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Clinical Trials on Genetic Diseases, X-Linked in Ireland
Total 396 results
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University College CorkAssistance Publique - Hôpitaux de Paris; KU Leuven; University of Washington; Queen... and other collaboratorsCompleted
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Children's University Hospital, IrelandUniversity College Dublin; Health Research Board, Ireland; Medical Research Charities...Completed
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St. James's Hospital, IrelandBaxter BioScienceUnknownSevere Haemophilia AIreland
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Queen's University, BelfastUniversity of SussexUnknownRetinitis Pigmentosa | Low Vision | Albinism | Stargardt Disease 1 | Stargardt Disease 3 | Stargardt Disease 4United Kingdom
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QLT Inc.CompletedRetinitis Pigmentosa (RP)Canada, Ireland
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Women and Infants Hospital of Rhode IslandNatera, Inc.CompletedTrisomy 21 | Trisomy 18 | Trisomy 13 | Monosomy XUnited States
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Astellas Pharma IncCompletedDermatitis, AtopicUnited Kingdom, Finland, Ireland, Canada, Latvia
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Astellas Pharma IncCompletedDermatitis, AtopicUnited Kingdom, Finland, Ireland, Canada, Latvia
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Pulmatrix Inc.CelerionCompletedCystic FibrosisUnited Kingdom
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VA Office of Research and DevelopmentNot yet recruitingAmyotrophic Lateral Sclerosis | Muscular Dystrophy | Spinal Cord Injury | Brain Stem Infarctions | Locked-in SyndromeUnited States
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University of UlsterDSM Nutritional Products, Inc.UnknownParticipants With the MTHFR 677TT GenotypeUnited Kingdom
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Children's Health IrelandQueen's University, Belfast; Cystic Fibrosis Foundation; European Cystic Fibrosis...Active, not recruiting
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AlgiPharma ASCompletedCystic FibrosisUnited Kingdom, Ireland
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Leigh R. Hochberg, MD, PhD.National Institute of Neurological Disorders and Stroke (NINDS); US Department... and other collaboratorsRecruitingAmyotrophic Lateral Sclerosis | Muscular Dystrophy | Spinal Cord Injuries | Tetraplegia | Brain Stem Infarctions | Locked in SyndromeUnited States
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American Thrombosis and Hemostasis NetworkSanofi; Pfizer; Genentech, Inc.; CSL Behring; Hemophilia of Georgia, Inc.; Hemab TherapeuticsRecruitingHemophilia | Thrombosis | Thrombophilia | Sickle Cell Disease | Thalassemia | Bleeding Disorder | Von Willebrand Diseases | Factor IX Deficiency | Connective Tissue Disorder | Factor VIII Deficiency | Hematologic Disorder | Rare Bleeding Disorder | Platelet DisorderUnited States
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Novartis PharmaceuticalsCompletedTNF-receptor Associated Periodic Syndromes (TRAPS)United Kingdom, Ireland, Italy
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Clinuvel Pharmaceuticals LimitedCompletedErythropoietic ProtoporphyriaNetherlands, Finland, France, Germany, Ireland, United Kingdom
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TESS Research FoundationBrown University; Stanford University; University of Texas Southwestern Medical...RecruitingEpilepsy | Movement Disorders | Rare Diseases | Genetic Disorder | Citrate Transporter Deficiency | SLC13A5 Deficiency | EIEE25 | Kohlschutter-Tonz Syndrome (Non-ROGDI) | Citrate Transporter Disorder | DEE25United States
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Celtaxsys, Inc.CelerionCompletedCystic FibrosisUnited Kingdom
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University College CorkNot yet recruitingGestational Diabetes | Neonatal Encephalopathy | Diastolic Dysfunction | Trisomy 21 | Transient Tachypnea of the Newborn | Small for Gestational Age at DeliveryIreland
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Arrowhead PharmaceuticalsWithdrawnAlpha-1 Antitrypsin DeficiencyIreland, Canada, Italy, Sweden
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Royal College of Surgeons, IrelandThe Hospital for Sick Children; Imperial College London; Erasmus Medical Center; University College Dublin and other collaboratorsActive, not recruitingCystic Fibrosis | Adherence, Medication | Cystic Fibrosis Gastrointestinal Disease | Cystic Fibrosis in Children | Cystic Fibrosis Liver DiseaseUnited Kingdom, Ireland
