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Clinical Trials on Genetic Alteration in Australia
Total 960 results
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University Hospital Birmingham NHS Foundation TrustNorthern Care Alliance NHS Foundation Trust; Cambridge University Hospitals... and other collaboratorsActive, not recruitingArrhythmia Burden, Risk of Sudden Cardiac Death and Stroke in Patients With Fabry Disease (RaILRoAD)Fabry DiseaseUnited Kingdom, Australia
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Suzhou Connect Biopharmaceuticals, Ltd.CompletedModerate-to-severe Atopic DermatitisUnited States, Australia, China, New Zealand
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Baxalta now part of ShireCompletedVon Willebrand DiseaseUnited States, Spain, Australia, Taiwan, Czechia, Turkey, Ukraine, Netherlands, Italy, United Kingdom, Austria, Germany, Russian Federation
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Bristol-Myers SquibbCompletedDermatitis, AtopicGermany, Australia, Poland, Canada, Austria, United States, Spain
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Tirol Kiniken GmbHLFB BIOMEDICAMENTSUnknown
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Disc Medicine, IncEnrolling by invitationErythropoietic ProtoporphyriaUnited States, Australia
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Healx LimitedWithdrawnFragile X SyndromeUnited States, Australia
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Regeneron PharmaceuticalsCompletedHomozygous Familial HypercholesterolemiaUnited States, Netherlands, Australia, Austria, Canada, France, Greece, Italy, Japan, South Africa, Ukraine
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Eli Lilly and CompanyDermira, Inc.CompletedAtopic DermatitisUnited States, Canada, Australia, Poland
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Western Sydney Local Health DistrictRecruitingFamilial Adenomatous PolyposisAustralia
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NovartisCompletedMyelodysplastic Syndromes | Hemoglobinopathies | Diamond-Blackfan Anemia | Transfusional Iron Overload | Other Inherited or Acquired Anaemia | MPD Syndrome | Other Rare AnaemiasAustralia
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bluebird bioCompletedβ-thalassemia MajorUnited States, Australia, Thailand
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Vertex Pharmaceuticals IncorporatedTerminatedCystic FibrosisUnited Kingdom, Canada, Australia
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Hoffmann-La RocheChugai PharmaceuticalCompletedHemophilia AUnited States, Belgium, Spain, Japan, Poland, Australia
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ReveraGen BioPharma, Inc.University of Pittsburgh; Cooperative International Neuromuscular Research...CompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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RHEACELL GmbH & Co. KGFGK Clinical Research GmbH; Ticeba GmbH; Granzer Regulatory Consulting & ServicesCompletedRecessive Dystrophic Epidermolysis BullosaUnited States, Austria, France, Germany, United Kingdom
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Scioderm, Inc.Amicus TherapeuticsCompletedEpidermolysis BullosaItaly, Spain, Serbia, United States, Australia, Netherlands, Austria, Germany, Israel, Lithuania, France, United Kingdom, Poland
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ReveraGen BioPharma, Inc.National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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ReveraGen BioPharma, Inc.National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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Medical University of GrazCompletedSkin Cancer | Basal Cell Nevus Syndrome | Xeroderma PigmentosumAustria
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Amicus TherapeuticsCompletedFabry DiseaseUnited States, Australia, France, United Kingdom, Brazil, Canada
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Novartis PharmaceuticalsCompletedAdvanced Solid Tumors With Alterations of FGFR1, 2 and or 3 | Squamous Lung Cancer With FGFR1 Amplification | Bladder Cancer With FGFR3 Mutation or Fusion | Advanced Solid Tumors With FGFR1 Amplication | Advanced Solid Tumors With FGFR2 Amplication | Advanced Solid Tumors With FGFR3 MutationFrance, Spain, Taiwan, Germany, Netherlands, Singapore, United States, Australia, Korea, Republic of, Thailand, Israel, Italy, Turkey, Austria
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SanofiRegeneron PharmaceuticalsCompletedAtopic DermatitisFrance, United States, Australia, Germany, Israel, Italy, Spain, Switzerland, United Arab Emirates, United Kingdom
