Clinical Trials on Genetic Diseases, X-Linked in Australia
Total 967 results
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, Canada, United Kingdom, Australia, Ireland
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Gilead SciencesCompletedCystic Fibrosis | Pseudomonas Aeruginosa | Lung InfectionUnited States, Australia, Canada
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ModernaTX, Inc.RecruitingPropionic AcidemiaUnited States, Spain, Netherlands, France, United Kingdom, Australia, Canada, Italy
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Ultragenyx Pharmaceutical IncActive, not recruitingAngelman SyndromeUnited States, United Kingdom, Canada, Australia, France, Germany, Spain, Israel
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Vertex Pharmaceuticals IncorporatedActive, not recruitingCystic FibrosisUnited States, United Kingdom, Canada, Australia, Germany
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Novartis PharmaceuticalsCompletedNevoid Basal Cell Carcinoma Syndrome | Basal Cell Carcinoma | Gorlin SyndromeBelgium, Austria, Germany, Canada
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PTC TherapeuticsRecruitingPhenylketonuriaUnited States, Germany, Spain, Australia, Brazil, United Kingdom, Denmark, Mexico, Portugal, Turkey, Canada, Georgia, Italy, Netherlands, Japan
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AmgenActive, not recruitingAtopic DermatitisUnited States, Spain, United Kingdom, Korea, Republic of, Australia, Denmark, Germany, Belgium, Canada, Japan, Sweden, Poland, Romania, Estonia, Brazil, Czechia, Portugal, Finland, Mexico, Turkey, South Africa
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Novo Nordisk A/SCompletedCongenital Bleeding Disorder | Haemophilia AUnited States, Netherlands, Austria, Spain, Poland, United Kingdom, Croatia, Germany, Malaysia, Australia, France, Israel, Thailand, Ukraine, Turkey
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Boehringer IngelheimCompletedCystic FibrosisUnited States, Australia, Belgium, France, Germany, Italy, Netherlands, New Zealand, Portugal, Russian Federation, United Kingdom
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Friedreich's Ataxia Research AllianceChildren's Hospital of Philadelphia; University of RochesterRecruitingFriedreich Ataxia | Neuro-Degenerative DiseaseUnited States, Canada, New Zealand, Australia, India
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Baxalta now part of ShireBaxalta Innovations GmbH, now part of ShireCompletedHemophilia ASpain, United States, Australia, Singapore, Taiwan, Hong Kong, Malaysia, Bulgaria, United Kingdom, Switzerland, Ukraine, Turkey, Italy, Norway, France, Austria, Romania, Sweden, Poland, Germany, Hungary, Israel
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CSL BehringCompletedHemophilia AUnited States, Australia, Austria, Canada, Czech Republic, Germany, Hungary, Italy, Japan, Lebanon, Malaysia, Netherlands, Philippines, Poland, Romania, Russian Federation, South Africa, Spain, Ukraine, United Kingdom
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AmgenRecruitingAtopic DermatitisUnited States, Japan, Korea, Republic of, Australia, Taiwan, Spain, Switzerland, Germany, Croatia, Austria, Bulgaria, France, Denmark, China, Netherlands, Hungary, Czechia, Poland, Brazil, Greece, Portugal, Italy, Finland, Argentina, Sl... and more
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BayerNovartisCompletedCystic FibrosisUnited States, Israel, Germany, Canada, Australia, Sweden, Denmark, Norway, United Kingdom
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Hoffmann-La RocheRecruitingHuntington DiseaseUnited States, Australia, Argentina, Canada, Germany, Italy, Spain, France, United Kingdom, Portugal, New Zealand, Austria, Poland, Switzerland, Denmark
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University of Washington, the Collaborative Health...Cystic Fibrosis FoundationCompletedCystic FibrosisSpain, United States, Australia, Italy, France, Canada, Belgium, Denmark, Netherlands
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Amicus TherapeuticsActive, not recruitingPompe Disease (Late-onset)United States, Germany, Taiwan, Belgium, Australia, Slovenia, Spain, Netherlands, Hungary, Japan, Austria, United Kingdom, France, Argentina, Canada, Sweden, Denmark, New Zealand, Greece, Korea, Republic of, Bosnia and Herzegovina, Ita... and more
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PTC TherapeuticsEnrolling by invitationFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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PTC TherapeuticsCompletedFriedreich AtaxiaUnited States, Australia, Brazil, Canada, France, Germany, Italy, New Zealand, Spain
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisUnited States, United Kingdom, Canada, Australia, Germany
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Genzyme, a Sanofi CompanyCompletedGlycogen Storage Disease Type II (GSD-II) | Pompe Disease | Glycogenesis 2 Acid Maltase DeficiencyUnited States, Canada, Australia
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Genzyme, a Sanofi CompanyCompletedGaucher DiseaseUnited States, Sweden, India, Netherlands, Austria, Japan, China, Serbia, France, Croatia, Australia, Portugal, Canada, Brazil, Greece, Romania, Russian Federation
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Baxalta now part of ShireBaxalta Innovations GmbH, now part of ShireTerminatedChronic Obstructive Pulmonary Disease | Alpha1-antitrypsin DeficiencyUnited States, Canada, Australia
