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Clinical Trials on Genetic Diseases, X-Linked in South Africa
Total 1104 results
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Novartis PharmaceuticalsActive, not recruitingSickle Cell Disease (SCD)United States, United Kingdom, Germany, Spain, Greece, Italy, Brazil, Lebanon, Turkey, Belgium, France, Jordan, India, Finland, Canada, Colombia, Netherlands, Oman, South Africa, Panama, Ghana
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Rhythm Pharmaceuticals, Inc.CompletedObesity | Genetic Obesity | Obesity Due to Melanocortin 4 Receptor DeficiencyUnited States, United Kingdom, Germany, Netherlands, France, Canada, Greece, Israel, Spain
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Acrotech Biopharma Inc.Active, not recruitingAtopic DermatitisUnited States
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SanofiCompletedAtopic DermatitisNetherlands, Chile, United States, Canada, Czechia, Germany, Poland
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Botanix PharmaceuticalsCompletedAtopic DermatitisUnited States, Australia, New Zealand
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Eli Lilly and CompanyIncyte CorporationTerminatedAtopic DermatitisUnited States, Puerto Rico, Canada
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Western Sydney Local Health DistrictRecruitingFamilial Adenomatous PolyposisAustralia
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SanofiRecruitingDermatitis AtopicItaly, United Kingdom, Argentina, France, Chile, Czechia, Germany, Japan, Spain, China, Netherlands, Brazil, Canada, Denmark, Korea, Republic of, South Africa, Taiwan, Poland, India, Mexico
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Incyte CorporationRecruitingAtopic DermatitisGermany, Poland, United States, Spain, United Kingdom, Italy, Belgium, Canada, Netherlands, Australia, Bulgaria, France, Switzerland, Hungary, Korea, Republic of
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AmgenActive, not recruitingAtopic DermatitisUnited States, Spain, United Kingdom, Korea, Republic of, Australia, Denmark, Germany, Belgium, Canada, Japan, Sweden, Poland, Romania, Estonia, Brazil, Czechia, Portugal, Finland, Mexico, Turkey, South Africa
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Kastle Therapeutics, LLCIonis Pharmaceuticals, Inc.CompletedMetabolic Diseases | Congenital Abnormalities | Infant, Newborn, Diseases | Genetic Diseases, Inborn | Dyslipidemias | Metabolism, Inborn Errors | Lipid Metabolism Disorders | Hypercholesterolemia | Hyperlipidemias | Hyperlipoproteinemias | Lipid Metabolism, Inborn Errors | Hyperlipoproteinemia Type II | Metabolic... and other conditionsUnited States, Canada, Brazil, Taiwan, Singapore, South Africa, United Kingdom
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The Medicines CompanyCompletedElevated Cholesterol | Heterozygous Familial HypercholesterolemiaUnited States, Canada, Czechia, Denmark, Netherlands, South Africa, Spain, Sweden
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Baxalta now part of ShireCompletedAlpha 1-Antitrypsin DeficiencyNew Zealand, Australia
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PfizerCompletedAtopic DermatitisGermany, United States, Canada, Denmark, Hungary, Australia, Latvia, Poland, Bulgaria, Japan
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Boehringer IngelheimCompletedCystic FibrosisUnited States, Australia, Austria, Belgium, Canada, Czech Republic, France, Germany, Hungary, Ireland, Israel, Italy, Poland, Portugal, Russian Federation, Slovakia, South Africa, Spain, Switzerland, United Kingdom
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LEO PharmaCompletedAtopic DermatitisUnited States, Denmark, United Kingdom, Korea, Republic of, Canada, Italy, Australia, Poland, Russian Federation
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BioMarin PharmaceuticalCompletedMucopolysaccharidosis IVA (Morquio A Syndrome)Australia
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Eisai Inc.CompletedLennox-Gastaut SyndromeFrance, Poland, United States, South Africa, Italy, Canada, Greece
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PharmaxisCompletedCystic FibrosisIreland, United Kingdom, Australia
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Grifols Therapeutics LLCCompletedEmphysema | Alpha 1-antitrypsin Deficiency (AATD)United States
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Vanda PharmaceuticalsCompletedAtopic DermatitisUnited States
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Grifols Therapeutics LLCCompleted
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PfizerCompletedSkin Diseases | Immune System Diseases | Hypersensitivity | Hypersensitivity, Immediate | Genetic Diseases, Inborn | Skin Diseases, Genetic | Dermatitis | Eczema | Skin Diseases, Eczematous | Dermatitis, AtopicSpain, Taiwan, United States, Australia, Poland, Germany, Hungary, Bulgaria, Czechia, Japan, Korea, Republic of, Latvia, Canada, United Kingdom, Mexico, Chile, Slovakia, Italy
