Clinical Trials on Genetic Disease in China

Total 31698 results

Shenzhen Geno-Immune Medical Institute

Unknown

Gene Transfer for SCID-X1 Using a Self-inactivating Lentiviral Vector （TYF-IL-2Rg）

SCID, X Linked

China
Xiaofan Zhu

Available

Use Massive Parallel Sequencing and Exome Capture Technology to Sequence the Exome of Fanconi Anemia Children and Their Patents

Fanconi Anemia | Autosomal or Sex Linked Recessive Genetic Disease | Bone Marrow Hematopoiesis Failure, Multiple Congenital Abnormalities, and Susceptibility to Neoplastic Diseases. | Hematopoiesis Maintainance.

China
Southwest Hospital, China

Unknown

Clinical Study of Subretinal Transplantation of Human Embryo Stem Cell Derived Retinal Pigment Epitheliums in Treatment of Macular Degeneration Diseases

Macular Degeneration | Stargardt's Macular Dystrophy

China
Wenjie Zheng

Terminated

Golimumab for the Treatment of Refractory Behcet's Uveitis

Behcet Syndrome | Uveitis

China
Wenjie Zheng

Terminated

Tocilizumab for the Treatment of Refractory Behcet's Uveitis

Behcet Syndrome | Uveitis

China
Children's Hospital of Chongqing Medical University

Recruiting

Gene Therapy for X Linked Severe Combined Immunodeficiency

Gene Therapy

China
Peking Union Medical College Hospital

Not yet recruiting

Tocilizumab and Tofacitinib in the Treatment of Vascular Behçet's Syndrome

Aneurysm | Behcet Syndrome, Vascular Type

China
Tianjin Eye Hospital

Completed

The Characteristics of Backscattering With Depth in the Progression of Keratoconus

Elasticum, Incomplete Pseudoxanthoma

China
Sunshine Guojian Pharmaceutical (Shanghai) Co.,...

Completed

Evaluation of 611 in Chinese Adults With Moderate to Severe Atopic Dermatitis

Dermatitis, Atopic

China
West China Hospital

Active, not recruiting

Safety and Efficacy of a Single Subretinal Injection of JWK006 Gene Therapy in Subjects With Stargardt Disease(STGD1)

Stargardt Disease 1

China
Peking Union Medical College Hospital

Recruiting

Lenalidomide in the Treatment of Mucosal Behçet's Syndrome

Oral Ulcer

China
Guangzhou Women and Children's Medical Center
University of Birmingham

Recruiting

IVF Offspring Born in Guangzhou (IVF-BIG)

Genetics | Offspring, Adult | Neurodevelopment | Host and Microbiome | ART

China
Peking Union Medical College Hospital

Recruiting

Pathogenesis of Intestinal Behcet's Syndrome

Behcet's Syndrome, Intestinal Type

China
Eye & ENT Hospital of Fudan University
Fudan University

Recruiting

Pilot Study of AuTNA I

Retinitis Pigmentosa

China
Pfizer

Completed

A Natural History Study In Chinese Male Patients With Duchenne Muscular Dystrophy

Duchenne Muscular Dystrophy

China
Peking University Third Hospital

Recruiting

Safety and Tolerability Study of Gene Editing Drug ZVS203e in Participants With Retinitis Pigmentosa

Retinitis Pigmentosa

China
Qi Zhou
Beijing Tongren Hospital

Unknown

Safety and Efficacy of Subretinal Transplantation of Clinical Human Embryonic Stem Cell Derived Retinal Pigment Epitheliums in Treatment of Retinitis Pigmentosa

Retinitis Pigmentosa

China
Sunshine Guojian Pharmaceutical (Shanghai) Co.,...

Completed

Evaluation of 611 in Chinese Adult Patients With Moderate-to-Severe Atopic Dermatitis

Dermatitis, Atopic

China
Shanghai Vitalgen BioPharma Co., Ltd.

Not yet recruiting

Safety and Tolerability of VGR-R01 for Patients With Bietti Crystalline Dystrophy

Bietti Crystalline Dystrophy

China
Beijing Tongren Hospital

Recruiting

Safety and Tolerability of VGR-R01 in Patients With Bietti Crystalline Dystrophy

Bietti Crystalline Dystrophy

China
Zhongmou Therapeutics

Not yet recruiting

Safety and Efficacy Study of Novel Gene Therapy ZM-02 for Retinitis Pigmentosa Patients (ZM-02)

Retinitis Pigmentosa

China
Children's Hospital of Fudan University

Not yet recruiting

Evaluation of the Safety, Tolerability and Efficacy of a Gene Therapy Drug for the Treatment of Pediatric Fabry Disease

Fabry Disease

China
Beijing Tongren Hospital

Recruiting

Safety Study of rAAV2/8-hCYP4V2 in Patients With Bietti's Crystalline Dystrophy (BCD)

Bietti's Crystalline Dystrophy

China
Xinhua Hospital, Shanghai Jiao Tong University...

Recruiting

Efficacy and Safety of Empagliflozin in GSD-Ib Patients

Glycogen Storage Disease Type IB

China
Second Affiliated Hospital, School of Medicine,...

Recruiting

Research and Development of a New Technology for Detection of Abnormal Excretion of Intestinal Uric Acid Involved in the Incidence of Gout

Single Nucleotide Polymorphism | Hyperuricemia | Gout | Gut Microbiota | Uric Acid | Genetic Loci | Feces

China
Chinese Alliance Against Lung Cancer
LiSen Imprinting Diagnostic Inc.

