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Clinical Trials on Genetic Diseases, Inborn in China
Total 31698 results
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Merz North America, Inc.Ulthera, IncCompletedImprovement in Skin Laxity of the Lower Face and SubmentumChina
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Second Affiliated Hospital, School of Medicine,...CompletedWilson Disease | Generalized EpilepsyChina
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Third Affiliated Hospital, Sun Yat-Sen UniversityUnknownLiver Failure | Wilson DiseaseChina
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Mylan Inc.Medicine Meda Pharmaceutical Information Consultancy (Beijing) Co., Ltd.Completed
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Shanghai Children's Medical CenterUnknown
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Shenzhen Beike Bio-Technology Co., Ltd.The Second Affiliated Hospital of Kunming Medical UniversityUnknownDuchenne Muscular DystrophyChina
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Hospital Affiliated to the Institute of Neurology...Not yet recruitingHepatolenticular Degeneration; WilsonChina
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Sunshine Guojian Pharmaceutical (Shanghai) Co.,...CompletedDermatitis, AtopicChina
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Children's Hospital of Fudan UniversityRecruiting
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Shenzhen Geno-Immune Medical InstituteUnknown
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Children's Hospital of Fudan UniversityTerminated
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YiYang ZhuUnknownPrenatal DiagnosisChina
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General Hospital of Chinese Armed Police ForcesUnknownDuchenne Muscular Dystrophy (DMD)China
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Peking Union Medical College HospitalUnknownX-linked HypophosphatemiaChina
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Southern Medical University, ChinaUnknownNeonatal HyperbilirubinemiaChina
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First Affiliated Hospital Xi'an Jiaotong UniversityActive, not recruitingComplicated Twin PregnancyChina
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Qianfoshan HospitalRecruitingIron Deficiency Anemia of Pregnancy | Iron Storage DiseaseChina
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Shenzhen Geno-Immune Medical InstituteUnknown
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Peking University Third HospitalRecruitingBietti's Crystalline DystrophyChina
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Peking Union Medical CollegeSuspended
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Xiaofan ZhuAvailableFanconi Anemia | Autosomal or Sex Linked Recessive Genetic Disease | Bone Marrow Hematopoiesis Failure, Multiple Congenital Abnormalities, and Susceptibility to Neoplastic Diseases. | Hematopoiesis Maintainance.China
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Shenzhen Geno-Immune Medical InstituteUnknown
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Xijing HospitalCompleted
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Frontera TherapeuticsPeking Union Medical College Hospital; Eye & ENT Hospital of Fudan University; Henan Provincial People's HospitalRecruitingX-Linked Retinitis PigmentosaChina
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Suzhou Alphamab Co., Ltd.RecruitingHemophilia A With Inhibitor | Hemophilia B With InhibitorChina
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Chia Tai Tianqing Pharmaceutical Group Co., Ltd.UnknownHemophilia A With Inhibitor | Hemophilia B With InhibitorChina
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Yanfang LiUnknown
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Shenzhen Geno-Immune Medical InstituteUnknownSCID, X LinkedChina
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Guangdong Provincial Hospital of Traditional Chinese...RecruitingAcute Pain | Acupuncture | Acute Gout ArthritisChina
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Xiaoping LuoRecruitingChildhood Short StatureChina
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Children's Hospital of Fudan UniversityRecruiting
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Hangzhou Zede Pharma-Tech Co., Ltd.Completed
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Hangzhou Zede Pharma-Tech Co., Ltd.Completed
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Shanghai Jiao Tong University School of MedicineNot yet recruitingCongenital Adrenal HyperplasiaChina
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Children's Hospital of Fudan UniversityRecruitingBCG | Vitamin D3 | Chronic-granulomatous DiseaseChina
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PfizerCompletedDuchenne Muscular DystrophyChina
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TakedaActive, not recruiting
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The First Affiliated Hospital, Guangzhou University...National Natural Science Foundation of ChinaUnknownPregnancy | ThalassemiaChina
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Shenzhen Second People's HospitalGuangzhou Women and Children's Medical Center; Shenzhen UniversityRecruitingAdrenoleukodystrophy | Metachromatic LeukodystrophyChina
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Children's Hospital of Fudan UniversityRecruitingActivated PI3K-delta Syndrome | Immunodeficiency PrimaryChina
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Wuhan Union Hospital, ChinaUnknownDilated CardiomyopathyChina
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Peking Union Medical College HospitalNational Natural Science Foundation of China; Cancer Institute and Hospital...Recruiting
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Bioray LaboratoriesFirst Affiliated Hospital of Guangxi Medical UniversitySuspendedThalassemia MajorChina
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Chigenovo Co., LtdRecruitingBietti's Crystalline DystrophyChina
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Bioray LaboratoriesFirst Affiliated Hospital of Guangxi Medical UniversityNot yet recruiting
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ShireQuintiles, Inc.Completed