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ADMA Biologics, Inc.CompletedPrimary Immune Deficiency DisorderUnited States
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Erasmus Medical CenterUniversitaire Ziekenhuizen KU Leuven; ZonMw: The Netherlands Organisation for... and other collaboratorsTerminatedNeurofibromatosis Type 1Spain, Belgium, Netherlands
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Grifols Therapeutics LLCCompleted
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ASLAN PharmaceuticalsRecruitingAtopic DermatitisUnited States, Canada
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MEDA Pharma GmbH & Co. KGCompletedAtopic DermatitisUnited States, Germany
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Western Sydney Local Health DistrictMonash University; University of Sydney; University of Melbourne; The University... and other collaboratorsNot yet recruiting
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PfizerCompletedPlaque Psoriasis | Atopic DermatitisUnited States, Australia, Canada, Poland
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HealthCore-NERINational Heart, Lung, and Blood Institute (NHLBI); Pediatric Heart NetworkCompletedCardiomyopathy, DilatedUnited States, Canada
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Tioga PharmaceuticalsCompletedPruritus | Atopic DermatitisUnited States
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Ultragenyx Pharmaceutical IncAbeona Therapeutics, IncTerminatedMucopolysaccharidosis III | Sanfilippo Syndrome | MPS IIIA | Sanfilippo AUnited States, Spain, Australia
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AstraZenecaCompletedAtopic DermatitisUnited States, Germany, Australia, Spain, United Kingdom, Poland
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Asana BioSciencesTerminatedAtopic DermatitisUnited States, Canada
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Eli Lilly and CompanyIncyte CorporationCompletedAtopic DermatitisUnited States, Puerto Rico, Canada
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Eli Lilly and CompanyIncyte CorporationCompletedAtopic DermatitisSpain, Australia, Korea, Republic of, Poland, Italy, Germany, Argentina, Austria, Japan, Taiwan
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Ionis Pharmaceuticals, Inc.Akcea TherapeuticsCompletedFamilial Chylomicronemia SyndromeUnited States, Brazil, Canada, France, Germany, Hungary, Israel, Italy, Netherlands, South Africa, Spain, United Kingdom
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UK Kidney AssociationRecruitingVasculitis | AL Amyloidosis | Tuberous Sclerosis | Fabry Disease | Cystinuria | Focal Segmental Glomerulosclerosis | IgA Nephropathy | Bartter Syndrome | Pure Red Cell Aplasia | Membranous Nephropathy | Atypical Hemolytic Uremic Syndrome | Autosomal Dominant Polycystic Kidney Disease | Cystinosis | Nephronophthisis | BK Nephropathy and other conditionsUnited Kingdom
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Eli Lilly and CompanyCompletedAtopic DermatitisUnited States
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PharmaxisCompletedCystic FibrosisAustralia, New Zealand
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Incyte CorporationCompletedAtopic DermatitisUnited States, Germany, Spain, Canada, Poland, Czechia, Bulgaria
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Eli Lilly and CompanyIncyte CorporationCompletedAtopic DermatitisSpain, Australia, Switzerland, Israel, Korea, Republic of, Japan, Poland, Argentina, Austria, Hungary
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Mayne Pharma International Pty LtdTerminatedLamellar IchthyosisUnited States, Spain, Canada, Germany, France, Australia, Israel, Ukraine, United Kingdom
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Daiichi Sankyo, Inc.CompletedAtopic DermatitisUnited States
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ShionogiCompletedAtopic DermatitisUnited States
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Regeneron PharmaceuticalsSanofiCompletedAtopic DermatitisUnited States, Italy, United Kingdom, Spain, Japan, Canada, Netherlands, New Zealand, Hungary, Czechia, Poland, Australia, Romania, Korea, Republic of
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Imara, Inc.CompletedSickle Cell DiseaseUnited States, United Kingdom
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Ardea Biosciences, Inc.CompletedGoutUnited States, Canada, South Africa, New Zealand, Belgium, Australia, Germany
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AbbVieActive, not recruitingAtopic DermatitisUnited States, Australia, Belgium, Bulgaria, Canada, China, Denmark, France, Germany, Hungary, Italy, Korea, Republic of, Mexico, Netherlands, Poland, Portugal, Puerto Rico, Romania, Slovakia, South Africa, Spain, Sweden, Switzerland, Taiwa... and more