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Clinical Trials on Genetic Diseases, Inborn in Canada
Total 24907 results
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The Hospital for Sick ChildrenRecruitingGenetic Disease | Inherited DiseaseCanada
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The Hospital for Sick ChildrenTerminatedMetabolic Disease | Genetic Disorder | MalignancyCanada
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Holland Bloorview Kids Rehabilitation HospitalThe Hospital for Sick ChildrenEnrolling by invitationRare Diseases | Genetic Disease | KCNC1 Related DisorderCanada
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Eloxx Pharmaceuticals, Inc.TerminatedGenetic Disease | Cystinosis | Nonsense MutationCanada
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University of British ColumbiaCanadian Institutes of Health Research (CIHR); Saudi Arabian Cultural Bureau...Unknown
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Laval UniversityCompletedFamilial HypercholesterolemiaCanada
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University of TorontoUnknownCardiovascular Risk Factor | Cholesterol; LipidosisCanada
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University of AlbertaCanadian Institutes of Health Research (CIHR); Imperial College London; University... and other collaboratorsCompleted
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University of AlbertaTerminated
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Amsterdam Molecular TherapeuticsICON plcTerminatedHyperlipoproteinemia Type ICanada
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Laval UniversityAmgenCompleted
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Laval UniversityCompletedHomozygous Familial HypercholesterolemiaCanada
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedHypertriglyceridemia | Familial HypercholesterolemiaCanada
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Université de SherbrookeInstitut de Recherches Cliniques de MontrealRecruitingLipoprotein Lipase DeficiencyCanada
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Sir Mortimer B. Davis - Jewish General HospitalDanone Institute InternationalCompleted
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Aeglea BiotherapeuticsTerminatedArginase I Deficiency | HyperargininemiaCanada
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Université de MontréalGenzyme, a Sanofi CompanyCompleted
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University of British ColumbiaVitaflo International, LtdUnknown
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Daniel GaudetUltragenyx Pharmaceutical IncActive, not recruitingSafety and Effectiveness of Evinacumab for the Treatment of Homozygous Familial HypercholesterolemiaHomozygous Familial HypercholesterolemiaCanada
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Cerenis Therapeutics, SACompleted
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Alexion PharmaceuticalsCompletedHypophosphatasia (HPP)United States, Canada
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Alexion PharmaceuticalsCompletedHypophosphatasia (HPP)United States, Canada
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Akcea TherapeuticsIonis Pharmaceuticals, Inc.WithdrawnHomozygous Familial HypercholesterolemiaCanada
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University of British ColumbiaRare Disease Foundation, Vancouver, Canada; Saudi Arabian Cultural Bureau,...Completed
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Hamilton Health Sciences CorporationChildren's Hospital of Eastern Ontario; McMaster Children's Hospital; BioMarin...CompletedPhenylketonuria | HyperphenylalaninemiaCanada
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University of ManitobaCo-Investigator - Dr. Cheryl Rockman-GreenbergCompletedHypoglycemia | Glycogen Storage Disorder Type 1 | Cornstarch | GlycosadeCanada
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Laval UniversityCompleted
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University of SaskatchewanDairy Farmers of CanadaCompletedHyperlipemia, Carbohydrate InducibleCanada
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Amsterdam Molecular TherapeuticsThe Clinical Trial CompanyCompletedFamilial Lipoprotein Lipase DeficiencyCanada
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University of British ColumbiaTerminated
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McGill University Health Centre/Research Institute...Sanofi; Merck Sharp & Dohme LLC; Pfizer; Amgen; Aegerion Pharmaceuticals, Inc.; Valeant...RecruitingFamilial Hypercholesterolemia | Lipid DisorderCanada
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Amsterdam Molecular TherapeuticsInternational Antiviral Therapy Evaluation CenterUnknownFamilial Lipoprotein Lipase DeficiencyCanada
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University Health Network, TorontoUniversity of Colorado, Denver; Mayo Clinic; Icahn School of Medicine at Mount... and other collaboratorsRecruiting
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University of British ColumbiaRare Disease Foundation, Vancouver, CanadaCompleted
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, Canada
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Innovaderm Research Inc.CompletedDermatitis, AtopicCanada
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GlaxoSmithKlineCompleted
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The Hospital for Sick ChildrenBioMarin PharmaceuticalCompletedPhenylketonuria | Mild HyperphenylalaninemiaCanada
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Welichem Biotech Inc.Completed
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Amsterdam Molecular TherapeuticsThe Clinical Trial CompanyUnknown
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Children's Hospital of Eastern OntarioCompleted
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Laval UniversityCentre de Recherche de l'Institut Universitaire de Cardiologie et de Pneumologie... and other collaboratorsActive, not recruitingDiet Habit | Hypercholesterolemia, Familial | Calcification; HeartCanada
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ShireTerminated
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McGill University Health Centre/Research Institute...March of DimesCompleted
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McMaster UniversityAstraZenecaCompletedSkin Diseases | Immune System Diseases | Hypersensitivity | Hypersensitivity, Immediate | Genetic Diseases, Inborn | Skin Diseases, Genetic | Dermatitis | Eczema | Skin Diseases, Eczematous | Dermatitis, AtopicCanada
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Resverlogix CorpWithdrawn
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Laval UniversityUniversité de Montréal; Centre de Recheche du Centre Hospitalier Université...RecruitingCardiovascular Diseases | Familial Hypercholesterolemia | Cholesterol, Elevated | Nutrition, Healthy | Cholesterol; Metabolic DisorderCanada
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M.A.G.I.C. Clinic LTDHanalytics Solutions Inc.RecruitingMitochondrial Diseases | Fabry Disease | Metabolic Disease | Gaucher Disease | Pompe DiseaseCanada
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The Hospital for Sick ChildrenCompletedEpidermolysis BullosaCanada