrowhead PharmaceuticalsTerminatedAlpha-1 Antitrypsin DeficiencyAustralia, Netherlands, Germany, United Kingdom
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States, Canada, Argentina, Australia, Israel, Italy
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Novartis PharmaceuticalsCompletedThalassemia, Non-transfusional-dependent Thalassemia (NTDT), Myeloplastic Dysplasia (MDS), Other AnemiaAustralia
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Suzhou Connect Biopharmaceuticals, Ltd.CompletedModerate-to-severe Atopic DermatitisUnited States, Australia, China, New Zealand
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Baxalta now part of ShireCompletedVon Willebrand DiseaseUnited States, Spain, Australia, Taiwan, Czechia, Turkey, Ukraine, Netherlands, Italy, United Kingdom, Austria, Germany, Russian Federation