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Santhera PharmaceuticalsCompletedFriedreich's AtaxiaNetherlands, Austria, United Kingdom, Belgium, France, Germany
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La Jolla Pharmaceutical CompanyTerminatedBeta-ThalassemiaAustralia, Thailand, United States, Greece, Italy, Lebanon, Turkey, United Kingdom
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AmgenCompletedOsteogenesis ImperfectaSpain, United States, Turkey, Austria, Germany, Greece, Hungary, Italy
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LEO PharmaTerminatedAtopic DermatitisUnited States, Netherlands, United Kingdom, France, Canada, Ireland, Austria, Germany, Poland
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisCanada, France, Germany, United Kingdom, Israel, Australia, Spain, Netherlands, Denmark, Switzerland
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Baxalta now part of ShireBaxalta Innovations GmbH, now part of ShireCompletedHemophilia ACzechia, Switzerland, Denmark, Canada, Australia, Austria, France, United Kingdom, Italy, Sweden, Belgium, Brazil, China, Colombia, Greece, Hungary, Norway, Poland, Portugal, Russian Federation, Slovenia, Spain
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OctapharmaCompletedSevere Haemophilia AAustria, United Kingdom, Bulgaria, Hungary, Germany, Poland, Romania, Slovakia
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BioMarin PharmaceuticalICON plcCompletedMucopolysaccharidosis IV Type A | Morquio A Syndrome | MPS IVAUnited States, United Kingdom, Australia, Taiwan, Belgium, Malaysia, Austria, Canada, Portugal, France, Ireland, Czechia, Denmark, Italy, Netherlands, Poland, Puerto Rico
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisCanada, France, United Kingdom, Israel, Australia, Spain, Germany, Netherlands, Denmark, Switzerland
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AlexionTerminatedWilson DiseaseUnited States, France, Germany, Spain, Canada, Singapore, Poland, Denmark, Hungary, Australia, Austria, Czechia, Hong Kong, Israel, Japan, Korea, Republic of, New Zealand, Russian Federation, Serbia, Taiwan, Turkey, United Kingdom
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Bioverativ Therapeutics Inc.Swedish Orphan BiovitrumCompletedHemophilia AUnited States, Poland, United Kingdom, Netherlands, South Africa, Hong Kong, Australia, Ireland
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Sage TherapeuticsRecruitingHuntington's DiseaseUnited States, Australia, Canada, United Kingdom
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Alexion Pharmaceuticals, Inc.RecruitingHypophosphatasiaItaly, Spain, Israel, Korea, Republic of, Belgium, Germany, United States, China, France, Taiwan, Austria, Japan, India, Australia, Argentina, Poland, Turkey, Brazil, Canada, Thailand, United Kingdom, Slovakia, Czechia
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Genzyme, a Sanofi CompanyCompletedHemophiliaUnited States, Australia, China, Denmark, France, Ireland, Israel, Italy, Japan, Korea, Republic of, Malaysia, Turkey, Ukraine, United Kingdom, Mexico
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CSL BehringCompletedHereditary AngioedemaCanada, Australia, Germany, United States, Israel
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Vertex Pharmaceuticals IncorporatedCompletedCystic FibrosisFrance, Spain, Belgium, Netherlands, Australia, Italy, Czechia
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Merck Sharp & Dohme LLCCompletedCystic FibrosisUnited States, Australia, Canada, New Zealand
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Dr. Rebecca SchuleGerman Federal Ministry of Education and Research; German Center for Neurodegenerative...RecruitingHereditary Spastic ParaplegiaAustria, Germany, Italy
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PrileniaTerminatedHuntington's DiseaseUnited States, Australia, Austria, Canada, France, Germany, Italy, Netherlands, Poland, Russian Federation, United Kingdom
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CHDI Foundation, Inc.Monash UniversityCompletedHuntington's DiseaseUnited States, Australia, United Kingdom, Canada
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Alnylam PharmaceuticalsCompletedAcute Hepatic Porphyria | Acute Intermittent Porphyria | Porphyria, Acute Intermittent | Acute Porphyria | Hereditary Coproporphyria (HCP) | Variegate Porphyria (VP) | ALA Dehydratase Deficient Porphyria (ADP)United States, Spain, United Kingdom, Korea, Republic of, Australia, Bulgaria, Canada, Denmark, Finland, France, Germany, Italy, Japan, Mexico, Netherlands, Poland, Sweden, Taiwan
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Wave Life Sciences Ltd.RecruitingHuntington DiseaseCanada, Spain, Australia, Denmark, Netherlands, Poland, United Kingdom, France, Germany, Italy
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PTC TherapeuticsCompletedPhenylketonuriaSpain, United States, Australia, Germany, United Kingdom, Brazil, Denmark, Canada, France, Georgia, Italy, Mexico, Netherlands, Portugal, Turkey
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Vertex Pharmaceuticals IncorporatedModerna, IncRecruitingCystic FibrosisUnited States, United Kingdom, Australia, Canada
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BayerTerminatedHemophilia ABelgium, Italy, Spain, United States, Canada, Switzerland, Estonia, Taiwan, France, Chile, Netherlands, United Kingdom, Austria, New Zealand, South Africa, Romania, Croatia, Israel, Germany, Poland, Australia, Denmark, Turkey, Argentina, Lithuan... and more