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Indiana University School of MedicineNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health...CompletedCystic FibrosisUnited States, Australia
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PfizerActive, not recruitingHemophilia BUnited States, Canada, Australia, Turkey
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Vertex Pharmaceuticals IncorporatedCompleted
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Sciotec Diagnostic Technologies GmbHAustrian Research Promotion AgencyCompletedFructose MalabsorptionAustria
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CelgeneCompletedMyelodysplastic Syndromes | Beta-thalassemiaAustria
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PfizerActive, not recruitingHemophilia BGermany, United Kingdom, Canada, Australia, Taiwan, Japan, France, Turkey, Korea, Republic of, United States, Brazil, Greece, Saudi Arabia, Sweden
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OctapharmaCompletedPrimary ImmunodeficiencyUnited Kingdom, Australia, Germany, Italy
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Vertex Pharmaceuticals IncorporatedRecruitingMyotonic Dystrophy Type 1 (DM1)United Kingdom, Canada, Australia
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Loxo Oncology, Inc.Eli Lilly and CompanyAvailableBreast Cancer | Pancreatic Cancer | Non Small Cell Lung Cancer | Colon Cancer | Medullary Thyroid Cancer | Papillary Thyroid Cancer | Other Solid Tumors With Evidence of Activating RET AlterationSpain, United States, Australia, France, Germany, Israel, Italy, Japan, New Zealand, Poland, Singapore, Switzerland
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Medical University InnsbruckUnknownFamilial Hypobetalipoproteinaemia - Heterozygous Form | Low-LDL-syndromeAustria
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Zynerba Pharmaceuticals, Inc.RecruitingFragile X SyndromeUnited States, Australia, United Kingdom, Ireland
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FerroKin BioSciences, Inc.CompletedBeta-thalassemia | Transfusional Iron OverloadUnited States, Australia, Thailand
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CSL BehringCompletedHemophilia BUnited States, Australia, Japan, France, Philippines, Spain, Czechia, Israel, Canada, Germany, Austria, Bulgaria, Italy, Malaysia, South Africa
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Gilead SciencesTerminatedCystic FibrosisFrance, Germany, Spain, United Kingdom, Australia
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Vertex Pharmaceuticals IncorporatedRecruitingCystic FibrosisUnited Kingdom, Canada, Australia
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Amryt Research LimitedCompletedEpidermolysis BullosaUnited States, Spain, Israel, Australia, France, Denmark, Switzerland, Italy, Hong Kong, Argentina, Austria, Brazil, Chile, Colombia, Czechia, Georgia, Germany, Greece, Hungary, Ireland, Romania, Russian Federation, Serbia, Singapore, U... and more
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Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumCompletedSevere Hemophilia BSweden, United States, France, Italy, Russian Federation, United Kingdom, Germany, China, Poland, Japan, Australia, Brazil, Canada, India, South Africa, Hong Kong, Belgium
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AVROBIOTerminatedFabry DiseaseUnited States, Australia, Brazil
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Amicus TherapeuticsTerminatedFabry DiseaseUnited Kingdom, United States, Australia, Brazil, France
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Ionis Pharmaceuticals, Inc.TerminatedBeta Thalassemia IntermediaAustralia, Thailand, Greece, Lebanon, Turkey
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ApcinteX LtdCentessa Pharmaceuticals plcRecruitingHemophilia B | Hemophilia B With InhibitorUnited States, Spain, Australia, Taiwan, France, Armenia, Germany
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Medical University of ViennaCompleted
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GlaxoSmithKlineCompletedMuscular DystrophiesGermany, Belgium, Turkey, Netherlands, Spain, Israel, Australia, France, United Kingdom
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PharmaxisCompletedCystic FibrosisIreland, United Kingdom, Australia
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Medical University InnsbruckUnknownCardiovascular Diseases | Diabetes Mellitus | Familial Renal GlucosuriaAustria
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Medical University of ViennaEnrolling by invitationGlaucoma | Cataract | Meibomian Gland Dysfunction | Aniridia | Corneal Transplantation | Acanthamoeba Keratitis | Demodicosis | Conjunctival PathologiesAustria
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Medical University of ViennaUnknownCutaneous NeurofibromasAustria