Clinical Trials on Genetic Diseases, Inborn in United Kingdom
Total 146858 results
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University of DundeeNHS TaysideCompletedAtopic EczemaUnited Kingdom
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Ultragenyx Pharmaceutical IncCompleted
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Nottingham University Hospitals NHS TrustKing's College Hospital NHS Trust; The Leeds Teaching Hospitals NHS Trust; Manchester... and other collaboratorsRecruitingRespiratory Tract Diseases | Lung Diseases | Cystic Fibrosis | Genetic Disease | Digestive System Disease | Pancreatic DiseaseUnited Kingdom
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Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation TrustRecruiting
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Keele UniversityCompleted
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Atopix Therapeutics, Ltd.Completed
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University College, LondonTerminated
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University of ManchesterManchester University NHS Foundation Trust; Great Ormond Street Hospital for... and other collaboratorsRecruiting
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University College, LondonDermatrustWithdrawn
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GlaxoSmithKlineCompleted
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HemoShear TherapeuticsPrometrika, LLC; AllStripes Research Inc.; Genome MedicalTerminatedPropionic Acidemia | Methylmalonic AcidemiaUnited States, Canada, United Kingdom
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University of ManchesterUniversity College, London; Manchester University NHS Foundation Trust; Orchard... and other collaboratorsActive, not recruitingMucopolysaccharidosis Type IIIAUnited Kingdom
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University College, LondonUnknown
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LEO PharmaCompleted
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Arcturus Therapeutics, Inc.RecruitingOTC Deficiency | Ornithine Transcarbamylase Deficiency | OTCDSpain, Belgium, United Kingdom, Sweden
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AnaMar ABCovanceCompletedAtopic DermatitisUnited Kingdom
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Momentum DataPfizer; Royal College of General Practitioners Research and Surveillance CentreUnknownEczema | Atopic Dermatitis | Atopic Dermatitis EczemaUnited Kingdom
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Guy's and St Thomas' NHS Foundation TrustKing's College London; National Institute for Health Research, United KingdomCompletedChild | Atopic Dermatitis | Atopic EczemaUnited Kingdom
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Alexion PharmaceuticalsTerminatedMucopolysaccharidosis III, Type B (MPS IIIB) | Sanfilippo BUnited Kingdom
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Alexion PharmaceuticalsCompletedMPS IIIB (Sanfilippo B Syndrome)United Kingdom
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REGENXBIO Inc.Active, not recruitingNeuronal Ceroid Lipofuscinosis Type 2United Kingdom
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Imperial College LondonJP Moulton Charitable FoundationRecruitingAtopic Dermatitis EczemaUnited Kingdom
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ACO Hud Nordic ABThe University of Sheffield Medical SchoolCompletedDermatitis, AtopicUnited Kingdom
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OrphalanCompletedWilson's DiseaseUnited Kingdom
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University College, LondonUniversity of Sydney; University Hospital BirminghamUnknownFabry DiseaseUnited Kingdom, Australia
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Alexion Pharmaceuticals, Inc.CompletedWilson DiseaseUnited Kingdom
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Sheffield Teaching Hospitals NHS Foundation TrustUniversity of SheffieldActive, not recruiting
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Canada, United Kingdom
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Astellas Pharma Europe B.V.CompletedDermatitis, AtopicUnited Kingdom
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Zymenex A/SEuropean CommissionCompletedAlpha-MannosidosisBelgium, Denmark, Spain, United Kingdom
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Amicus TherapeuticsTerminatedType 1 Gaucher DiseaseUnited States, United Kingdom
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LEO PharmaCompletedAtopic DermatitisUnited Kingdom
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Ziarco Pharma LtdCompletedAtopic DermatitisUnited Kingdom
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University of OxfordUniversity College, London; University of Southampton; Moorfields Eye Hospital... and other collaboratorsCompleted
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University College, LondonMedical Research Council; Moorfields Eye Hospital NHS Foundation TrustRecruiting
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Vitaflo International, LtdArla FoodsCompletedPhenylketonuriasUnited Kingdom, Denmark
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Vitaflo International, LtdBirmingham Women's and Children's NHS Foundation TrustCompletedPhenylketonuria | Inborn Errors of MetabolismUnited Kingdom
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Imperial College LondonSarepta Therapeutics, Inc.; Department of Health, United KingdomCompletedDuchenne Muscular DystrophyUnited Kingdom
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BioMarin PharmaceuticalTerminatedLate-onset Pompe DiseaseUnited States, United Kingdom
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Vitaflo International, LtdCompleted
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BioMarin PharmaceuticalCompleted
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ShireCompletedMucopolysaccharidosis (MPS)United Kingdom, Netherlands
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University Hospitals, LeicesterCompletedUlcerative Colitis | Lactose IntoleranceUnited Kingdom
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Recordati Rare DiseasesCompletedCystinosisBelgium, France, United Kingdom, Germany, Italy
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Great Ormond Street Hospital for Children NHS Foundation...Unknown
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National Institute of Neurological Disorders and...CompletedGaucher DiseaseUnited States, United Kingdom
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Origin BiosciencesCompletedMolybdenum Cofactor Deficiency, Type AUnited States, Australia, Netherlands, United Kingdom, Tunisia
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Birmingham Women's and Children's NHS Foundation...BioMarin PharmaceuticalWithdrawnMucopolysaccharidosis IV | Morquio A DiseaseUnited Kingdom
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University of West LondonCompletedVitamin B12 DeficiencyUnited Kingdom
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PTC TherapeuticsGenzyme, a Sanofi CompanyTerminatedAmino Acid Metabolism, Inborn ErrorsFrance, United Kingdom, Italy, Belgium, Germany, Switzerland