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Clinical Trials on Genetic Diseases, Inborn in Canada
Total 25021 results
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University of British ColumbiaHuntington Study Group; Huntington Society of CanadaCompletedHuntington DiseaseCanada
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ReveraGen BioPharma, Inc.University of Pittsburgh; Cooperative International Neuromuscular Research...CompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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Reistone Biopharma Company LimitedCompletedAtopic DermatitisChina, Canada
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AmgenCompletedFamilial HypercholesterolemiaCanada, Italy, Norway, Belgium, United States, Turkey, Australia, Austria, South Africa, Poland, Switzerland, Spain, Portugal, Slovenia, Brazil, Russian Federation, Hungary, United Kingdom, Colombia, Czechia, Netherlands, Greece, Ma...
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Vertex Pharmaceuticals IncorporatedCRISPR TherapeuticsRecruitingHematologic Diseases | Genetic Diseases, Inborn | Hemoglobinopathies | Thalassemia | Beta-ThalassemiaUnited States, Germany, Italy, United Kingdom, Canada
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease | Glycogenesis 2 Acid Maltase DeficiencyUnited States, Canada, Australia
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Virginia Commonwealth UniversityUniversity of Western Ontario, Canada, Children's Health Research Institute; Fondazione Serena Onlus - Centro Clinico NeMO MilanoRecruitingCongenital Myotonic DystrophyUnited States, Italy, Canada
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University of AlbertaCompleted
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ShireCompletedHunter SyndromeSpain, United States, Canada, United Kingdom, France, Australia, Mexico
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Merck Sharp & Dohme LLCActive, not recruitingHypercholesterolemia | Familial HypercholesterolemiaUnited States, Australia, Brazil, Canada, Chile, Colombia, Czechia, Finland, Hong Kong, Hungary, Israel, Netherlands, New Zealand, Norway, Singapore, Spain, Taiwan
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SanofiRegeneron PharmaceuticalsCompletedHypercholesterolemiaUnited States, Austria, Canada, Czech Republic, Denmark, France, Israel, Netherlands, Norway, Russian Federation, South Africa, Spain, Sweden, United Kingdom
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ReveraGen BioPharma, Inc.National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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ReveraGen BioPharma, Inc.National Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS) and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States, Canada, United Kingdom, Sweden, Australia, Israel
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CymaBay Therapeutics, Inc.CompletedGoutUnited States, Canada, Georgia
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CF Therapeutics Development Network Coordinating...Cystic Fibrosis FoundationCompletedCystic FibrosisCanada, United States
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Janssen Research & Development, LLCTerminatedDermatitis, AtopicUnited States, Germany, Canada, Poland, Japan
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Passage Bio, Inc.Active, not recruitingGM1 Gangliosidosis | GM1 Gangliosidosis, Type I | GM1 Gangliosidosis, Type 2 | Beta-Galactosidase-1 (GLB1) DeficiencyUnited States, Canada, United Kingdom, Turkey, Brazil
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Children's Hospital Medical Center, CincinnatiThe Hospital for Sick Children; University of Wisconsin, Madison; University...Active, not recruiting
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LEO PharmaCompletedAtopic DermatitisUnited States, Canada, Australia
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AmgenRecruitingAtopic DermatitisUnited States, Canada
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PfizerAvailableAtopic DermatitisTaiwan, United States, Australia, Austria, Belgium, Canada, Greece, Mexico, Netherlands, Russian Federation, Spain, Switzerland
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PfizerActive, not recruitingHemophilia BUnited States, Canada, Australia, Turkey
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Robert NickelThe Hospital for Sick Children; Ann & Robert H Lurie Children's Hospital of... and other collaboratorsRecruitingSickle Cell DiseaseUnited States, Canada
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University of British ColumbiaHeart and Stroke Foundation of CanadaCompleted
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Novartis PharmaceuticalsCompletedAcute GoutColombia, Switzerland, Germany, Russian Federation, Singapore, Australia, Belgium, Canada, Estonia, Guatemala, Latvia, Lithuania, Mexico, Norway, Poland, Sweden, Ukraine
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SanofiCompletedAtopic DermatitisNetherlands, Chile, United States, Canada, Czechia, Germany, Poland
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MeiraGTx UK II LtdJanssen, LPActive, not recruitingRetinitis PigmentosaUnited States, United Kingdom, Canada
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Arrowhead PharmaceuticalsWithdrawnAlpha-1 Antitrypsin DeficiencyIreland, Canada, Italy, Sweden
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Children's Hospital of Eastern OntarioCompleted
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SanofiRecruitingDermatitis AtopicChile, United Kingdom, United States, Canada, Turkey, Israel, Korea, Republic of
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SanofiRecruiting
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ItalfarmacoRecruitingDuchenne Muscular DystrophyCanada, Italy, France, Belgium, Germany, Netherlands, United Kingdom
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Vertex Pharmaceuticals IncorporatedRecruitingCystic FibrosisUnited Kingdom, Canada, Australia
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The Hospital for Sick ChildrenCompletedAsthma | Cystic Fibrosis | Heart DiseaseCanada
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Chiesi Farmaceutici S.p.A.Active, not recruitingFabry DiseaseUnited States, Netherlands, Australia, Hungary, United Kingdom, Canada, Czechia, Finland, France, Italy, Norway, Slovenia, Spain
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Ralexar Therapeutics, Inc.Unknown
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Phoenicia BioScienceNational Heart, Lung, and Blood Institute (NHLBI)RecruitingSickle Cell Disease | Beta Thalassemia IntermediaUnited States, Canada
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Ardea Biosciences, Inc.CompletedGoutUnited States, Canada, Belgium, Australia, Germany, New Zealand, South Africa
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Genzyme, a Sanofi CompanyCompletedGaucher Disease, Type 1United States, France, Germany, Italy, Brazil, Australia, Argentina, Canada, Egypt, Russian Federation, Spain, United Kingdom
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BioMarin PharmaceuticalTerminatedLate-onset Pompe Patients Untreated or Treated With rhGAASpain, Slovenia, Serbia, Korea, Republic of, Greece, Australia, Singapore, Brazil, Canada, Taiwan, Ireland, Poland, Romania
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Abfero Pharmaceuticals, IncWithdrawnIron Overload | Beta-ThalassemiaThailand, Lebanon, Turkey, Canada
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ASLAN PharmaceuticalsRecruitingAtopic DermatitisUnited States, Canada
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Kyowa Kirin, Inc.Kyowa Kirin Co., Ltd.CompletedAtopic DermatitisUnited States, Canada, Germany, Japan
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Ultragenyx Pharmaceutical IncCompletedOsteogenesis ImperfectaBelgium, United States, Canada, Germany
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Ardea Biosciences, Inc.CompletedGoutUnited States, Canada, Australia, New Zealand, Switzerland, Poland
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Agios Pharmaceuticals, Inc.RecruitingPediatric Pyruvate Kinase Deficiency | Pediatric Hemolytic AnemiaUnited States, Spain, Germany, Netherlands, Canada, France, Israel, Switzerland, Italy
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Agios Pharmaceuticals, Inc.Active, not recruitingPediatric Pyruvate Kinase Deficiency | Pediatric Hemolytic AnemiaUnited States, Spain, Denmark, Turkey, Netherlands, Czechia, United Kingdom, Germany, Canada, Switzerland
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseUnited States, Sweden, India, Netherlands, Austria, Japan, China, Serbia, France, Croatia, Australia, Portugal, Canada, Brazil, Greece, Romania, Russian Federation
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Bausch Health Americas, Inc.CompletedSickle Cell DiseaseUnited States, Canada, Kenya