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Applied Genetic Technologies CorpNational Heart, Lung, and Blood Institute (NHLBI)CompletedAlpha-1 Antitrypsin DeficiencyUnited States, Ireland
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Children's Health IrelandBelfast Health and Social Care Trust; University of Edinburgh; University Hospital... and other collaboratorsRecruitingQuality of Life | Obstructive Sleep Apnea | Down Syndrome | Behavior | Adherence, TreatmentUnited Kingdom, Ireland
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Ionis Pharmaceuticals, Inc.CompletedCystic Fibrosis | Healthy SubjectsUnited Kingdom, Germany
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Fougera Pharmaceuticals Inc.CompletedPsoriasis | Atopic DermatitisUnited States
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Synspira, Inc.TerminatedLung Diseases | Cystic Fibrosis | Pulmonary Disease | Antibiotic Resistant Infection | Respiratory Tract Disease | Cystic Fibrosis Pulmonary Exacerbation | Lung Inflammation | Burkholderia Infections | Lung Infection | Multi-antibiotic Resistance | Pulmonary Inflammation | Lung Infection Pseudomonal | Cystic Fibrosis... and other conditionsUnited Kingdom
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PharmaxisCompletedCystic FibrosisIreland, United Kingdom, Australia
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AmgenActive, not recruiting
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Kamada, Ltd.Syneos HealthRecruitingAlpha 1-Antitrypsin DeficiencyUnited Kingdom, Sweden, Ireland, Netherlands, Belgium, Finland
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Nationwide Children's HospitalNational Heart, Lung, and Blood Institute (NHLBI); National Institutes of Health... and other collaboratorsNot yet recruitingSickle Cell DiseaseUnited States
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GenEmbryomics Pty. LtdRecruitingFertility Issues | Single-Gene DefectsUnited States, Turkey
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Children's Cancer and Leukaemia GroupUnknown
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Alexion PharmaceuticalsCompletedHypophosphatasiaUnited States, United Arab Emirates, United Kingdom
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Oneness Biotech Co., Ltd.Active, not recruitingAtopic DermatitisUnited States
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Ascendis Pharma Growth Disorders A/SActive, not recruitingAchondroplasiaUnited States, Denmark, Ireland, New Zealand, Australia, Canada, Spain
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Queen's University, BelfastCystic Fibrosis FoundationRecruiting
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Astellas Pharma IncCompletedDermatitis, Atopic | Eczema, AtopicFrance, Germany, United Kingdom, Spain, Belgium, Netherlands, Finland, Poland, Ireland, Hungary, Denmark, Latvia
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Alexion PharmaceuticalsCompletedWolman Disease | Lysosomal Acid Lipase DeficiencyUnited Kingdom, France, United States, Egypt, Ireland
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Kamada, Ltd.CompletedEmphysemaUnited Kingdom, Canada, Denmark, Germany, Ireland, Netherlands, Sweden
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Galapagos NVCompletedCystic FibrosisUnited Kingdom, Australia, Ireland, Germany, Czech Republic
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NovartisCompletedDermatitis, AtopicUnited States
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Ardea Biosciences, Inc.Completed
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Regeneron PharmaceuticalsSanofiCompletedAtopic DermatitisGermany, Poland, Belgium, Netherlands, Russian Federation, Ireland, United Kingdom, Slovakia, Austria, Spain
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AstraZenecaCompletedCystic FibrosisSweden, Russian Federation, United Kingdom, Poland, Denmark, Germany
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New York State Institute for Basic ResearchEunice Kennedy Shriver National Institute of Child Health and Human Development... and other collaboratorsUnknownAlzheimer Disease | Down SyndromeUnited States, Canada, Australia, United Kingdom
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Sun Pharmaceutical Industries LimitedRecruitingDermatitis, AtopicUnited States, El Salvador
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Dermavant Sciences GmbHCompletedAtopic DermatitisCanada, United States
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Numab Therapeutics AGKaken Pharmaceutical Co., Ltd.RecruitingAtopic DermatitisGermany, Canada, United States, Poland
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Hoffmann-La RocheCompletedAtopic DermatitisUnited States, Canada