Unknown

Role of Genomic Imprinting in Cancer Diagnosis

Cancer | Biomarker | Early Diagnosis | Genomic Imprinting

China
Sun Yat-sen University
Sun Yat-Sen Memorial Hospital of Sun Yat-Sen University; Zhujiang Hospital; Guangzhou...

Not yet recruiting

Clinical Trials of Continuous Oxygen Therapy Combined With Blue Light Deprivation in the Treatment of Retinitis Pigmentosa

Retinitis Pigmentosa

China
Cui Yimin

Unknown

Effect of Smoking Status and Genetic Risk Factors on Restenosis and Efficacy of Clopidogrel After de Novo Percutaneous Coronary Intervention

Coronary Heart Disease | Percutaneous Coronary Intervention | Restenosis | Clopidogrel | Smoking Status | Genetic Risk Factors

China
Second Affiliated Hospital, School of Medicine,...
The First Affiliated Hospital with Nanjing Medical University; The First People... and other collaborators

Recruiting

Study on the Correlation Between Intestinal Microecology and Allergic Diseases in Children

Asthma | Rhinitis, Allergic | Dermatitis, Atopic | Urticaria

China
Children's Hospital of Fudan University

Recruiting

Rapamycin Treatment for Activated Phosphoinositide 3-Kinase δ Syndrome

Activated PI3K-delta Syndrome | Immunodeficiency Primary

China
Peking University Third Hospital

Recruiting

Safety and Tolerability of ZVS101e in Patients With Bietti 's Crystalline Dystrophy

Bietti's Crystalline Dystrophy

China
Peking Union Medical College Hospital
Cancer Institute and Hospital, Chinese Academy of Medical Sciences; Air Force...

Unknown

Efficacy of Rapamycin (Sirolimus) in the Treatment of Peutz-Jeghers Syndrome

Peutz-Jeghers Syndrome

China
Fudan University

Completed

Study on the Brain Network of Angelman Syndrome

Angelman Syndrome

China
Xijing Hospital

Completed

Supramaximal Titrated Inhibition of RAAS in Dilated Cardiomyopathy

Dilated Cardiomyopathy

China
Wyeth is now a wholly owned subsidiary of Pfizer

Completed

Study Evaluating On-Demand Treatment With BeneFIX In Chinese Subjects

Hemophilia B

China
YiYang Zhu

Unknown

Comparison of Karyotyping, CMA and NIPT for Prenatal Diagnosing Chromosomal Anomalies

Prenatal Diagnosis

China
Innovent Biologics (Suzhou) Co. Ltd.

Completed

A Study of IBI311 in Subjects With Active Thyroid Eye Disease

Thyroid Eye Disease

China
First Affiliated Hospital Xi'an Jiaotong University

Active, not recruiting

The Value of Prenatal Ultrasound in Complicated Twin Pregnancy and Its Correlation With Chromosomal Anomalies

Complicated Twin Pregnancy

China
Essen Biotech

Not yet recruiting

Investigation Into the Use of BAH243 Lentiviral Vector for Gene Therapy in Treating Sickle Cell Disease (BAH243)

Sickle Cell Disease | Sickle-Cell Disease With Crisis

China
Frontera Therapeutics
Peking Union Medical College Hospital; Eye & ENT Hospital of Fudan University; Henan Provincial People's Hospital

Recruiting

Gene Therapy for Subjects With RPGR Mutation-associated X-linked Retinitis Pigmentosa

X-Linked Retinitis Pigmentosa

China
Peking University Third Hospital

Recruiting

Exploring the Value of 18F-AlF-FAPI PET/CT in Assessing the Activity of Thyroid Eye Disease

Thyroid Eye Disease

China
Bioray Laboratories
First Affiliated Hospital of Guangxi Medical University

Not yet recruiting

Clinical Study of BRL-101 in Severe SCD

Sickle Cell Disease

China
Harbour BioMed (Guangzhou) Co. Ltd.

Recruiting

A Study to Evaluate the Efficacy and Safety of HBM9161 on Moderate to Severe Thyroid Eye Disease

Thyroid Ophthalmopathy

China
Xiaoping Luo

Recruiting

Long-term Efficacy and Safety Evaluation of Growth Hormone in Children in China(CGLS)

Childhood Short Stature

China
Xiao-Lin Yin

Unknown

The Effective and Safety of Thalidomide in TI

Thalassemia

China
Xiao-Lin Yin

Unknown

The Effective and Safety of Thalidomide in NTDT

Thalassemia

China
Yanfang Li

Unknown

Therapeutic Effect of Colla Corii Asini on Improving Anemia and Hemoglobin Composition in Pregnant Women With Thalassemia

Thalassemia

China
Henan Provincial People's Hospital

Not yet recruiting

Study on Gene Evolution in Glioma Under Stress Therapy

Genetic Change

China
Bioray Laboratories
First Affiliated Hospital of Guangxi Medical University

Suspended

Safety and Efficacy Evaluation of γ-globin Reactivated Autologous Hematopoietic Stem Cells

Thalassemia Major

China
Ruijin Hospital

Unknown

A Prospective, Randomized Trial of Intravenous Pulse Versus Sequential Steroid Therapy for Patients With Graves' Orbitopathy

Graves' Ophthalmopathy

China

Clinical Trials on Genetic Disease in China

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