Clinical Trials on Genetic Diseases, X-Linked in United States
Total 7913 results
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University of FloridaEngage Health Inc.CompletedDuchenne Muscular DystrophyUnited States
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University of FloridaCureDuchenneCompletedMuscular Dystrophy, DuchenneUnited States
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University of FloridaUnited States Department of DefenseCompletedDuchenne Muscular DystrophyUnited States
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Jerry R. MendellEunice Kennedy Shriver National Institute of Child Health and Human Development...CompletedDuchenne Muscular DystrophyUnited States
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Boston Children's HospitalBeth Israel Deaconess Medical CenterCompletedDuchenne Muscular DystrophyUnited States
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Applied Genetic Technologies CorpFoundation Fighting BlindnessCompletedX-linked Retinoschisis | XLRSUnited States
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Eunice Kennedy Shriver National Institute of Child...TerminatedFragile X Syndrome | Premature Ovarian Failure | Premature Menopause | FMR1 Premutation | Primary Ovairan InsufficiencyUnited States
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Beacon TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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National Institute of Allergy and Infectious Diseases...Completed
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TakedaTakeda Development Center Americas, Inc.Active, not recruitingHunter SyndromeUnited States, Germany, Malaysia, Philippines, Thailand, Dominican Republic, Serbia, Vietnam
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Kevin FlaniganMuscular Dystrophy AssociationTerminated
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Janssen Research & Development, LLCActive, not recruitingX-Linked Retinitis PigmentosaUnited States, United Kingdom
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Rare Disease Research, LLCSarepta Therapeutics, Inc.TerminatedDuchenne Muscular DystrophyUnited States
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Denali Therapeutics Inc.Enrolling by invitationMucopolysaccharidosis IIUnited States, Canada, Belgium, Czechia, Netherlands
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Sangamo TherapeuticsTerminated
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Beacon TherapeuticsEnrolling by invitationX-Linked Retinitis PigmentosaUnited States
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Lundquist Institute for Biomedical Innovation at...TerminatedMucopolysaccharidosis I | Mucopolysaccharidosis II | Mucopolysaccharidosis VIUnited States
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National Institute of Neurological Disorders and...CompletedMuscular Dystrophy | Muscular DiseaseUnited States
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Cedars-Sinai Medical CenterCompleted
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Cooperative International Neuromuscular Research...CompletedMuscular Dystrophy, DuchenneUnited States
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CSL BehringRecruiting
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SwanBio Therapeutics, Inc.RecruitingAMN | AMN Gene Mutation | X-ALDNetherlands, United States
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University of California, San DiegoBioMarin PharmaceuticalWithdrawnBehavioral Manifestations of Lesch-Nyhan DiseaseUnited States
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REGENXBIO Inc.RecruitingDuchenne Muscular DystrophyUnited States
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Edgewise Therapeutics, Inc.Medpace, Inc.CompletedBecker Muscular DystrophyUnited States
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Kevin FlaniganSarepta Therapeutics, Inc.Completed
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Kevin FlaniganActive, not recruitingDuchenne Muscular DystrophyUnited States
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Solid Biosciences Inc.CompletedDuchenne Muscular DystrophyUnited States
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Megan WaldropAudentes TherapeuticsActive, not recruitingDuchenne Muscular DystrophyUnited States
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Roxanna Marie BendixenTerminatedDuchenne Muscular DystrophyUnited States
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Craig McDonald, MDCardero Therapeutics, Inc.CompletedBecker Muscular DystrophyUnited States
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Sarepta Therapeutics, Inc.CompletedDuchenne Muscular DystrophyUnited States
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University of FloridaNational Institute of Arthritis and Musculoskeletal and Skin Diseases (NIAMS)Completed
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National Human Genome Research Institute (NHGRI)CompletedDuchenne Muscular DystrophyUnited States
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Nationwide Children's HospitalCompletedDuchenne Muscular DystrophyUnited States
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Nationwide Children's HospitalAsklepios Biopharmaceutical, Inc.CompletedDuchenne Muscular DystrophyUnited States
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ShireCompletedMucopolysaccharidosis IIUnited States, United Kingdom, Brazil, Germany
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Edimer PharmaceuticalsCompletedEctodermal DysplasiaUnited States
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Cangene CorporationWithdrawnHemophilia BUnited Kingdom, United States
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St. Jude Children's Research HospitalRecruitingHemophilia B | Gene TherapyUnited States
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Children's National Research InstituteFoundation to Eradicate DuchenneActive, not recruitingDuchenne Muscular DystrophyUnited States
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University of North Carolina, Chapel HillNational Institute of Neurological Disorders and Stroke (NINDS)CompletedMuscular Dystrophy, DuchenneUnited States
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Cooperative International Neuromuscular Research...Completed
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St. Jude Children's Research HospitalNot yet recruiting
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4D Molecular TherapeuticsActive, not recruitingX-Linked Retinitis PigmentosaUnited States
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Edimer PharmaceuticalsCompletedHypohidrotic Ectodermal DysplasiaUnited States
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ShireCompletedHunter SyndromeUnited Kingdom, United States, Brazil
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Mayo ClinicNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)Completed
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Cedars-Sinai Medical CenterCompleted
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Washington University School of MedicineBoston Children's Hospital; University of California, Davis; University of Minnesota and other collaboratorsCompletedDuchenne Muscular DystrophyUnited States